Search clinical trials for: Diamond-Blackfan Anemia

Total 4608 results

Orthogyn Medical Center, Bulgaria

Recruiting

Diastolic Deceleration Area in Early-onset FGR

Hypoxia | Anemia

Bulgaria
Universitas Sumatera Utara

Recruiting

The Association Between Anemia and Cardiomegaly

Cardiomegaly | Anemia in Children

Indonesia
Australian and New Zealand Intensive Care Research...

Not yet recruiting

Red Blood Cell Transfusion in ECMO - A Feasibility Trial (ROSETTA)

Extracorporeal Membrane Oxygenation Complication | Blood Loss Anemia
St. Jude Children's Research Hospital

Recruiting

Gene Therapy Communication: Use of a Needs Assessment to Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)

Sickle Cell Disease

United States
Masonic Cancer Center, University of Minnesota

Recruiting

Allo HSCT Using RIC and PTCy for Hematological Diseases

Follicular Lymphoma | Myelodysplastic Syndromes | Leukemia, Myeloid | Myelofibrosis | Burkitt Lymphoma | Marginal Zone Lymphoma | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Prolymphocytic Leukemia | Plasma Cell Leukemia | Myeloproliferative Neoplasm | Small Lymphocytic... and other conditions

United States
Istituto Ortopedico Galeazzi

Recruiting

Patient Blood Management in the Approach to Prosthetic Surgery [PBM(L4178)] (PBM(L4178))

Anemia, Iron Deficiency

Italy
Qianfoshan Hospital

Recruiting

Analysis of the Effect of Iron Supplements on Iron Deficiency Anemia in Pregnancy

Iron Deficiency Anemia of Pregnancy | Iron Storage Disease

China
Mario Negri Institute for Pharmacological Research

Recruiting

Functional Implications of Rare Gene Mutations in aHUS Open the Door to Personalized Therapy (aHUS-iPSC-EC)

Atypical Hemolytic Uremic Syndrome

Italy
Fox Chase Cancer Center

Recruiting

Iron Replacement to Reduce Anemia During Neoadjuvant Chemotherapy (Iron-RANC)

Anemia

United States
Cyprus Institute of Neurology and Genetics

Recruiting

Study of the Role of Genetic Modifiers in Hemoglobinopathies (INHERENT)

Sickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, Beta

United States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
Jiangsu HengRui Medicine Co., Ltd.

Recruiting

Safety and Effectiveness of Trappa Ethanolamine Tablets Combined With Ciclosporin in the Treatment of Primary Treatment of Non-severe Aplastic Anemia

Non-severe Aplastic Anemia

China
Shandong Qilu Stem Cells Engineering Co., Ltd.
Second Affiliated Hospital of Zhengzhou University; The Second Affiliated Hospital... and other collaborators

Recruiting

Clinical Study of UCB Combined With UC-MSCs in the Treatment of Bone Marrow Failure Disorders

Bone Marrow Failure Disorders

China
Novartis Pharmaceuticals

Not yet recruiting

Evaluate Long-term Safety, Tolerability and Efficacy of Iptacopan in Study Participants With aHUS

Atypical Hemolytic Uremic Syndrome
Catholic University of the Sacred Heart
Fondazione Poliambulanza

Recruiting

Virtual Reality Training for Aphasia Rehabilitation (Aphasia360)

Anomic Aphasia

Italy
Tomsk National Research Medical Center of the Russian...

Recruiting

The Prevalence of Iron Deficiency and the Effectiveness of Ferinject® in Patients With HFpEF (ID-HFpEF) (ID-HFpEF)

Chronic Heart Failure | Iron Deficiency, Latent

Russian Federation
LGD
ProRelix Services LLP

Recruiting

Safety and Efficacy of Orally Administered NUV001 Nutraceutical Supplement in Sickle Cell Disease Patients

Sickle Cell Disease

India
Sanofi

Recruiting

Cold Agglutinin Disease Real World Evidence Registry (CADENCE)

Cold Agglutinin Disease (CAD) | Cold Agglutinin Syndrome (CAS)

United States, Austria, France, Italy, Germany, Japan, Spain, United Kingdom
Assiut University

Not yet recruiting

Assessment of Quality of Life in Thalassemic Patients at Assiut University Hospital: A Single-center Experience

Thalassemia
LGD
Assistance Publique Hopitaux De Marseille; CEN Biotech; Etablissement Français...

