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Search clinical trials for: LCHAD Deficiency
Total 9681 results
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Ultragenyx Pharmaceutical IncRecruitingLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)Turkey, United Kingdom, Spain, Saudi Arabia, Poland, Czechia, Germany
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Ultragenyx Pharmaceutical IncRecruitingLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States, Canada
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Ultragenyx Pharmaceutical IncCompletedCarnitine Palmitoyltransferase (CPT I or CPT II) Deficiency | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Long-chain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine-acylcarnitine Translocase (CACT) DeficiencyUnited States, United Kingdom
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Ultragenyx Pharmaceutical IncTerminatedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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Ultragenyx Pharmaceutical IncCompletedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD) | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine Palmitoyltransferase (CPT II) Deficiency | Longchain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) DeficiencyUnited States, United Kingdom
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Oregon Health and Science UniversityUniversity of PittsburghCompletedVery Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase 2 (CPT2) Deficiency | Mitochondrial Trifunctional Protein (TFP) Deficiency | Long-chain 3 hydroxyacylCoA Dehydrogenase (LCHAD) DeficiencyUnited States
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Oregon Health and Science UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Oregon...TerminatedPeripheral Neuropathy | Mitochondrial Trifunctional Protein DeficiencyUnited States
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China-Japan Friendship HospitalRecruiting
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University of North Carolina, Chapel HillNorth Carolina Translational and Clinical Sciences InstituteNot yet recruitingColorectal Cancer | Rectal Cancer | Rectal Neoplasms | Colon Cancer | Colon Adenocarcinoma | Colon Rectal Cancer | Hereditary Nonpolyposis Colon CancerUnited States
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Cairo UniversityNot yet recruitingHeart Failure With Reduced Ejection Fraction
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University of UlsterNorthern Health & Social Care Trust (NHSCT); Solvotrin Therapeutics - Active...Not yet recruitingIron Deficiency Anemia of PregnancyUnited Kingdom
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Uppsala UniversityUniversity of Turku; Bielefeld University; Vivo international e.V.; The Swedish... and other collaboratorsNot yet recruitingMalnutrition | Psychological Distress | Mental Health | Malnutrition, Child | Dietary Deficiency
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Belgian Research on AIDS and HIV ConsortiumNot yet recruitingHuman Immunodeficiency Virus
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Hospital Universitario 12 de OctubreNot yet recruitingShock | Vasopressor Adverse Reaction | Vasopressin Causing Adverse Effects in Therapeutic Use | Vasopressin DeficiencySpain
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Rocket Pharmaceuticals Inc.Not yet recruitingPyruvate Kinase DeficiencySpain, United States
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King's College Hospital NHS TrustChiesi LimitedNot yet recruitingRespiratory Distress Syndrome | Surfactant Deficiency Syndrome Neonatal | Preterm Pregnancy
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ANRS, Emerging Infectious DiseasesNot yet recruiting
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Fundacja NutriciaInstitute of Mother and Child, Warsaw, PolandNot yet recruitingChild | Nutritional Status | Children | Dietary Habits | Consumption | Diet, Healthy | Diet Habit | Nutritional Deficiency | Cross-sectional Study | Dietary Assessment | Macronutrients
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IRCCS Ospedale San RaffaeleNot yet recruitingRare Diseases | Corneal Neovascularization | Limbal Stem Cell Deficiency | Aniridia | Neurotrophic Keratopathy | Ocular Cicatricial Pemphigoid | Ocular Graft-versus-host Disease | EEC Syndrome
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Raydiant Oximetry, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingOxygen Deficiency | Fetal Complications | Fetal Hypoxia | Fetal Conditions | Fetal Distress | Labor (Obstetrics)--Complications | Labor Fetal AnoxiaUnited States
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Johns Hopkins UniversityNational Institutes of Health (NIH); Desmond Tutu HIV FoundationNot yet recruitingHuman Immunodeficiency Virus | Emergency Department | Pre-Exposure Prophylaxis | South Africa
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Wave Life Sciences Ltd.Not yet recruiting
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University of ZurichSwiss HIV Cohort StudyRecruiting
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Dr. Lutfi Kirdar Kartal Training and Research HospitalRecruiting
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Yonsei UniversityRecruitingCoronary Artery Bypass, Off-Pump | Iron DeficienciesKorea, Republic of
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Maastricht University Medical CenterNot yet recruitingProtein-Energy Malnutrition | Nutrition PoorNetherlands
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Policlinico HospitalRecruitingTransplantation | Ascorbic Acid DeficiencyItaly
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Vanderbilt University Medical CenterAminu Kano Teaching HospitalNot yet recruitingMalnutrition | Sickle Cell Disease
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United States Army Research Institute of Environmental...RecruitingEnergy Supply; DeficiencyUnited States
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First People's Hospital of HangzhouRecruitingColorectal Cancer | Cancer-Related FatigueChina
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MetroHealth Medical CenterKent State UniversityNot yet recruiting
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Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
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Mayo ClinicRecruiting
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Changchun GeneScience Pharmaceutical Co., Ltd.Not yet recruitingPediatric Growth Hormone Deficiency (PGHD)China
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Shanghai Hutchison Pharmaceuticals LimitedRecruitingCervical Spondylotic MyelopathyChina
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Privatpraxis für Knie- und SchulterchirurgieRecruiting
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L-Nutra IncUniversity of Tennessee Medical CenterRecruitingChemotherapy Effect | Fasting, Intermittent | Cancer, Ovarian | Calorie DeficiencyUnited States
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Liaquat University of Medical & Health SciencesNot yet recruitingVitamin B 12 DeficiencyPakistan
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University of Missouri-ColumbiaGilead SciencesRecruitingHIV Infections | ART | Noncompliance, PatientUnited States
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McGill University Health Centre/Research Institute...Not yet recruiting
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Cairo UniversityNot yet recruitingDental Caries | Vitamin Deficiency
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Apollo Therapeutics LtdNot yet recruitingMyelodysplastic Syndrome With Excess Blasts | Acute Myeloid Leukemia, in Relapse | Acute Myeloid Leukemia Refractory | Myelodysplastic Syndrome Acute Myeloid Leukemia
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Milton S. Hershey Medical CenterNot yet recruitingCardiovascular Diseases | Postmenopausal Symptoms
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University of StellenboschUniversity College London Hospitals; University of Copenhagen; Imperial College... and other collaboratorsNot yet recruiting
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Linnaeus UniversityWorld Anti-Doping Agency; Swedish Research Council for Sport Science; Swedish...RecruitingEating Disorders | RED SSweden
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University of California, Los AngelesUniversity of North Carolina, Chapel Hill; University of California, Irvine; Florida... and other collaboratorsRecruitingHIV InfectionsUnited States
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bioLytical LaboratoriesNot yet recruitingHuman Immunodeficiency Virus I Infection | Human Immunodeficiency Virus II Infection
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ViiV HealthcareRecruiting
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The Cooper Health SystemWon Sook Chung FoundationNot yet recruitingVitamin D Deficiency