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Search clinical trials for: Genetic modifiers
Total 18536 results
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University Hospital, AntwerpUniversity Hospital, GhentRecruitingMarfan Syndrome | FBN1 MutationBelgium
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Ahmadu Bello University Teaching HospitalCyprus Institute of Neurology and GeneticsNot yet recruiting
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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Stanford UniversityJohns Hopkins University; University of California, San FranciscoRecruitingNeurofibromatosis 1United States
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St. Jude Children's Research HospitalRecruitingPancreatic Cancer | Hodgkin Lymphoma | Lynch Syndrome | Tuberous Sclerosis | Fanconi Anemia | AML | Non Hodgkin Lymphoma | Familial Adenomatous Polyposis | Acute Leukemia | Nevoid Basal Cell Carcinoma Syndrome | Neurofibromatosis Type 1 | Neuroblastoma | Retinoblastoma | MDS | Rhabdomyosarcoma | Von Hippel-Lindau Disease | Adrenocortical Carcinoma and other conditionsUnited States
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University of IowaJohns Hopkins University; University of Colorado, Denver; King's College Hospital... and other collaboratorsRecruitingCharcot-Marie-Tooth Disease, Type Ia (Disorder) | HMSNUnited States, Italy, United Kingdom, Australia
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University of FloridaUniversity of California, Los Angeles; National Ataxia FoundationRecruitingSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6United States
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Peloton Therapeutics, Inc., a subsidiary of Merck...National Institutes of Health (NIH)CompletedClear Cell Renal Cell Carcinoma | Von Hippel-Lindau Disease | Clear Cell RCC | ccRCC | VHL Gene Mutation | VHL Syndrome | VHL Gene Inactivation | VHL | Von Hippel | Von Hippel's Disease | Von Hippel-Lindau Syndrome, Modifiers ofUnited States
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruiting
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University of North Carolina, Chapel HillNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Cystic...Active, not recruitingCystic Fibrosis | Liver DiseaseUnited States
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Johns Hopkins UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Northwestern... and other collaboratorsEnrolling by invitationCystic Fibrosis Related DiabetesUnited States
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State University of New York - Upstate Medical...Albert Einstein College of MedicineCompleted
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University College, LondonUnknown
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St. Jude Children's Research HospitalCompletedAcute Lymphoblastic Leukemia (ALL)United States
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Tongji HospitalUnknown
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Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Completed
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University Hospital, MontpellierCompletedCystic Fibrosis | Healthy SubjectsFrance
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Assistance Publique - Hôpitaux de ParisFrench National Referral Center for NeurofibromatosesUnknown
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Boston Children's HospitalNot yet recruiting
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Groupe Hospitalier de la Region de Mulhouse et...Not yet recruitingChronic Obstructive Pulmonary Disease | Pulmonary Fibrosis | Cystic Fibrosis
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CSL BehringNot yet recruiting
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Adam S. Kibel, MDNational Cancer Institute (NCI)Not yet recruitingProstate Cancer | Polygenic Risk ScoreUnited States
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Essen BiotechNot yet recruitingSickle Cell Disease | Sickle-Cell Disease With CrisisChina
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Oneness Biotech Co., Ltd.Not yet recruiting
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TakedaNot yet recruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)
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Academisch Medisch Centrum - Universiteit van Amsterdam...RecruitingSickle Cell Disease | Sickle Cell SC Disease | Sickle Cell-SS Disease | Sickle Cell RetinopathyNetherlands
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Vanderbilt University Medical CenterAminu Kano Teaching HospitalNot yet recruitingMalnutrition | Sickle Cell Disease
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Institute of Liver and Biliary Sciences, IndiaRecruitingGlycogen Storage DiseasesIndia
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Steminent US, Inc.Not yet recruitingSpinocerebellar Ataxias
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Apogee Therapeutics, Inc.Recruiting
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Alnylam PharmaceuticalsNot yet recruitingCerebral Amyloid Angiopathy
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Pauls Stradins Clinical University HospitalRecruiting
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Janjira PetsuksiriMahidol UniversityNot yet recruitingThyroid Associated OphthalmopathyThailand
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Natural Resources Institute FinlandTampere UniversityRecruitingMicrobial Colonization | Atopic Dermatitis | Immune System and Related Disorders | Nature, HumanFinland
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Peking University First HospitalRecruitingRenal Cell Carcinoma | VHL SyndromeChina
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Peking Union Medical College HospitalNot yet recruitingDuchenne Muscular Dystrophy (DMD)
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AbbVieNot yet recruiting
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Hannover Medical SchoolBoehringer IngelheimNot yet recruitingAutosomal Dominant Polycystic Kidney
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Assistance Publique - Hôpitaux de ParisNot yet recruitingLimb Girdle Muscular Dystrophy
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GRIN Therapeutics, Inc.RecruitingTuberous Sclerosis Complex | Focal Cortical DysplasiaSpain, United Kingdom, Australia, Belgium, Canada, Italy, Poland
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GeneCradle IncRecruitingPompe Disease (Late-onset)China
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Gene SolutionsUniversity of Medicine and Pharmacy at Ho Chi Minh CityRecruitingCancer, Breast | Cancer, Lung | Cancer Colon | Cancer, Gastric | Cancer, LiverVietnam
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Clinuvel Europe LimitedRecruiting
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OcugenRecruitingRetinitis PigmentosaUnited States
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University College, LondonLondon School of Hygiene and Tropical Medicine; King's College London; University... and other collaboratorsRecruitingTourette Syndrome | Deep Brain StimulationUnited Kingdom
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Laval UniversityRecruitingFamilial Hypercholesterolemia | Cholesterol, Elevated | Nutrition, HealthyCanada
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Belite Bio, IncNot yet recruitingStargardt Disease 1 | STGD1United States
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University of Mississippi Medical CenterUniversity of Alabama at BirminghamRecruiting
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Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
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AbbVieNot yet recruiting