- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Genetic lipids disorders
Total 157252 results
-
Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
-
Washington University School of MedicineNational Cancer Institute (NCI); The Foundation for Barnes-Jewish HospitalRecruitingMultiple Myeloma | Rectal Cancer | Cholangiocarcinoma | Colon CancerUnited States
-
Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
-
IRCCS Eugenio MedeaRecruiting
-
IRCCS San RaffaeleRecruiting
-
GCS Ramsay Santé pour l'Enseignement et la RechercheNot yet recruiting
-
Assistance Publique - Hôpitaux de ParisNot yet recruitingAutism Spectrum DisorderFrance
-
Centre Hospitalier Sud FrancilienNot yet recruiting
-
Anhui Medical UniversityRecruitingCognitive Impairment | Intracranial Atherosclerosis | Cerebrovascular EventChina
-
Mahidol UniversityNot yet recruitingBMI | Metabolic Syndrome | Insulin Resistance | NAFLD | Genetic Polymorphism | Cardiovascular Disease (CVD) | MASLD | Daily Step Count
-
Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States
-
Qianfoshan HospitalNot yet recruitingFrail Elderly | Perioperative Neurocognitive Disorders
-
Nina HermansUniversity Hospital, AntwerpRecruitingLow-Density-Lipoprotein-Type [LDL] HyperlipoproteinemiaBelgium
-
CARsgen Therapeutics Co., Ltd.Not yet recruitingMultiple Myeloma | Primary Plasma Cell Leukemia
-
Maastricht University Medical CenterRecruitingQuality of Life | Tuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
-
Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Recruiting
-
Hospital do CoracaoUniversity of Sao Paulo; Instituto Dante Pazzanese de Cardiologia; National Institute...Not yet recruiting
-
Siriraj HospitalNot yet recruiting
-
Tampere UniversityProfessor Lauri Lehtimäki; Professor Mika Mäkelä; Professor Sanna Toppila-Salmi; Professor Ilkka JunttilaNot yet recruitingAsthma | Allergy | Rhinitis, Allergic | Asthma in Children | Atopic Dermatitis | Allergen ImmunotherapyFinland
-
MinYoung Kim, MD, PhDNot yet recruitingAlzheimer Dementia (AD)
-
ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
-
Chiesi Farmaceutici S.p.A.ICON plcNot yet recruiting
-
ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
-
University Health Network, TorontoNot yet recruitingIrritable Bowel Syndrome | Gastrointestinal Dysfunction | Ehlers-Danlos Syndrome | Hypermobility SyndromeCanada
-
Caroline Michaela KistorpSanofiNot yet recruitingChronic Kidney Diseases | Fabry DiseaseDenmark
-
National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
-
University of AarhusAarhus University HospitalRecruitingCardiovascular Diseases | Inflammation | Lymphedema | Turner SyndromeDenmark
-
Dr. Sascha DrewloNot yet recruitingFetal Growth Retardation | Preeclampsia | Cervix; Pregnancy | Inherited Genetic Conditions (Diagnosis)
-
Blueskin ASRecruitingPsoriasis | Atopic Dermatitis | Vitiligo | Alopecia AreataDenmark
-
University of RochesterNot yet recruitingAge-Related Macular Degeneration | Retinitis Pigmentosa | Retinal Dystrophies | Alcohol Use Disorder | Stargardt DiseaseUnited States
-
National University of Natural MedicineRecruiting
-
Kathelijn FischerRadboud University Medical Center; University Medical Center Groningen; Maastricht... and other collaboratorsRecruitingAdolescent | Child | Hemophilia A With Inhibitor | Adult | Hemophilia A Without Inhibitor | Hemophilia A, SevereNetherlands
-
Maastricht University Medical CenterRecruiting
-
Qilu Hospital of Shandong UniversityRecruitingChild | Williams Syndrome | Neurodevelopmental DelayChina
-
Boryung Pharmaceutical Co., LtdRecruitingMixed Dyslipidemia | Primary HypercholesterolemiaKorea, Republic of
-
Noema Pharma AGNot yet recruiting
-
Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
-
University of California, Los AngelesRecruitingTuberous SclerosisUnited States
-
University of ValenciaAsociación de Fibrosis Quística - Comunidad ValencianaNot yet recruiting
-
University of Nevada, Las VegasRecruitingColorectal Disorders | Surgical Site Infection | Wound SurgicalUnited States
-
M.D. Anderson Cancer CenterNovartis PharmaceuticalsNot yet recruitingAcute Lymphoblastic Leukemia | Philadelphia Chromosome-PositiveUnited States
-
Zhujiang HospitalNot yet recruitingEfficacy Endpoint: no New Cerebrovascular Adverse Events Within 1 Year | Safety Endpoint: no New Moderate or Serious Adverse Events Within 1 Year | All-cause Mortality Events (Within 1 Year) | Incident Ischemic Stroke Events (Within 1 Year) | New Hemorrhagic Stroke Events (Within 1 Year) | New... and other conditions
-
Forge Biologics, IncNot yet recruiting
-
Halic UniversityRecruitingCystic Fibrosis | Cystic Fibrosis in ChildrenTurkey
-
NewAmsterdam PharmaNot yet recruitingCoronary Artery Disease | Plaque, Atherosclerotic | Lipidemia
-
Massachusetts General HospitalJohns Hopkins UniversityNot yet recruitingNeurofibromatosis 1 | Neurofibromas, CutaneousUnited States
-
Inozyme PharmaGACI GlobalNot yet recruitingATP-Binding Cassette Subfamily C Member 6 Deficiency | Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
-
Chang Gung Memorial HospitalRecruiting
-
Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
-
ARTHEx Biotech S.L.Not yet recruitingMyotonic Dystrophy 1