Recruiting

Effect of NUV001 Supplementation in Patients Suffering From Sickle Cell Disease (SCD)

Sickle Cell Disease

France
Zhongnan Hospital

Recruiting

A Study of Shengxuening Tablet in the Treatment of Chemotherapy-related Anemia in Hematologic Tumors

Hematological Malignancy | Cancer-Related Anemia

China
Zenas BioPharma (USA), LLC

Recruiting

A Study of Obexelimab in Patients With Warm Autoimmune Hemolytic Anemia (SApHiAre)

Warm Autoimmune Hemolytic Anemia

Japan, United States, Taiwan, Spain, Italy, United Kingdom, Turkey, Poland
Centre Hospitalier Universitaire de Pointe-a-Pitre
Direction Générale de l'Offre de Soins

Recruiting

Lipid Balance in Adult Sickle Cell Patients (HDL2)

Dyslipidemia | Sickle Cell Disease | Complication

France
Assiut University

Not yet recruiting

NAC Effect on Iron Overload and Blood Transfusion in β-thalassemia Major

Thalassemia Major
Shanghai BDgene Co., Ltd.
Ruijin Hospital

Not yet recruiting

Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent β-thalassemia

β-thalassemia

China
Swedish Orphan Biovitrum

Recruiting

A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) (COMPLETE)

Paroxysmal Nocturnal Hemoglobinuria

Spain
Shanghai BDgene Co., Ltd.
Shanghai Children's Medical Center

Not yet recruiting

Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent Beta-thalassemia

β-thalassemia
Ascentage Pharma Group Inc.

Recruiting

A Study to Investigate the Safety, Pharmacokinetics and Efficacy of APG-5918 in Healthy Subjects or Anemic Patients

Anemia

China
Hallym University Medical Center

Recruiting

High Dose IV Iron Plus ESA in Chemotherapy-induced Anemia

Anemia

Korea, Republic of
First Affiliated Hospital of Guangxi Medical University
Genmedicn Biopharma Ltd.

Recruiting

A Study Evaluating the Safety and Efficacy of LentiRed Drug Product in Transfusion-dependent β-Thalassemia [TDT]

Transfusion Dependent Beta-Thalassemia

China
First Affiliated Hospital of Guangxi Medical University
Genmedicn Biopharma Ltd.

Recruiting

A Study Evaluating the Safety and Efficacy of the GMCN-508A Drug Product in Transfusion-dependent α-Thalassemia Participants

Transfusion-dependent α-Thalassemia

China
University of Alabama at Birmingham

Recruiting

Study on Use of Omega-3 Fatty Acids to Improve Outcomes in Individuals With Sickle Cell Disease

Sickle Cell Disease

United States
City of Hope Medical Center
National Cancer Institute (NCI)

Recruiting

A Reduced-Intensity Conditioning Regimen (Cyclophosphamide, Pentostatin, Anti-thymocyte Globulin) Followed by Haploidentical Hematopoietic Stem Cell Transplant for the Treatment of Patients With Refractory or Recurrent Severe Aplastic Anemia

Recurrent Severe Aplastic Anemia | Refractory Severe Aplastic Anemia

United States
Alpine Immune Sciences, Inc.

