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Search clinical trials for: Human acid sphingomyelinase deficiency
Total 56516 results
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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Hannover Medical SchoolTerminatedDepression | Schizophrenia | Anxiety Disorders | Dementia | Psychosomatic DisordersGermany
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Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
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Assiut UniversityNot yet recruiting
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Chung-Hsing WangSanofiNot yet recruiting
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SanofiPulse Infoframe Ltd.RecruitingNiemann-Pick Diseases | Acid Sphingomyelinase DeficiencyUnited States
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National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States
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OctapharmaNot yet recruiting
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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Rhode Island HospitalRecruitingOpioid Use Disorder | Human Immunodeficiency VirusUnited States
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ViiV HealthcareNot yet recruitingHIV Infections | HIVSpain, Poland, France, Israel, Belgium, Portugal, Germany, Italy, Argentina, Greece, Japan, Ireland, Switzerland, United Kingdom, Denmark, Sweden, Mexico
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Eline C. B. EskesRecruitingAsmd, Visceral TypeNetherlands
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Fundación Española de Hematología y HemoterapíaRecruitingNiemann-Pick Diseases | Gaucher Disease | Splenomegaly | Acid SphingoMyelinase Deficiency | ASMDSpain
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Stellah MpagamaRadboud University Medical Center; University of St AndrewsRecruitingTuberculosis | Human Immunodeficiency VirusTanzania
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SanofiRecruitingAcid Sphingomyelinase Deficiency (ASMD)France
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Second Affiliated Hospital, School of Medicine,...RecruitingCardiac Surgery | Iron Deficiency Anemia | Patient Blood ManagementChina
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Montefiore Medical CenterNational Cancer Institute (NCI); University of Rwanda; Rwanda Military HospitalRecruitingCervical Cancer | Human Immunodeficiency Virus | HPV-Related Carcinoma | Human Papilloma VirusRwanda
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Merck Sharp & Dohme LLCNot yet recruitingHIV | Human Immunodeficiency Virus
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University of Massachusetts, WorcesterNational Institute of Allergy and Infectious Diseases (NIAID); Aurum Institute and other collaboratorsRecruitingTuberculosis | Pulmonary Tuberculosis | HIV CoinfectionSouth Africa
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SanofiRecruitingAcid SphingoMyelinase Deficiency | Gaucher Disease, SplenomegalyFrance
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Grifols Therapeutics LLCRecruiting
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Anna CrucetaRecruitingHIV Primary InfectionSpain
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingTuberculosis | Human Immunodeficiency Virus | CoinfectionGhana
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
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National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingHIV InfectionPuerto Rico, United States, Argentina, Brazil, South Africa, Uganda, Zambia, Haiti, Kenya, Malawi, Tanzania, Thailand, Zimbabwe
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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National Human Genome Research Institute (NHGRI)RecruitingPulmonary Fibrosis | Healthy Volunteers | Hermansky-Pudlak Syndrome (HPS)United States
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National Human Genome Research Institute (NHGRI)RecruitingHermansky-Pudlak Syndrome (HPS)United States
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ViiV HealthcareGlaxoSmithKline; Janssen PharmaceuticalsCompletedHIV Infections | Infection, Human Immunodeficiency VirusGermany, Spain, France, United States, Canada
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ViiV HealthcareGlaxoSmithKline; PPDActive, not recruitingHIV InfectionsUnited States, France, Germany, Canada, Spain, Italy, Argentina, Chile, Puerto Rico
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National Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Colon Mucinous Adenocarcinoma | Colon Signet Ring Cell Adenocarcinoma | Stage IIA Colon Cancer AJCC v7 | Stage IIB Colon Cancer AJCC v7 | Stage IIC Colon Cancer AJCC v7United States, Canada, Puerto Rico, Peru, South Africa
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ViiV HealthcareJanssen, LPCompletedHIV InfectionsUnited States, Netherlands, Germany, Canada, Australia, Belgium, France, Spain, Ireland, Italy, United Kingdom, Austria, Japan, Switzerland
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Janssen Sciences Ireland UCActive, not recruitingHuman Immunodeficiency Virus Type 1Portugal, South Africa, Thailand, Uganda, Spain
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Tuberculosis Research Centre, IndiaUnited States Agency for International Development (USAID)CompletedTuberculosis | Human Immunodeficiency VirusIndia
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Chelsea and Westminster NHS Foundation TrustGilead Sciences; Imperial College LondonTerminatedHuman Immunodeficiency VirusUnited Kingdom
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University College DublinViiV Healthcare; Mater Misericordiae University HospitalTerminatedHuman Immunodeficiency VirusIreland
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University of WashingtonBill and Melinda Gates FoundationCompletedHIV InfectionsKenya, Malawi, South Africa, Swaziland, Uganda, Zambia, Zimbabwe
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University College, LondonLondon School of Hygiene and Tropical Medicine; MRC/UVRI and LSHTM Uganda Research... and other collaboratorsActive, not recruitingHIV Infections | Hiv | HIV-1-infection | Paediatric Human Immunodeficiency Virus InfectionUganda, Zimbabwe, Kenya, South Africa
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Emory UniversityCenters for Disease Control and PreventionCompleted
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Gritstone bio, Inc.Completed
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Grifols Therapeutics LLCActive, not recruitingPulmonary Emphysema in Alpha-1 PI DeficiencyUnited States, Australia, Denmark, New Zealand, Estonia, Poland, Russian Federation, Sweden, Brazil, Canada, France, Finland
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Merck Sharp & Dohme LLCActive, not recruitingHIV InfectionUnited States, Australia, Austria, Canada, Finland, France, Germany, Italy, Japan, Puerto Rico, Spain
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ViiV HealthcareGlaxoSmithKlineCompletedHIV Infections | Infection, Human Immunodeficiency VirusUnited States, France, Spain, United Kingdom, Canada, Thailand, Italy, Portugal, Russian Federation, Mexico, Argentina, South Africa, Puerto Rico
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ViiV HealthcareGlaxoSmithKline; Janssen PharmaceuticalsActive, not recruitingHIV Infections | Infection, Human Immunodeficiency VirusGermany, Spain, France, United States, Canada, Australia, Korea, Republic of, Italy, South Africa, Russian Federation, Argentina, Mexico, Sweden
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Swiss Federal Institute of TechnologyCompletedIron-deficiency | Iron Deficiency AnemiaSwitzerland
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ViiV HealthcareJanssen Research and DevelopmentActive, not recruitingHIV InfectionsUnited States, Germany, Spain, France, Canada, Korea, Republic of, Italy, South Africa, Australia, Russian Federation, Mexico, Sweden, Argentina
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Gilead SciencesActive, not recruitingPre-Exposure Prophylaxis of HIV InfectionUnited States, Thailand, Brazil, Peru, Argentina, South Africa, Mexico, Puerto Rico
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ViiV HealthcareGlaxoSmithKline; Janssen PharmaceuticalsCompletedHuman Immunodeficiency Virus Type 1 (HIV-1)United States, Spain, Canada, United Kingdom, South Africa, Japan