- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: GNE Gene
Total 268683 results
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University of Campania "Luigi Vanvitelli"Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico; University of Milan and other collaboratorsRecruitingChronic Kidney Diseases | Ureteropelvic Junction ObstructionItaly
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Federico II UniversityUniversity of Pisa; University of Roma La Sapienza; Università degli Studi del... and other collaboratorsRecruitingInfections | Obesity | Lipodystrophy | Obesity Associated Disorder | Type2diabetesItaly
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Sheba Medical CenterNot yet recruitingRectal Cancer | Colon Cancer | Liver Metastasis Colon CancerIsrael
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Hospices Civils de LyonRecruitingRare Diseases | Toxic Epidermal NecrolysesFrance
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National Human Genome Research Institute (NHGRI)Therapeutics for Rare and Neglected Diseases (TRND)RecruitingGNE Myopathy | GNE Related DiseasesUnited States
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Leadiant Biosciences, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsActive, not recruiting
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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NobelpharmaCompletedGNE Myopathy | Nonaka Disease | Distal Myopathy With Rimmed Vacuoles (DMRV) | Hereditary Inclusion Body Myopathy (hIBM)Japan
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National Institute of Allergy and Infectious Diseases...Completed
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National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedHIV Infections | HIV SeronegativityUnited States
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National Institute of Allergy and Infectious Diseases...Completed
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National Institute of Allergy and Infectious Diseases...CompletedHIV InfectionsUnited States
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Newcastle UniversityUnknownHereditary Inclusion Body Myopathy | GNE MyopathyUnited Kingdom
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National Human Genome Research Institute (NHGRI)CompletedHereditary Inclusion Body MyopathyUnited States
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS)Completed
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
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University of California, San FranciscoGenentech, Inc.Terminated
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Institut de Myologie, FranceCompleted
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Ultragenyx Pharmaceutical IncNewcastle UniversityCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Nonaka Disease | Quadriceps Sparing Myopathy (QSM) | Distal Myopathy With Rimmed Vacuoles (DMRV)United States, Bulgaria, Canada, France, United Kingdom
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Ultragenyx Pharmaceutical IncCompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States, Israel
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Hadassah Medical OrganizationCompletedThrombocytopenia
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Sheba Medical CenterEuropean UnionUnknown
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS); Therapeutics...CompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE MyopathyUnited States, Israel
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Hamilton Health Sciences CorporationGenentech, Inc.Completed
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University Health Network, TorontoUnknown
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Oregon Health and Science UniversityAcorda TherapeuticsCompleted
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University of California, San FranciscoGenentech, Inc.CompletedRenal Transplant RejectionUnited States
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Gesellschaft fur Padiatrische Onkologie und Hamatologie...Unknown
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VaxGenCompleted
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VaxGenCompletedHIV Infections | HIV SeronegativityUnited States, Canada, Netherlands, Puerto Rico
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Faming ZhangNot yet recruitingChronic ConstipationChina
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Link Campus UniversityRecruitingOpen Abdomen | Diverticular PerforationItaly
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Merck Sharp & Dohme LLCNot yet recruiting
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Arab American University (Palestine)Not yet recruitingAutism Spectrum Disorder
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...Recruitingthe Recommended Target of Daily Vegetables Intake | Risk of HyperkalemiaTaiwan
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National Yang Ming Chiao Tung UniversityNot yet recruitingBreast Cancer | Weight LossTaiwan
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University of VirginiaRecruitingBreast Cancer | Blood Loss, SurgicalUnited States
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Etlik Zubeyde Hanım Women's Health Care, Training...Not yet recruitingDepression | Sexual Dysfunction | Polycystic Ovary
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Shirley Ryan AbilityLabNot yet recruitingEssential Tremor | Healthy IndividualsUnited States
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Blokhin's Russian Cancer Research CenterRecruitingColorectal CancerRussian Federation
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Merck Sharp & Dohme LLCNot yet recruiting
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Omer AyhanRecruiting
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University of California, San FranciscoRecruitingHeart Transplant Infection | Heart Transplant FailureUnited States
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Ain Shams UniversityRecruitingIntraoperative BleedingEgypt
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Boston Children's HospitalNot yet recruitingHypoxic-Ischemic Encephalopathy | Infant Development | Neurodevelopment | HIE
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Massachusetts General HospitalAmerican Heart AssociationRecruiting