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Search clinical trials for: Genetic HCM
Total 18739 results
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Gene SolutionsRecruitingBreast Cancer | Gastric Cancer | Colorectal Cancer | Non Small Cell Lung Cancer | Advanced Cancer | Liver Cancer | Immune Checkpoint InhibitorVietnam
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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Gene SolutionsRecruitingTriple Negative Breast Cancer | HER2-positive Breast Cancer | Stage II Breast Cancer | Breast Cancer Female | Stage III Breast CancerVietnam
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Magdi Yacoub Heart FoundationRecruiting
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Tenaya TherapeuticsRecruitingHypertrophic CardiomyopathyUnited States
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Bristol-Myers SquibbRecruitingCardiomyopathy, HypertrophicUnited States, Poland, Spain, Italy
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Tenaya TherapeuticsRecruitingNatural History Study in Pediatric Patients With MYBPC3 Mutation-associated Cardiomyopathy (MyCLIMB)CardiomyopathyUnited States, Canada, United Kingdom, Spain
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University Hospital HeidelbergCharite University, Berlin, Germany; Goethe University; University Medicine Greifswald and other collaboratorsRecruitingAmyloidosis | HCM - Hypertrophic Cardiomyopathy | Arrhythmogenic Right Ventricular Cardiomyopathy | Inflammatory Cardiomyopathy | DCM - Dilated Cardiomyopathy | Non-ischemic Cardiomyopathy | HOCM - Hypertrophic Obstructive Cardiomyopathy | Left Ventricular Noncompaction CardiomyopathyGermany
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University of Texas Southwestern Medical CenterRecruitingDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Dilated Cardiomyopathy | Cardiomyopathy, Hypertrophic | Heart Failure With Reduced Ejection Fraction | Cardiac Sarcoidosis | Heart Failure With Preserved Ejection FractionUnited States
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Andrea GropmanEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingBrain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Urea Cycle DisordersUnited States, Canada, Germany, Switzerland
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HeterozygousUnited States, Germany, South Africa, Greece, Italy, Czechia, Taiwan, Slovakia, Turkey, France, Russian Federation, Canada, Spain, Jordan, Switzerland, Hungary, Poland, Netherlands, Norway, United Kingdom, Lebanon, Argentina, Brazil, ... and more
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PfizerCompletedTransthyretin Amyloidosis Cardiomyopathy (ATTR-CM)Italy, Romania, France, Australia, Austria, Portugal, Slovakia, Slovenia, Spain, United Kingdom
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Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationHypertrophic Cardiomyopathy (HCM) | Long QT Syndrome (LQTS) | Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT) | Inherited Cardiac Arrythmias | Brugada Syndrome (BrS) | Early Repolarization Syndrome (ERS) | Arrhythmogenic Cardiomyopathy (AC, ARVD/C) | Dilated Cardiomyopathy (DCM) | Muscular... and other conditionsUnited States
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University of VirginiaNational Heart, Lung, and Blood Institute (NHLBI); Oxford University Hospitals...Active, not recruitingHypertrophic CardiomyopathyUnited States, Canada, Germany, United Kingdom, Netherlands, Italy
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Montreal Heart InstituteCanadian Institutes of Health Research (CIHR)Enrolling by invitationCardiomyopathies | Hypertrophic Cardiomyopathy | Hypertrophic Obstructive Cardiomyopathy | Familial Hypertrophic CardiomyopathyCanada
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Yale UniversityNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedHypertrophic Cardiomyopathy | Long QT SyndromeUnited States, United Kingdom, Canada, Australia, New Zealand
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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The Cleveland ClinicCompletedHypertrophic Cardiomyopathy | Genetic Disease | Gene Product Sequence VariationUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCardiomyopathy | Obstructive Hypertrophic CardiomyopathyUnited States
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University Hospital, BordeauxAmicus Therapeutics; Fédération Française de Cardiologie; Fondation Bordeaux...CompletedEndothelial Dysfunction | Hypertrophic CardiomyopathyFrance
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Wuerzburg University HospitalTakedaEnrolling by invitationLysosomal Storage Diseases | Fabry Disease | Fabry Disease, Cardiac Variant | HCM - Hypertrophic Cardiomyopathy | Anderson Fabry DiseaseGermany
