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Search clinical trials for: Hereditary study for PH
Total 422225 results
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Eloxx Pharmaceuticals, Inc.Recruiting
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Bulgaria, Czechia, Hungary, Spain, France, Germany, Poland, Canada, Israel
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Ionis Pharmaceuticals, Inc.RecruitingHereditary AngioedemaUnited States, Puerto Rico, Belgium, Bulgaria, Canada, France, Germany, Israel, Italy, Netherlands, Poland, Spain, Turkey, United Kingdom
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Santen Inc.ActualEyes Inc.RecruitingFuchs Endothelial Corneal DystrophyUnited States
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello SyndromeUnited States
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Jaeb Center for Health ResearchDepartment of Health and Human Services; Food and Drug Administration (FDA); Conquering...RecruitingGyrate Atrophy | Gyrata of Choroid and Retina; Atrophy | Ornithine-δ-aminotransferase | OAT | Chorioretinal DegenerationUnited States, Canada, Finland, France, United Kingdom, Germany, Brazil
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AstraZenecaMerck Sharp & Dohme LLCRecruitingNeurofibromatosis Type 1United States, Spain, Germany, Russian Federation, Japan, Italy, Netherlands
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Kiora Pharmaceuticals, Inc.RecruitingRetinitis Pigmentosa | ChoroideremiaAustralia
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Sling Therapeutics, Inc.RecruitingEye Diseases | Endocrine System Diseases | Thyroid Diseases | Thyroid Eye Disease | Graves Ophthalmopathy | Exophthalmos | Orbital Diseases | Thyroid Associated Ophthalmopathy | Graves Orbitopathy | Proptosis | IGF1R | HashimotoUnited States, Spain, Canada, Italy, United Kingdom
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River 3 Renal Corp.RecruitingFocal Segmental Glomerulosclerosis | Alport SyndromeUnited States, Belgium, United Kingdom, France, Germany, Netherlands
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Novartis PharmaceuticalsRecruiting
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OcugenRecruitingRetinitis Pigmentosa | Leber Congenital AmaurosisUnited States
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Viridian Therapeutics, Inc.RecruitingThyroid Eye DiseaseSpain, United States, Netherlands, Germany, Canada, United Kingdom, Italy, Australia, France, Turkey
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Azienda Ospedaliero, Universitaria PisanaNot yet recruiting
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Abramson Cancer Center at Penn MedicineRecruitingBreast Cancer | Gastric Cancer | Cancer Gene MutationUnited States
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BioMarin PharmaceuticalRecruitingHereditary Angioedema | HAEUnited States, Spain, Australia
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Darcy KruegerRecruitingEpilepsy | Tuberous Sclerosis ComplexUnited States
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Tasly GeneNet Pharmaceuticals Co., LtdRecruitingCharcot-Marie-Tooth Type 1AChina
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Ionis Pharmaceuticals, Inc.RecruitingHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Italy, Portugal, Spain, Taiwan, Sweden, Canada, Brazil, France, New Zealand, Argentina, Cyprus, Australia, Turkey
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University of PisaUniversity of Messina; University of Catania; Università degli Studi dell'InsubriaNot yet recruiting
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Vigil Neuroscience, Inc.RecruitingALSPUnited States, Canada, Germany, Netherlands, United Kingdom
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Travere Therapeutics, Inc.RecruitingFocal Segmental Glomerulosclerosis | Immunoglobulin A Nephropathy | Minimal Change Disease | Alport Syndrome | IgA VasculitisUnited States, Italy, Netherlands, Poland, Spain, United Kingdom, Germany, Sweden
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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UNC Lineberger Comprehensive Cancer CenterUniversity of North Carolina, Chapel Hill; National Center for Advancing Translational... and other collaboratorsRecruitingLynch SyndromeUnited States
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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Centre d'Etude des Cellules SouchesGenethonRecruitingWolfram SyndromeFrance, Spain
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Shanghai Children's HospitalRecruitingAlport Syndrome, X-LinkedChina
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St. Jude Children's Research HospitalPfizer; IpsenRecruitingRefractory Malignant Solid Neoplasm | Recurrent Ewing Sarcoma | Recurrent Hepatoblastoma | Recurrent Malignant Germ Cell Tumor | Recurrent Malignant Solid Neoplasm | Recurrent Neuroblastoma | Recurrent Osteosarcoma | Recurrent Peripheral Primitive Neuroectodermal Tumor | Recurrent Rhabdoid Tumor | Recurrent... and other conditionsUnited States, Canada
