- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Genetic Association Studies
Total 30419 results
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PfizerActive, not recruitingSickle Cell DiseaseUnited States, Lebanon, United Kingdom, Oman, Turkey, Canada, Egypt, Kenya, France, Italy, Netherlands
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyCompleted
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, United States, Ireland, Belgium, New Zealand, Spain, Netherlands, Portugal, Canada, Australia, France, Austria, Germany, Sweden
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Meyer Children's Hospital IRCCSActive, not recruitingChronic Kidney DiseasesItaly
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National Cancer Institute (NCI)CompletedAcute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Recurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia in Remission | Myelodysplastic Syndrome With Excess Blasts | Adult Acute Monocytic Leukemia | Adult Acute Myeloid Leukemia With Inv(16)(p13.1q22); CBFB-MYH11 and other conditionsUnited States, Israel, Peru
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City of Hope Medical CenterActive, not recruitingUnspecified Childhood Solid Tumor, Protocol Specific | Solid Tumor | Ewing Sarcoma | Unspecified Adult Solid Tumor, Protocol Specific | Recurrent Childhood Medulloblastoma | Recurrent Childhood Ependymoma | Recurrent Neuroblastoma | Recurrent Adult Soft Tissue Sarcoma | Recurrent Adult Brain Tumor | Recurrent... and other conditionsUnited States
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); St. Jude Children... and other collaboratorsEnrolling by invitationAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia | Multisystem ProteinopathyUnited States, South Africa, Germany
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AbbVieEndo Pharmaceuticals; Allergan Sales, LLC; Acerus Pharmaceuticals Corporation; Upsher-Smith...CompletedCardiovascular Diseases | HypogonadismUnited States, Puerto Rico
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Leipzig University Medical CenterEuropean Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyGermany
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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University of Washington, the Collaborative Health...Cystic Fibrosis FoundationCompletedCystic FibrosisUnited States
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University of Washington, the Collaborative Health...Cystic Fibrosis FoundationCompletedCystic FibrosisSpain, United States, Australia, Italy, France, Canada, Belgium, Denmark, Netherlands
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Centre for Addiction and Mental HealthCompletedCigarette Smoking BehaviorCanada
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University of DundeeBritish Lung Foundation; Newcastle University; University of Leicester; University... and other collaboratorsActive, not recruitingIdiopathic Pulmonary Fibrosis | Lung Diseases, Interstitial | Idiopathic Interstitial Pneumonias | Alveolitis, Extrinsic Allergic | Lung; Disease, Interstitial, With Fibrosis | Bird Fancier's LungUnited Kingdom
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Indiana UniversityCompletedLactose IntoleranceUnited States
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AmgenCompletedPsoriasisUnited States, Belgium, Italy, France, Germany, Puerto Rico, Canada
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Immunic AGTerminatedUlcerative ColitisUnited States, Russian Federation, Serbia, Belarus, Netherlands, Spain, United Kingdom, Croatia, Poland, Albania, Bosnia and Herzegovina, Bulgaria, Czechia, Georgia, North Macedonia, Portugal, Romania, Turkey, Ukraine
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Institut de Recherches Internationales ServierADIR, a Servier Group companyTerminatedMetastatic Colorectal CancerDenmark, Japan, Belgium, Finland, Hungary, United States
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AbbVieActive, not recruitingAtopic DermatitisUnited States, Australia, Austria, Belgium, Bulgaria, Canada, Croatia, Czechia, Denmark, France, Germany, Greece, Hungary, Ireland, Italy, Korea, Republic of, Netherlands, New Zealand, Portugal, Singapore, Spain, Taiwan, United Kingdom
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Principia Biopharma, a Sanofi CompanyCompleted
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Foundation for Prader-Willi ResearchPrader-Willi Syndrome Association USA; Foundation for Prader-Willi Research... and other collaboratorsCompletedPrader-Willi SyndromeUnited States
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RAPT Therapeutics, Inc.SuspendedAtopic DermatitisUnited States, Canada
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National Human Genome Research Institute (NHGRI)Active, not recruitingWiskott- Aldrich Syndrome | ADA Deficient SCIDUnited States
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Nektar TherapeuticsEli Lilly and CompanyCompleted
