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Search clinical trials for: Homozygous Sitosterolemia
Total 130 results
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada
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Vertex Pharmaceuticals IncorporatedCompletedCystic Fibrosis, Homozygous or Heterozygous for the F508del-CFTR MutationUnited States, France, United Kingdom, Germany, Spain, Belgium, Canada, Australia, Netherlands, Denmark, Czech Republic, Italy, Austria, Ireland, Sweden
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Central South UniversityCompletedHomozygous Familial HypercholesterolemiaChina
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Nivalis Therapeutics, Inc.Medidata SolutionsCompletedCystic FibrosisUnited States
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Nivalis Therapeutics, Inc.CompletedCystic FibrosisUnited States
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Vertex Pharmaceuticals IncorporatedCompletedCystic Fibrosis, Homozygous for the F508del CFTR MutationUnited States, France, Spain, Belgium, Canada, Austria, Australia, Germany, United Kingdom, Denmark
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Canada, Brazil, Taiwan, Singapore, South Africa, United Kingdom
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Taiwan, Brazil, Canada, South Africa, United Kingdom, Singapore
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Israel, Netherlands, Taiwan, Belgium, Denmark
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CymaBay Therapeutics, Inc.CompletedHomozygous Familial HypercholesterolemiaCanada, France, Netherlands, Norway
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Laval UniversityCompletedHomozygous Familial HypercholesterolemiaCanada
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Charite University, Berlin, GermanyUnknownHomozygous or Compound Heterozygous POMC, LEPR or PCSK1 Gene MutationGermany
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, France, United Kingdom, Germany, Australia, New Zealand, Belgium
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Vertex Pharmaceuticals IncorporatedCystic Fibrosis FoundationTerminated
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Vertex Pharmaceuticals IncorporatedCompletedCystic Fibrosis, Homozygous for the F508del CFTR MutationUnited States, Germany, Canada, Netherlands, Czech Republic, Italy, Ireland, Sweden, United Kingdom, Australia, France
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Cerenis Therapeutics, SACompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Netherlands, United Kingdom
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The University of Hong KongCompletedHomozygous αº-thalassemia | Hb Bart's DiseaseChina
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Merck Sharp & Dohme LLCTerminatedHyperlipoproteinemia Type II | Homozygous Familial Hypercholesterolemia
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Nivalis Therapeutics, Inc.Completed
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Rennes University HospitalCompletedHereditary Hemochromatosis C282Y HomozygousFrance
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Boehringer IngelheimCompletedAsthmaAustria, Belgium, Denmark, Finland, France, Germany, Greece, Italy, Russian Federation, Slovakia, South Africa, Spain, Turkey, United Kingdom
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Aegerion Pharmaceuticals, Inc.University of Pennsylvania; Doris Duke Charitable FoundationCompletedHomozygous Familial HypercholesterolemiaUnited States
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TakedaTerminatedHypercholesterolemiaFrance, United Kingdom, United States, Israel, Poland, Canada
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HaEmek Medical Center, IsraelCompletedHgb C HemoglobinopathyIsrael
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Children's Hospital of PhiladelphiaNational Center for Research Resources (NCRR); Cystic Fibrosis FoundationCompleted
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University of TehranCompletedHypercholesterolemia, FamilialIran, Islamic Republic of
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National Center for Research Resources (NCRR)Medical University of South CarolinaCompleted
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Medical Research Laboratories InternationalTerminatedFamilial HypercholesterolemiaIsrael, Netherlands, United States, Canada, Norway