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Palvella Therapeutics, Inc.RecruitingBCCs in Gorlin Syndrome PatientsUnited States, United Kingdom
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
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Ionis Pharmaceuticals, Inc.RecruitingAlexander DiseaseUnited States, United Kingdom, Australia, Canada, Israel, Italy, Japan, Netherlands
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Children's National Research InstituteRecruitingSoft Tissue Sarcoma | Ewing Sarcoma | Bone Metastases | Solid Tumors | Rhabdomyosarcoma | Wilms Tumor | Germ Cell Tumor | Hepatic Tumor | Malignant Epithelial NeoplasmUnited States
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Boston Children's HospitalCureAP4 FoundationRecruitingHereditary Spastic Paraplegia | SPG50 | SPG47 | SPG51 | SPG52 | AP4-related Hereditary Spastic Paraplegia | Early Onset Hereditary Spastic Paraplegia | SPG4 | SPG3A | SPG15 | SPG11United States
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Seoul National University HospitalRecruiting
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Centre Hospitalier National d'Ophtalmologie des...Assistance Publique - Hôpitaux de ParisRecruiting
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Columbia UniversityLudwig-Maximilians - University of Munich; Moorfields Eye Hospital NHS Foundation... and other collaboratorsRecruitingRetinitis Pigmentosa Associated With CNGB1 MutationsUnited States, France, Germany, United Kingdom
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Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated Amyloidosis | ATTR AmyloidosisIsrael, Italy, Netherlands, Spain, United States, France, Denmark, Germany, Portugal, Brazil, Taiwan
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AmgenRecruitingBehçet DiseaseSpain, United Kingdom, Turkey, France, Greece, Italy, Israel, Switzerland
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI); Oregon Health and Science UniversityRecruitingMalignant Solid Neoplasm | Lynch Syndrome | Hematopoietic and Lymphoid System Neoplasm | Breast Ductal Carcinoma In Situ | Hereditary Neoplastic Syndrome | BRCA1/2-Associated Hereditary Breast and Ovarian Cancer SyndromeUnited States
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University Hospital, Strasbourg, FranceRecruitingBardet-Biedl Syndrome | Alström SyndromeFrance
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Abramson Cancer Center at Penn MedicineFox Chase Cancer Center; Merck Sharp & Dohme LLC; AstraZeneca; Basser Center for...Recruiting
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingStage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Recurrent Kidney Wilms Tumor | Anaplastic Kidney Wilms TumorUnited States, Canada, Puerto Rico, Australia, New Zealand, Saudi Arabia
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Akcea TherapeuticsRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, Canada
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Assistance Publique - Hôpitaux de ParisMotion analysis laboratory, Garches; Fondation de GarchesRecruitingNeuromuscular Diseases | Charcot-Marie-Tooth Disease | HemiparesisFrance
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Cedars-Sinai Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Recruiting
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University of BaselNational Cancer Center, Korea; University Hospital, Geneva; Swiss National Science... and other collaboratorsRecruitingBreast Cancer | Ovarian Cancer | Hereditary CancerSwitzerland
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George ZogopoulosRecruitingPancreatic Cancer | Bile Duct Cancer | Pancreas Cancer | Gallbladder Cancer | Pancreas Neoplasm | Familial Pancreatic Cancer | Duodenal Cancer | Hereditary Cancer | Pancreas Cyst | Ampullary Cancer | Pancreatic Precancerous ConditionCanada
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Taproot HealthRecruitingMelanoma | Sarcoma | Kidney Cancer | Adenocarcinoma | Renal Cell Carcinoma | Cervical Cancer | Acute Myeloid Leukemia | Stomach Cancer | Breast Cancer | Head and Neck Neoplasms | Nasopharyngeal Carcinoma | Glioblastoma | Astrocytoma | Multiple Myeloma | Colorectal Cancer | Pancreatic Cancer | Esophageal Cancer | Small Bowel Cancer and other conditionsUnited States
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Novartis PharmaceuticalsRecruitingGlioblastoma | Astrocytoma | Anaplastic Astrocytoma | Neurofibromatosis Type 1 | Anaplastic Ganglioglioma | Anaplastic Pleomorphic Xanthoastrocytoma | Ganglioglioma | Pleomorphic Xanthoastrocytoma | Diffuse Astrocytoma | Anaplastic Oligodendroglioma | Pilocytic Astrocytoma | Gangliocytoma | Central Neurocytoma | Oligodendroglioma... and other conditionsUnited States, Belgium, Spain, Denmark, Germany, Czechia, Italy, Australia, Russian Federation, France, Netherlands, Japan, Canada, Finland, Sweden, United Kingdom, Argentina, Israel, Brazil
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Vanderbilt-Ingram Cancer CenterNational Cancer Institute (NCI)RecruitingCancer Survivor | Retinoblastoma | Unilateral Retinoblastoma | Intraocular Retinoblastoma | Biological SiblingUnited States, Canada