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- US Clinical Trials Registry
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Search clinical trials for: Orphan Diseases
Total 373053 results
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); FDA Office of Orphan Products DevelopmentCompletedLeukemia | Chronic Lymphocytic LeukemiaUnited States
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Swedish Orphan BiovitrumAmgenCompletedHead and Neck Cancer | Mucositis | Stomatitis | Solid Tumors | Squamous Cell Carcinoma
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Assistance Publique Hopitaux De MarseilleUnknownMeningo-encephalitis | Community-based MeningitisFrance
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AmgenCompleted
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AOP Orphan Pharmaceuticals AGCompletedEssential ThrombocythaemiaPoland, Slovakia, Bulgaria, Russian Federation, Romania, Croatia, Lithuania, Austria, Ukraine
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Zuzana Zbožínková, M.Sc.Boehringer IngelheimCompletedChronic Obstructive Pulmonary DiseaseLatvia, Croatia, Austria, Bulgaria, Czech Republic, Hungary, Poland, Russian Federation, Serbia, Slovakia, Slovenia
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BFrance, Germany, Italy, Spain, Sweden, Belgium, United Kingdom
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AOP Orphan Pharmaceuticals AGPharmaEssentia Corporation (Co-Sponsor for USA)CompletedPolycythemia VeraAustria, Bulgaria, Czech Republic, France, Hungary, Poland, Slovakia, Ukraine
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University of California, San FranciscoFDA Office of Orphan Products DevelopmentCompleted
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Januario Castro, M.D.FDA Office of Orphan Products Development; Memgen, LLCTerminatedChronic Lymphocytic Leukemia | Small Lymphocytic LymphomaUnited States
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Swedish Orphan BiovitrumCompletedEfficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 (HT-1)Hereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Sweden
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Saglik Bilimleri Universitesi Gulhane Tip FakultesiCompletedFamilial Mediterranean FeverTurkey
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AOP Orphan Pharmaceuticals AGCompletedEssential ThrombocythemiaAustria, Bulgaria, Lithuania, Poland, Russian Federation
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University of California, San FranciscoFDA Office of Orphan Products DevelopmentTerminatedPersistent Corneal Epithelial Defects
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Children's Hospital Los AngelesCompletedThrombosis | Heparin-induced ThrombocytopeniaUnited States
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Mayo ClinicUniversity of Florida; Orphan MedicalCompleted
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Emory UniversityTerminated
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Case Western Reserve UniversityTerminated
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); FDA Office of Orphan Products... and other collaboratorsCompletedMarfan SyndromeUnited States, Canada, Belgium
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Swedish Orphan BiovitrumCompletedMultiple MyelomaGermany
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FDA Office of Orphan Products DevelopmentBezoloven, Inc.WithdrawnVitamin D Deficiency | Lead PoisoningUnited States
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University of ChicagoCompleted
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Columbia UniversityCompletedOsteoporosisUnited States
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Children's Hospital Medical Center, CincinnatiCompleted
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Retina Foundation of the SouthwestCompleted
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University of PittsburghCompletedSezary Syndrome | Cutaneous T-cell LymphomaUnited States
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FDA Office of Orphan Products DevelopmentUniversity of UtahCompleted
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University of ChicagoCompleted
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FDA Office of Orphan Products DevelopmentCompletedGuillain-Barre SyndromeUnited States
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University of IowaCompletedLymphatic MalformationsUnited States
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FDA Office of Orphan Products DevelopmentUniversity of North CarolinaCompleted
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University of CincinnatiChildren's Hospital Medical Center, CincinnatiTerminatedAdrenoleukodystrophy | Zellweger Syndrome | Infantile Refsum's Disease | Bifunctional Enzyme Deficiency
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Children's Hospital Medical Center, CincinnatiCompletedCystic FibrosisUnited States, Italy
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University of TexasCompleted
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FDA Office of Orphan Products DevelopmentMedical University of South CarolinaCompleted
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityCompleted
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The Cleveland ClinicCompleted
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Northwestern UniversityTerminated
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FDA Office of Orphan Products DevelopmentBoston Children's HospitalCompleted
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University of TexasCompletedAcute Renal FailureUnited States
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FDA Office of Orphan Products DevelopmentCompletedPneumonia | Bronchiolitis Obliterans | Respiratory Distress Syndrome, AdultUnited States
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University of PittsburghCompletedMycosis Fungoides | Sezary Syndrome | Cutaneous T-cell LymphomaUnited States
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California Department of Health ServicesCompletedBotulism | Infant BotulismUnited States
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FDA Office of Orphan Products DevelopmentSt. Luke's-Roosevelt Hospital CenterCompletedErythropoietic Protoporphyria
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Medical College of Hampton RoadsEastern Virginia Medical SchoolCompletedCorneal NeovascularizationUnited States
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Children's Hospital of PhiladelphiaCompleted
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University of WashingtonCompleted
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Johns Hopkins UniversityCompletedEpilepsy | Cysticercosis
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Children's Hospital of PhiladelphiaCompleted
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Point TherapeuticsCompletedChronic Lymphocytic LeukemiaUnited States