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Search clinical trials for: Late Infantile Neuronal Lipofuscinosis
Total 12652 results
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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BioMarin PharmaceuticalActive, not recruitingLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2United States
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky Disease | CLN2 DisorderUnited States, Germany, Italy, United Kingdom
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky Disease | CLN2 DisorderUnited States, Germany, Italy, United Kingdom
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Amicus TherapeuticsTerminatedBatten Disease | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3United States
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Amicus TherapeuticsCompletedVariant Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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REGENXBIO Inc.WithdrawnLate-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2)
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH)CompletedBatten Disease | Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky DiseaseUnited States, Italy, Germany, United Kingdom
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late-Infantile Neuronal Ceroid Lipfuscinosis
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Weill Medical College of Cornell UniversityTerminatedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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StemCells, Inc.CompletedNeuronal Ceroid LipofuscinosisUnited States
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New York Stem Cell Foundation Research InstituteRecruitingPTSD | Multiple Sclerosis | Cervical Cancer | Diabetes Mellitus, Type 2 | Diabetes Mellitus | Diabetes | Macular Degeneration | Diabetes Mellitus, Type 1 | Parkinson Disease | Amyotrophic Lateral Sclerosis | Dementia | Ovarian Cancer | Alzheimer Disease | ALS | Vulvar Cancer | Post Traumatic Stress Disorder | Lewy Body Disease and other conditionsUnited States
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Universitätsklinikum Hamburg-EppendorfRecruitingBatten Disease | Neuronal Ceroid Lipofuscinosis | CLN1 Disease | CLN2 Disease | CLN3 Disease | CLN4 Disease | CLN5 Disease | CLN6 Disease | CLN7 Disease | CLN8 Disease | CLN10 Disease | CLN11 Disease | CLN12 Disease | CLN13 Disease | CLN14 DiseaseGermany
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Eunice Kennedy Shriver National Institute of Child...CompletedInfantile Neronal Ceroid LipofuscinosisUnited States
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Azienda Ospedaliera di BolzanoRecruitingSyncope | Asystole | Pacemaker | Neurally Mediated SyncopeItaly
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Casa Sollievo della Sofferenza IRCCSMinistry of Health, ItalyRecruitingAmyotrophic Lateral SclerosisItaly
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Boston University Charles River CampusMassachusetts Institute of TechnologyNot yet recruitingChildhood DepressionUnited States
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Queen Fabiola Children's University HospitalThe Belgian Kids Fund; Fonds IRIS-Recherche; Ars StatisticaRecruitingSepsis | Premature Birth | Jaundice | Respiratory Distress Syndrome in Premature Infant | Intraventricular Hemorrhage of Prematurity | BronchodysplasiaBelgium
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University Hospital, LimogesNational Research Agency, France; Institut du Cerveau et de la Moelle épinière and other collaboratorsNot yet recruitingAmyotrophic Lateral SclerosisFrance
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Leigh R. Hochberg, MD, PhD.National Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Dysarthria | Brain Stem Infarctions | Locked-in Syndrome | AnarthriaUnited States
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Bursa City HospitalRecruitingRespiratory Distress Syndrome | Lung Ultrasonography ScoreTurkey
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Ministry of Health, Saudi ArabiaNot yet recruitingRespiratory Disease | Prematurity | Ventilator Lung; Newborn
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Universitätsklinikum Hamburg-EppendorfRecruitingAutism Spectrum DisorderGermany
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University of CologneRecruitingPreterm Birth | Infant Development | Mother-Infant InteractionGermany
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Chulalongkorn UniversityRecruitingPreterm Birth | Respiratory Distress of NewbornVietnam
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Forge Biologics, IncRecruitingKrabbe DiseaseUnited States
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Ana Maria LinaresUniversity of KentuckyRecruiting
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Leigh R. Hochberg, MD, PhD.National Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Dysarthria | Brain Stem Infarctions | Locked in Syndrome | AnarthriaUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingNiemann-Pick Disease Type C1 | Juvenile Neuronal Ceroid Lipofuscinosis | Smith-Lemli-Opitz Syndrome | Creatine Transporter DeficiencyUnited States
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Franciscus GasthuisChiesi Farmaceutici S.p.A.; Revenio Research; Stichting BeterKetenRecruitingSmoking Cessation | Respiratory Tract Infections | Premature Birth | Preterm Birth | Telemedicine | Bronchopulmonary Dysplasia | Respiratory Disease | RSV Infection | Pollution; Exposure | Health-Related Behavior | eHealth | Bronchial Hyperreactivity | Pollution Related Respiratory Disorder | RSV PneumoniaNetherlands
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St. Jude Children's Research HospitalRecruitingMedulloblastomaUnited States
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Masaryk UniversitySt. Anne's University Hospital Brno, Czech RepublicRecruiting
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VA Office of Research and DevelopmentNot yet recruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Cord Injury | Brain Stem Infarctions | Locked-in SyndromeUnited States
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University of PennsylvaniaNational Heart, Lung, and Blood Institute (NHLBI)RecruitingDeath | Bronchopulmonary Dysplasia | Extubation FailureUnited States, Canada
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University Hospitals Coventry and Warwickshire...RecruitingNervous System Diseases | Neuromuscular Diseases | Respiratory Failure | Respiratory Insufficiency | Amyotrophic Lateral Sclerosis | Sleep-Disordered Breathing | Neuro-Degenerative Disease | Neuron Disease, MotorUnited Kingdom
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Cedars-Sinai Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Recruiting
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Neurogene Inc.RecruitingNeuronal Ceroid Lipofuscinosis CLN5United States, United Kingdom
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University of Erlangen-Nürnberg Medical SchoolRecruitingPompe Disease (Late-onset) | Pompe Disease | Pompe's Disease Juvenile Onset | Pompe Disease Infantile-OnsetGermany
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National Human Genome Research Institute (NHGRI)RecruitingDiabetes | Undiagnosed Diseases | Inherited Metabolic Disorders | Batten's Disease | Tay SachsUnited States
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Boston CollegeBeth Israel Deaconess Medical Center; University of North Carolina, Chapel...RecruitingInfant, Premature, Diseases | Feeding, Bottle | Behavior, InfantUnited States
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St. Jude Children's Research HospitalSpringWorks Therapeutics, Inc.RecruitingLow-Grade Glioma | Recurrent Low-Grade Glioma | Progressive Low-Grade GliomaUnited States
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Assiut UniversityNot yet recruitingNutrition Disorder, Child
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VENTO GIOVANNIRecruitingBronchopulmonary Dysplasia | Chronic Pulmonary Insufficiency of PrematurityItaly
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Children's Hospital of PhiladelphiaRhode Island Hospital; Children's Miracle Network; American Respiratory Care...RecruitingBronchopulmonary Dysplasia | Mechanical Ventilation | Neurally Adjusted Ventilatory AssistUnited States
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Kantonsspital AarauRecruiting
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University of BernRecruitingChildhood Cancer | Late EffectSwitzerland