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Search clinical trials for: Mucopolysaccharidosis IVA Type A
Total 494786 results
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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Hospital de Clinicas de Porto AlegreThe Isaac FoundationActive, not recruitingMucopolysaccharidoses | Mucopolysaccharidosis VI | Morquio A Syndrome | Mucopolysaccharidosis IV A | MPS IV A | MPS VI | MPS - Mucopolysaccharidosis | Morquio Syndrome A | Morquio SyndromeBrazil
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVATaiwan, United States, Italy, United Kingdom
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalWithdrawnMucopolysaccharidosis IV | Morquio A DiseaseUnited Kingdom
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, United Kingdom, Canada, Germany
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited Kingdom, United States, Germany
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IV A | Mucopolysaccharidosis IVAUnited Kingdom
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IV A | Mucopolysaccharidosis IVAFrance, United Kingdom, Taiwan, United States, Argentina, Netherlands, Canada, Brazil, Germany, Italy
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Emory UniversityBioMarin PharmaceuticalTerminatedMucopolysaccharidosis Type IVAUnited States
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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BioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
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Novo Nordisk A/SNot yet recruitingAlcohol-related Liver DiseaseSpain, Denmark, United States, Australia, Canada, Netherlands, Italy, Bulgaria, Czechia, Germany, Greece, France, Japan, Poland
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Mayo ClinicNot yet recruitingLocalized Prostate Carcinoma | Stage I Prostate Cancer AJCC v8 | Stage II Prostate Cancer AJCC v8 | Stage III Prostate Cancer AJCC v8 | Stage IVA Prostate Cancer AJCC v8 | Oligometastatic Prostate CarcinomaUnited States
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Weill Medical College of Cornell UniversityCurium US LLCNot yet recruiting
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Veerle SnijdersCroatian Institute of Public Health; Andrija Štampar School of Public HealthRecruitingColorectal Cancer | Behavior ChangeCroatia
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BiocadRecruitingMultiple MyelomaRussian Federation
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GlaxoSmithKlineNot yet recruitingNeoplasms, Head and NeckUnited States, Taiwan, Mexico, Belgium, Sweden, Australia, Germany, Canada, Japan, Norway, Portugal, Turkey, United Kingdom, Korea, Republic of, Argentina, Italy, Poland, Romania, Czechia, Hungary, Brazil, France, Greece
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Castilla-La Mancha Health ServiceRecruiting
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis Type IIIAUnited States
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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University Health Network, TorontoNot yet recruitingArteriovenous Malformations
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Fujian Cancer HospitalNot yet recruitingNasopharyngeal CarcinomaChina
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis III-AGermany
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University of Texas Southwestern Medical CenterRecruitingRenal Cell Carcinoma | Renal Tumor | Renal Tumor, BenignUnited States
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University Hospital OstravaNot yet recruitingCardiovascular Diseases | Heart Failure With Reduced Ejection FractionCzechia
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Tang-Du HospitalRecruitingChemotherapy | Esophageal Squamous Cell Carcinoma | PD-1 Inhibitor | NeoadjuventChina
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Instituto Tecnologico de SonoraNational Council of Science and Technology, MexicoNot yet recruitingCardiovascular Diseases | Diabetes Mellitus, Type 2Mexico
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Castilla-La Mancha Health ServiceRecruiting
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Jiangsu Cancer Institute & HospitalNot yet recruitingStage IVA Nasopharyngeal CarcinomaChina
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University of California, San FranciscoRecruiting
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National Cancer Institute (NCI)RecruitingGastric Adenocarcinoma | Clinical Stage III Gastric Cancer AJCC v8 | Clinical Stage III Gastroesophageal Junction Adenocarcinoma AJCC v8 | Gastroesophageal Junction Adenocarcinoma | Clinical Stage I Gastric Cancer AJCC v8 | Clinical Stage II Gastric Cancer AJCC v8 | Clinical Stage IVA Gastric... and other conditionsUnited States
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Sun Yat-sen UniversityRecruiting
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudNot yet recruitingSanfilippo Syndrome Type CUnited States, France
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Bristol-Myers SquibbRecruitingMultiple MyelomaCanada, Taiwan, United States, Australia, Denmark, China, Korea, Republic of, Israel, Spain, France, Germany, Czechia, Austria, Japan, Sweden, United Kingdom, Greece, Italy, Finland, Argentina, Belgium, Brazil, Colombia, Hong Kong, India, Mexic... and more
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Sidney Kimmel Comprehensive Cancer Center at Johns...Incyte CorporationRecruitingMyelodysplastic Syndromes | Myeloproliferative Disorders | Multiple Myeloma | Plasma Cell Leukemia | CML | T-cell Prolymphocytic Leukemia | Leukemia, Acute | Myelomonocytic Leukemia, ChronicUnited States
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BiocadRecruitingMelanoma (Skin) | Melanoma Stage IIIRussian Federation, Belarus
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BiocadRecruitingMelanoma | Melanoma (Skin) | Melanoma Stage IV | Melanoma Stage III | Melanoma Metastatic | Melanoma Unresectable | Melanoma AdvancedIndia, Russian Federation, Belarus
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingMalignant Solid Neoplasm | Recurrent Prostate Carcinoma | Localized Prostate Carcinoma | Stage I Prostate Cancer AJCC v8 | Stage II Prostate Cancer AJCC v8 | Stage IIA Cervical Cancer FIGO 2018 | Stage IIB Cervical Cancer FIGO 2018 | Stage IIIA Cervical Cancer FIGO 2018 | Stage IIIB Cervical Cancer... and other conditionsUnited States
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University Hospital, AntwerpErasmus Medical Center; ZonMw: The Netherlands Organisation for Health Research... and other collaboratorsRecruitingGastroenteropancreatic Neuroendocrine TumorNetherlands, Belgium
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Jena University HospitalBayerRecruitingMetastatic Hormone-Sensitive Prostate Cancer (mHSPC)Germany
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Universitätsklinikum Hamburg-EppendorfGemeinsamer Bundesausschuss (G-BA); Staburo GmbHRecruiting
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Novo Nordisk A/SRecruitingCardiovascular DiseaseNetherlands, Australia, Italy, United States, Serbia, Spain, United Kingdom, Thailand, India, Malaysia, Turkey, Mexico, Canada, Argentina, Germany, France, Poland, South Africa, Brazil, Bulgaria, Colombia, Denmark, Ireland, Japan
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AIDS Malignancy ConsortiumNational Cancer Institute (NCI)RecruitingHIV Infection | Hematopoietic and Lymphoid Cell Neoplasm | Malignant Solid Neoplasm | Lymphoma | Multicentric Castleman Disease | Plasmablastic Lymphoma | Kaposi Sarcoma | Recurrent Lymphoma | Anal Carcinoma | Recurrent Kaposi Sarcoma | Recurrent Plasmablastic Lymphoma | Transplant-Related Kaposi SarcomaUnited States
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SLK Kliniken Heilbronn GmbHRecruitingAdvanced Renal Cell CarcinomaGermany