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Search clinical trials for: Friedreich
Total 86 results
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BiogenNot yet recruiting
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Friedreich's Ataxia Research AllianceRecruitingFriedreich AtaxiaUnited States, Canada, New Zealand, Australia, France, Austria, Belgium, Brazil, Czechia, Germany, Greece, Ireland, Italy, Spain, United Kingdom, India, Netherlands
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German Center for Neurodegenerative Diseases (DZNE)McMaster University; Sorbonne UniversityRecruitingFriedreich AtaxiaAustria, Germany, France
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Institut National de la Santé Et de la Recherche...Not yet recruiting
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Lexeo TherapeuticsRecruitingFriedreich Ataxia | Cardiomyopathy, SecondaryUnited States, Canada
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMyocardial Fibrosis | Cardiomyopathies | Friedreich Ataxia | Cardiac HypertrophyUnited States
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Institut National de la Santé Et de la Recherche...Imagine InstituteRecruiting
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Children's Hospital of PhiladelphiaNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of RochesterRecruitingFriedreich Ataxia | Neuro-Degenerative DiseaseUnited States, Canada, New Zealand, Australia, India
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University of FloridaNational Institutes of Health (NIH); National Center for Advancing Translational... and other collaboratorsRecruiting
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Weill Medical College of Cornell UniversityRecruitingFriedreich's AtaxiaUnited States
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European Friedreich's Ataxia Consortium for Translational...RecruitingFriedreich's AtaxiaAustria, Germany, Italy, Spain, Belgium, Czechia, France, Greece, Ireland, United Kingdom
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Murdoch Childrens Research InstituteActive, not recruiting
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Design Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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Larimar Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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Reata, a wholly owned subsidiary of BiogenAbbVie; Friedreich's Ataxia Research AllianceActive, not recruitingFriedreich AtaxiaUnited States, Australia, Austria, Italy, United Kingdom
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RWTH Aachen UniversityAssistance Publique - Hôpitaux de ParisWithdrawnFriedreich AtaxiaSpain, Italy, Austria, Germany, United Kingdom, France
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PTC TherapeuticsNo longer available
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Monash UniversityChildren's Hospital of Philadelphia; McGill University; University of Florida; University... and other collaboratorsActive, not recruitingFriedreich AtaxiaUnited States, Canada, Australia, Brazil, Germany
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Berta AlemanyInstitut d'Investigació Biomèdica de Girona Dr. Josep Trueta; Universitat de... and other collaboratorsCompleted
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University of PittsburghCompletedPulmonary Hypertension | Friedreich Ataxia | Iron-sulfur Cluster DeficiencyUnited States
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University of PittsburghFriedreich's Ataxia Research AllianceCompleted
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Stealth BioTherapeutics Inc.Active, not recruitingFriedreich AtaxiaUnited States
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Metro International Biotech, LLCChildren's Hospital of PhiladelphiaCompleted
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Design TherapeuticsCompleted
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University of MinnesotaCompleted
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IRCCS Eugenio MedeaUniversity of Rome Tor VergataCompleted
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University of MinnesotaFriedreich's Ataxia Research Alliance; Bob Allison Ataxia Research CenterCompletedFriedreich AtaxiaUnited States
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University of ChicagoPfizer; Biogen; APDM Wearable TechnologiesActive, not recruitingSpinocerebellar Ataxia Type 3 | Friedreich Ataxia | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6United States
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Children's Hospital of PhiladelphiaUniversity of California, Los Angeles; University of FloridaCompleted
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Burke Medical Research InstituteActive, not recruitingStroke | Multiple Sclerosis | Cerebral Palsy | Parkinson Disease | Spinal Cord Injuries | Neurologic Disorder | Hemiplegia | Hemiparesis | Friedreich Ataxia | Trauma, Brain | Transverse MyelitisUnited States
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Minoryx Therapeutics, S.L.CompletedFriedreich AtaxiaSpain, Belgium, France, Germany
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CENTOGENE GmbH RostockEnrolling by invitationHereditary Diseases | FXN Gene | FRDALebanon
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Larimar Therapeutics, Inc.Clinilabs, Inc.CompletedHealthy Volunteers | Friedreich AtaxiaUnited States
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University of South FloridaCompletedFriedreich's Ataxia | Spinocerebellar Ataxia - All Sub-typesUnited States
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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Neurocrine BiosciencesTakedaCompletedFriedreich AtaxiaUnited States
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ShireCompletedFriedreich's AtaxiaUnited States
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Vidara Therapeutics Research LtdCompleted
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research AllianceCompleted
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research AllianceCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Institut National de la Santé Et de la Recherche...Completed