Recruiting

An Open-label Study of Povetacicept in Subjects With Autoimmune Cytopenias (RUBY-4)

Immune Thrombocytopenia | Idiopathic Thrombocytopenic Purpura | Cold Agglutinin Disease | Warm Autoimmune Hemolytic Anemia

United States, Canada, Australia, Turkey, United Kingdom
Aplastic Anemia and MDS International Foundation
National Organization for Rare Disorders

Recruiting

Global PNH Patient Registry

Paroxysmal Nocturnal Hemoglobinuria

United States
The George Institute
University of Oxford

Recruiting

SMART Health Pregnancy 2 - Intervention to Reduce Anaemia and Cardiometabolic Risk During Pregnancy and in the First Year Following Birth

Hypertension | Anemia | Type 2 Diabetes | Pre-Eclampsia | Gestational Diabetes | Anemia of Pregnancy | Gestational Hypertension

India
The University of Texas Health Science Center,...

Recruiting

Effectiveness of Small Phlebotomy Tubes in Reducing Blood Transfusions in Adult Medical Intensive Care Unit and Intermediate Care Unit Patients With Anemia

Anemia

United States
The University of The West Indies

Recruiting

Arterial Function Parameters and Transcranial Doppler Velocity in Paediatric Patients With Sickle Cell Disease (AFAT)

Sickle Cell Disease

Jamaica
Regeneron Pharmaceuticals

Recruiting

A Study to Examine the Long-term Safety, Tolerability, and Effectiveness of Pozelimab and Cemdisiran Combination Therapy in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (ACCESS-EXT)

Paroxysmal Nocturnal Hemoglobinuria

Taiwan, Korea, Republic of, Turkey, Spain, Thailand, Singapore, Japan, Canada, Malaysia, Poland, Italy
Shenzhen Hemogen

Recruiting

Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients

β-thalassemia

China
Disc Medicine, Inc

Recruiting

Study of DISC-0974 to Assess the Safety, Tolerability, PK and PD of DISC-0974 in Participants With CKD and Anemia

Chronic Kidney Diseases | Anemia of Chronic Kidney Disease

United States
The University of Texas Health Science Center,...

Not yet recruiting

A New Combination of Evidence-Based Interventions to Improve Primary Care Diagnostic Safety and Efficiency

Anemia | Decreased Glomerular Filtration Rate

United States
Memorial Sloan Kettering Cancer Center

Recruiting

A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)

Sickle Cell Disease | Thalassemia | Thalassemia, Beta

United States
H. Lee Moffitt Cancer Center and Research Institute
Bristol-Myers Squibb

Recruiting

Luspatercept for Anemia in Lower Risk MDS or Non-proliferative MDS/MPN Neoplasms

Myelodysplastic Syndromes | Anemia | Myeloproliferative Neoplasm

United States
University of Aberdeen

Not yet recruiting

ORCHARD- Optimising Home Assessment of Rural Patients (ORCHARD)

Cancer | Sickle Cell Disease | Immunosuppression | Inborn Errors of Metabolism | Organ Transplant | COPD Asthma
NovelMed Therapeutics

Not yet recruiting

Study of NM8074 in Soliris-Treated Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

PNH - Paroxysmal Nocturnal Hemoglobinuria
University of Pennsylvania

Recruiting

Effects of the Contraceptive Implant in Women With Sickle Cell Disease (SCD CURE)

Sickle Cell Disease

United States
Assistance Publique - Hôpitaux de Paris

Recruiting

Eculizumab in Hypertensive Emergency-associated Hemolytic Uremic Syndrome (HYPERSHU)

Hypertensive Emergency-associated Hemolytic Uremic Syndrome

France
Forma Therapeutics, Inc.
Emory University

Not yet recruiting

Study of the Effect of Etavopivat on Cerebral Hemodynamic Response in Children With Sickle Cell Disease

Sickle Cell Disease

United States
Institute of Hematology & Blood Diseases Hospital

Recruiting

Avatrombopag Combined With IST as First-line Treatment for SAA

Severe Aplastic Anemia

China
Peking Union Medical College Hospital
Pharmacosmos A/S

Recruiting

The Effects of Ferric Derisomaltose on Postoperative Anemia in Spinal Deformity Surgery

Surgery | Spinal Deformity | Adult | Perioperative Anemia

China

Search clinical trials for: Diamond-Blackfan Anemia

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