Search clinical trials for: Orphan Diseases
Total 373053 results
-
Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedHemophilia BUnited States, United Kingdom, South Africa, Netherlands, Ireland, Australia
-
Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumTerminatedHemophilia A | Hemophilia BUnited States
-
Bioverativ Therapeutics Inc.Swedish Orphan Biovitrum; Syntonix Pharmaceuticals, Inc.Completed
-
Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedSevere Hemophilia BSweden, United States, France, Italy, Russian Federation, United Kingdom, Germany, China, Poland, Japan, Australia, Brazil, Canada, India, South Africa, Hong Kong, Belgium
-
PharmaxisCompletedCystic FibrosisUnited States, Spain, Israel, Belgium, Czechia, South Africa, Italy, Mexico, Argentina, Australia, Canada, Hungary, New Zealand, Poland, Romania, Russian Federation, Slovakia, Ukraine
-
PTC TherapeuticsCystic Fibrosis FoundationCompletedCystic FibrosisUnited States, France, Belgium, Spain, Canada, Germany, Israel, Italy, Netherlands, Sweden, United Kingdom
-
Elizabeth Glaser Pediatric AIDS FoundationTanzania Ministry of Health, Community Development, Gender, Elderly and Children and other collaboratorsCompletedPediatric HIV InfectionTanzania
-
Swedish Orphan BiovitrumCompletedAcute Gouty ArthritisUnited States
-
Dr. Schär AG / SPACompletedFatty Acid Oxidation DisorderRussian Federation
-
PTC TherapeuticsCystic Fibrosis FoundationCompletedCystic FibrosisUnited States, France, Belgium, United Kingdom, Spain, Canada, Germany, Israel, Italy, Netherlands, Sweden
-
Johns Hopkins Bloomberg School of Public HealthCompletedEarly Childhood Development (ECD)
-
University of HoustonMichigan State University; Bar-Ilan University, Israel; University of the Free...CompletedHIV Affected Children (Single and/or Double Orphans)South Africa
-
Swedish Orphan BiovitrumPediatric Rheumatology International Trials OrganizationCompletedCryopyrin-Associated Periodic SyndromesUnited Kingdom, Netherlands
-
Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Austria, Czechia, Finland, Hungary, Ireland, Italy, Netherlands, Norway, Poland, Portugal, Spain, Sweden, United Kingdom
-
RedHill Biopharma LimitedMedical University of South Carolina; National Cancer Institute (NCI); FDA Office... and other collaboratorsCompletedPancreatic Cancer | Unspecified Adult Solid Tumor, Protocol SpecificUnited States
-
Cairo UniversityUnknownGingival Disease Due to Bacteria
-
Swedish Orphan BiovitrumCompletedStill Disease, Juvenile OnsetItaly
-
Imperial College LondonWellcome Trust; World Bank; Biomedical Research and Training Institute; UNICEF; Catholic...CompletedEducation | Vaccination | Birth Registration | Financial SupportZimbabwe
-
Assistance Publique - Hôpitaux de ParisSwedish Orphan BiovitrumCompleted
-
Cerenis Therapeutics, SATerminatedFamilial HypoalphalipoproteinemiaFrance, United States, Belgium, Canada, Israel, Italy, Netherlands
-
Symphogen A/SSwedish Orphan BiovitrumCompletedImmune Thrombocytopenic PurpuraUnited States, Belgium, Germany, India, Israel, Poland, Romania, Russian Federation, Serbia, Spain, Ukraine, United Kingdom
-
University of Texas Southwestern Medical CenterFDA Office of Orphan Products DevelopmentCompleted
-
Arbeitsgemeinschaft medikamentoese TumortherapieAOP Orphan Pharmaceuticals AGCompletedChronic Phase Chronic Myeloid LeukemiaAustria
-
Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedPoverty | Orphaned Children | AIDS OrphansUganda
-
Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, United Kingdom, Belgium, Italy, Netherlands
-
Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, Netherlands
-
Medical University of South CarolinaMerck Sharp & Dohme LLC; FDA Office of Orphan Products DevelopmentCompletedFractures | Juvenile Osteoporosis | Low Bone DensityUnited States
-
Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
-
Horizon Pharma USA, Inc.Completed
-
AOP Orphan Pharmaceuticals AGCompletedPolycythemia VeraAustria
-
Johns Hopkins UniversityGenentech, Inc.; FDA Office of Orphan Products DevelopmentCompletedIntraventricular HemorrhageUnited States, Germany, Canada, United Kingdom
-
Assistance Publique - Hôpitaux de ParisCompleted
-
Pacific Institute for Research and EvaluationNational Institute of Mental Health (NIMH); University of North Carolina, Chapel... and other collaboratorsCompletedHIVUnited States, Kenya
-
University of FloridaFood and Drug Administration (FDA); FDA Office of Orphan Products DevelopmentCompletedMitochondrial DiseasesUnited States, Canada
-
AdventHealthSagent Pharmaceuticals Inc.CompletedUnilateral Knee ArthroplastyUnited States
-
Swedish Orphan BiovitrumCompleted
-
University of FloridaNo longer availableMitochondrial Enzyme DeficienciesUnited States
-
Swedish Orphan BiovitrumAmgenCompleted
-
George BrewerFDA Office of Orphan Products DevelopmentCompletedPrimary Biliary CirrhosisUnited States
-
Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, Netherlands
-
Horizon Pharma USA, Inc.Completed
-
GlaxoSmithKlineCompleted
-
NeuroHealing Pharmaceuticals Inc.FDA Office of Orphan Products DevelopmentSuspended
-
Swedish Orphan BiovitrumAmgenCompletedNon-Small Cell Lung Cancer | Lung Cancer | Dysphagia
-
Tulane University School of Social WorkUnited States Agency for International Development (USAID)CompletedStress, Psychological | Adolescent Behavior | Risk Reduction Behavior
-
Tulane University School of Social WorkUnited States Agency for International Development (USAID)Completed
-
Children's Hospital of PhiladelphiaMedical University of South Carolina; FDA Office of Orphan Products DevelopmentCompleted
-
Jazz PharmaceuticalsFDA Office of Orphan Products DevelopmentCompletedSevere Hepatic Veno-Occlusive DiseaseUnited States, Canada
-
Brett KingSwedish Orphan BiovitrumTerminatedStevens-Johnson Syndrome | Toxic Epidermal NecrolysisUnited States
-
AOP Orphan Pharmaceuticals AGPharmaEssentia (Co-Sponsor for USA)CompletedPolycythemia VeraSpain, Belgium, Austria, Italy, Bulgaria, Czech Republic, France, Germany, Hungary, Poland, Romania, Russian Federation, Slovakia, Ukraine