- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Hemoglobinopathies
Total 1333 results
-
National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Hemolytic AnemiaUnited States
-
PfizerActive, not recruitingSickle Cell DiseaseUnited States, Oman, United Kingdom, France, Egypt, Ghana, Italy, Kenya, Nigeria, Saudi Arabia
-
Agios Pharmaceuticals, Inc.Active, not recruitingNon-Transfusion-dependent Alpha-Thalassemia | Non-Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United Kingdom, Malaysia, United States, Netherlands, Bulgaria, Turkey, Italy, Canada, Brazil, France, United Arab Emirates, Denmark, Greece, Lebanon, Saudi Arabia
-
Children's Hospital Medical Center, CincinnatiTerminated
-
Agios Pharmaceuticals, Inc.Active, not recruitingTransfusion-dependent Alpha-Thalassemia | Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United States, France, Canada, Malaysia, Germany, Netherlands, Bulgaria, United Kingdom, Turkey, Italy, Greece, United Arab Emirates, Brazil, Denmark, Lebanon, Saudi Arabia
-
Hospital Universitari Vall d'Hebron Research InstituteActive, not recruitingSickle Cell DisordersSpain, Netherlands, France, Italy
-
Agios Pharmaceuticals, Inc.Active, not recruitingThalassemiaUnited States, Canada, United Kingdom
-
PfizerActive, not recruitingSickle Cell Disease | Leg UlcersBrazil, Nigeria, Kenya
-
PfizerPfizerAvailableSickle Cell DiseaseUnited States, Brazil
-
Forma Therapeutics, Inc.Medpace, Inc.CompletedHealthy Volunteers | Sickle Cell DiseaseUnited States
-
Bangabandhu Sheikh Mujib Medical University, Dhaka...CompletedTransfusion-dependent ThalassemiaBangladesh
-
St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); University of Memphis; Methodist...Active, not recruiting
-
Novartis PharmaceuticalsCompleted
-
University of PennsylvaniaEnrolling by invitationSickle Cell Disease | Vaso-occlusive CrisisUnited States
-
University of Alabama at BirminghamNational Heart, Lung, and Blood Institute (NHLBI)TerminatedHypertension | Proteinuria | Sickle Cell Disease | Anemia, Sickle Cell | Kidney DiseaseUnited States
-
Roswell Park Cancer InstituteActive, not recruitingAcute Myeloid Leukemia | Polycythemia Vera | Myelofibrosis | Chronic Myelomonocytic Leukemia | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Secondary Acute Myeloid Leukemia | Sickle Cell Disease | Myelodysplastic Syndrome | Plasma Cell Myeloma | Chronic Granulomatous... and other conditionsUnited States
-
PfizerActive, not recruitingSickle Cell DiseaseUnited States, Lebanon, United Kingdom, Oman, Turkey, Canada, Egypt, Kenya, France, Italy, Netherlands
-
Vanderbilt University Medical CenterAminu Kano Teaching Hospital; Murtala Muhammad Specialist HospitalCompletedSickle Cell Anemia | Severe Acute MalnutritionNigeria, United States
-
RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
-
Gary M Brittenham, MDActive, not recruitingRespiratory Tract Infections | Respiratory Tract Diseases | Respiration Disorders | Lung Diseases | Nutrition Disorders | Vitamin D Deficiency | Asthma | Sickle Cell Disease | Anemia, Sickle Cell | Anemia, Hemolytic, Congenital | Acute Chest Syndrome | Deficiency Diseases VitaminUnited States
-
Vifor (International) Inc.FortreaCompletedSickle Cell DiseaseUnited States, France, Greece, Lebanon, United Kingdom
-
Boston Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)Completed
-
bluebird bioActive, not recruitingTransfusion-dependent Beta-ThalassemiaUnited States, France, United Kingdom, Australia, Thailand, Italy, Germany, Greece
-
PfizerTerminatedSickle Cell Disease | Vaso-occlusive Pain Episode in Sickle Cell Disease | Vaso-occlusive CrisisUnited States, Oman, France, Brazil, Colombia, Lebanon, Nigeria, Germany, Italy, Kenya, Saudi Arabia, Turkey, United Kingdom, Zambia
-
Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
-
Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Hematological DiseasesUnited States, Belgium, Canada, France, Germany, Italy, United Kingdom
-
King's College Hospital NHS TrustKing's College LondonCompletedLiver Failure | Cancer | Asthma | Renal Failure | Cystic Fibrosis | Chronic Heart Failure | Sickle Cell Disease | Interstitial Lung Disease | COPD | Dyspnea | Post COVID-19 | Bronchiectasis AdultUnited Kingdom
-
Chiesi Canada CorpCompletedIron Overload | Beta Thalassemia Major AnemiaEgypt, Indonesia
-
New York Medical CollegeWashington University School of Medicine; University of California, Los Angeles and other collaboratorsActive, not recruitingSickle Cell DiseaseUnited States
-
PfizerWithdrawn
-
National Institute of Blood and Marrow Transplant...Completed
-
Emory UniversityNational Institute of Nursing Research (NINR)CompletedSickle Cell DiseaseUnited States
-
bluebird bioCompletedBeta-ThalassemiaUnited States, Germany, United Kingdom, France, Greece, Italy
-
City of Hope Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Active, not recruitingSickle Cell Disease | Anemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Sickle Cell DisorderUnited States
-
King's College LondonSickle Cell SocietyActive, not recruitingSickle Cell DiseaseUnited Kingdom
-
PfizerPfizerCompletedSickle Cell DiseaseUnited States
-
Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
-
University of BahrainCompletedSelf-Efficacy | Self-CareBahrain
-
Bioray LaboratoriesXiangya Hospital of Central South University; First Affiliated Hospital of... and other collaboratorsEnrolling by invitation
-
University Hospital, Basel, SwitzerlandCompleted
-
Children's Hospital Medical Center, CincinnatiCompletedSickle Cell DiseaseUnited States
-
PfizerActive, not recruitingSickle Cell Disease | Vaso-occlusive Pain Episode in Sickle Cell Disease | Vaso-occlusive CrisisUnited States, Oman, France, Brazil, Colombia, Egypt, Nigeria, Lebanon, Germany, Italy, Kenya, Saudi Arabia, Tanzania, Turkey, Zambia, Ghana, United Kingdom
-
Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
-
PfizerCompleted
-
National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Congenital Hemolytic AnemiaUnited States
-
Bioray LaboratoriesFirst Affiliated Hospital of Guangxi Medical UniversitySuspendedThalassemia MajorChina
-
Jesse NodoraNational Cancer Institute (NCI)TerminatedCoronary Artery Disease | Heart Failure | Obesity | Diabetes Mellitus, Type 2 | Cancer | Chronic Kidney Diseases | Sickle Cell Disease | COPDUnited States
-
Children's Hospital of PhiladelphiaActive, not recruitingHemoglobinopathies | Immunodeficiencies | Non Malignant DiseasesUnited States
-
Zagazig UniversityCompletedVitamin D Deficiency | Sickle Cell Disease | Bone Mineral Density | Health Related Quality of Life | Hand Grip StrengthEgypt
-
National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingVenous Thrombosis | Sickle Cell Disease | Venous Thromboembolism | Sickle Cell Trait | Hypercoagulable StateUnited States