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Swedish Orphan BiovitrumCompletedChronic GoutUnited States
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Institut National de la Santé Et de la Recherche...Commissariat A L'energie Atomique; Imagine InstituteCompleted
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University Hospitals Bristol and Weston NHS Foundation...University College, London; The Tuberous Sclerosis AssociationActive, not recruitingTuberous Sclerosis ComplexUnited Kingdom
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Cellaion SAEnrolling by invitationUrea Cycle Disorder | Crigler-Najjar Syndrome | Acute on Chronic Liver FailureBelgium, Spain, France, Bulgaria, Poland
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MAPS Europe B.V.Multidisciplinary Association for Psychedelic StudiesCompletedPTSDCzechia, Germany, Netherlands, Norway, United Kingdom
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Centre Hospitalier Universitaire de NiceActive, not recruitingMuscular Dystrophy | FacioscapulohumeralFrance
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Virginia Commonwealth UniversityMuscular Dystrophy AssociationActive, not recruitingLGMD2E | LGMD2I | LGMD2A | LGMD2B | LGMD2C | LGMD1B | LGMD1C | LGMD1D | LGMD1E | LGMD1F | LGMD1G | LGMD1H | LGMD2D | LGMD2F | LGMD2G | LGMD2J | LGMD2K | LGMD2L | LGMD2M | LGMD2N | LGMD2O | LGMD2P | LGMD2Q | LGMD2S | LGMD2T | LGMD2U | LGMD2W | LGMD2X | LGMD2YUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingAcute Lymphoblastic Leukemia | Down Syndrome | Philadelphia Chromosome Positive | Childhood B Acute Lymphoblastic Leukemia With t(9;22)(q34.1;q11.2); BCR-ABL1 | Childhood B Acute Lymphoblastic Leukemia | Adult B Lymphoblastic Lymphoma | Ann Arbor Stage I B Lymphoblastic Lymphoma | Ann Arbor Stage... and other conditionsUnited States, Canada, Puerto Rico, Australia, New Zealand, Switzerland, Ireland
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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Washington University School of MedicineActive, not recruitingAlzheimer Disease | Dementia of Alzheimer TypeUnited States
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ItalfarmacoCompletedDuchenne and Becker Muscular Dystrophy | Polycytemia VeraCanada
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University College, LondonRadboud University Medical Center; Groupe Hospitalier Pitie-Salpetriere; Leiden... and other collaboratorsCompletedDuchenne Muscular DystrophyNetherlands, France, United Kingdom
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Janssen Research & Development, LLCCompletedPlaque PsoriasisUnited States, Korea, Republic of, Germany, France, Canada, Japan, Taiwan, Spain, United Kingdom, Poland
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CelgeneCompletedEczema | Dermatitis, AtopicUnited States, Canada, Japan, Poland, China, Czechia
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University of Southern CaliforniaMultidisciplinary Association for Psychedelic StudiesActive, not recruiting
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Hunan Province Tumor HospitalCompletedNon-small Cell Lung CancerChina
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Multidisciplinary Association for Psychedelic StudiesWithdrawnAnxiety | Stage IV MelanomaUnited States
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Neurocrine BiosciencesVoyager TherapeuticsCompletedParkinson's DiseaseUnited States
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University of Colorado, DenverOhio State University; American Heart AssociationCompletedHeart Failure, Systolic | Ventricular Remodeling | Dilated Cardiomyopathies, Idiopathic | Electrical RemodelingUnited States
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DICE Therapeutics, Inc., a wholly owned subsidiary...Active, not recruitingPlaque PsoriasisCanada, Hungary, Germany, Spain, United States, Poland, United Kingdom, Czechia
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Worldwide Innovative Network AssociationPfizer; ARC Foundation for Cancer ResearchTerminatedNon-small Cell Lung Cancer Metastatic | Non-small Cell Lung Cancer Stage IIIBIsrael, United States, Luxembourg, Spain
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Galapagos NVGilead SciencesCompletedCrohn's DiseaseHong Kong, United States, Netherlands, Belgium, France, Israel, Spain, Korea, Republic of, Taiwan, Germany, Australia, United Kingdom, Italy, India, Singapore, Portugal, Malaysia, New Zealand, Serbia, Ireland, Poland, Romania, Japan, ... and more
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedBradycardia | Down SyndromeUnited States
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AbbVieCompletedPsoriasisUnited States, Australia, Austria, Belgium, Canada, Czechia, Finland, France, Germany, Japan, Korea, Republic of, Mexico, Poland, Portugal, Spain, Sweden, Taiwan
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Janssen Research & Development, LLCCompletedColitis, UlcerativeUnited States, Russian Federation, Australia, Poland, Germany, Brazil, Ukraine, Argentina, Mexico