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University of PittsburghTerminated
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Institut Universitari DexeusCompletedFertility DisordersSpain, Vietnam
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National Human Genome Research Institute (NHGRI)CompletedCardiovascular DiseaseUnited States
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Gilead SciencesTerminatedHypertrophic CardiomyopathyAustralia, United States, Netherlands, Israel, Italy, France, Germany, United Kingdom
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University of HaifaBnai Zion Medical Center; Clalit Health Services, Haifa and West GalileeNot yet recruitingCardiovascular Diseases | Infections | Autoimmune Diseases | Parkinson Disease | Dementia | Alzheimer Disease | Chronic Lymphocytic Leukemia | Monoclonal B-Cell Lymphocytosis | Cancers
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Ospedale San RaffaeleRecruitingHypertension | AKI | CKD | Hematologic Malignancy | Ckd-Mbd | ADPKD | Bone Marrow Transplant Complications | CKD (Chronic Kidney Disease) Stage 5DItaly
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Instituto Nacional de Investigacao em Saude, AngolaFUNDAÇAO CALOUSTE GULBENKIAN; FUNDACIÓN BANCARIA CAIXA D'ESTALVIS I PENSIONS... and other collaboratorsRecruitingPregnancy Complications | Pregnancy Related | Sickle Cell Disease | Pre-EclampsiaAngola
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AstraZenecaRecruitingCarpal Tunnel Syndrome | Amyloidosis | Polyneuropathy | Hereditary Transthyretin AmyloidosisRussian Federation
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SanofiRegeneron PharmaceuticalsNot yet recruiting
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Jiangsu HengRui Medicine Co., Ltd.Not yet recruitingGout With Hyperuricemia in Adults
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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Poitiers University HospitalNot yet recruiting
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SpinogenixAvance Clinical Pty Ltd.Not yet recruiting
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CytokineticsNot yet recruitingPediatric | Symptomatic Obstructive Hypertrophic Cardiomyopathy
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Children's Hospital Los AngelesNot yet recruitingCystic Fibrosis | Constipation Chronic IdiopathicUnited States
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IRCCS Ospedale San RaffaeleNot yet recruitingRare Diseases | Corneal Neovascularization | Limbal Stem Cell Deficiency | Aniridia | Neurotrophic Keratopathy | Ocular Cicatricial Pemphigoid | Ocular Graft-versus-host Disease | EEC Syndrome
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Ospedale San RaffaeleFondazione IRCCS Ca' Granda, Ospedale Maggiore PoliclinicoRecruitingNon-Tuberculous Mycobacterial Pneumonia | Cystic Fibrosis LungItaly
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All India Institute of Medical Sciences, BhubaneswarNot yet recruitingThyroid Eye Disease | Graves OphthalmopathyIndia
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Masonic Cancer Center, University of MinnesotaNot yet recruitingAcquired Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Acquired Amegakaryocytic Thrombocytopenia
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QED Therapeutics, Inc.RecruitingChildren With HypochondroplasiaUnited States, Australia, Norway, Portugal, Singapore, Spain
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Avidity Biosciences, Inc.Not yet recruitingMyotonic Dystrophy | Myotonic Disorders | Myotonia | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert Disease | Steinert
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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Johns Hopkins UniversityNational Center for Complementary and Integrative Health (NCCIH); Bowdoin CollegeRecruitingTourette Syndrome | Tic Disorders | Tourette's Disorder | Persistent Tic Disorder | Chronic Motor Tic Disorder | Chronic Vocal Tic Disorder | Persistent Motor Tic Disorder | Persistent Vocal Tic DisorderUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingRenal TransplantationFrance
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Riphah International UniversityNot yet recruiting
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Wave Life Sciences Ltd.Not yet recruiting
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Tisento TherapeuticsNot yet recruitingMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)United States, Australia, Italy, Germany, Canada, United Kingdom
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Başak Çağla ArslanHacettepe UniversityRecruitingDuchenne Muscular Dystrophy | Occupational Therapy | GamificationTurkey