Search clinical trials for: Orphan Diseases

Total 372923 results

AOP Orphan Pharmaceuticals AG

Completed

Lancovutide (Moli1901) Inhalation Solution Study in Adolescents and Adults With Cystic Fibrosis

Cystic Fibrosis

Austria
Swedish Orphan Biovitrum
Amgen

Withdrawn

A Study of Palifermin for the Reduction of Oral Mucositis in Subjects With Locally Advanced Head and Neck Cancer Receiving Postoperative Radiotherapy

Head and Neck Cancer
PTC Therapeutics
Cystic Fibrosis Foundation; FDA Office of Orphan Products Development

Completed

PTC124 for Cystic Fibrosis

Cystic Fibrosis

United States
Medical University of Lodz
Ministry of Science and Higher Education, Poland

Completed

Markers of Atopy in Children With Presumed Early Exposure to Allergens, Unhygienic Conditions, and Infections

Atopic Diseases

Poland
University Hospital, Strasbourg, France

Completed

Bardet-Biedl Syndrome Study: Clinical and Genetic Epidemiology Study in Adults

Bardet-Biedl Syndrome | Orphan Diseases

France
National Institute of Arthritis and Musculoskeletal...
FDA Office of Orphan Products Development

Completed

Etanercept for Wegener's Granulomatosis

Wegener's Granulomatosis

United States
Orphanetics Pharma Entwicklungs GmbH

Terminated

Long-Term Tetrahydrobiopterin Treatment in PKU Patients of 0-18 Years - Study on Phenylalanine Tolerance and Safety

Phenylalanine Hydroxylase Deficiencies
National Cancer Center, Korea

Unknown

Study of Genetic Polymorphisms of Drug Transporters and Orphan Nuclear Receptors on Treatment Effects of Irinotecan

Colorectal Neoplasms | Secondary

Korea, Republic of
Bellus Health Inc
FDA Office of Orphan Products Development

Completed

Study of the Safety and Efficacy of NC-503 in Secondary (AA) Amyloidosis

Gastrointestinal Diseases | Kidney Diseases | Rheumatoid Arthritis | Nephrotic Syndrome | Secondary (AA) Amyloidosis | Familial Mediterranean Syndrome

United States, Israel, Finland, France, Italy, Lithuania, Netherlands, Poland, Russian Federation, Spain, Turkey, United Kingdom
The Avicena Group

Unknown

Study of Creatine Monohydrate in Patients With Amyotrophic Lateral Sclerosis

Amyotrophic Lateral Sclerosis (ALS)

United States
Orphan Medical

Completed

Safety and Efficacy of Xyrem Oral Solution (Sodium Oxybate) Compared With Placebo in Narcoleptic Patients

Narcolepsy

United States, Canada, Switzerland
Shanghai Yueyang Integrated Medicine Hospital
Shanghai Hongkou District Center for Disease Control And Prevention

Not yet recruiting

Comprehensive Intervention of Diabetes and Psoriasis Comorbidity Prevention and Control

Diabetes | Psoriasis
Assistance Publique - Hôpitaux de Paris

Not yet recruiting

Choroid Plexus Dysfunction in Neurological Diseases (PLEXFOLD)

Metabolic Syndrome | Plexus Choroideus

France
Hospital Israelita Albert Einstein

Recruiting

Gestrinone and Endothelial Function in Young Women

Cardiovascular Diseases | Hormones; Abuse

Brazil
McGill University Health Centre/Research Institute...
The Scientific and Technological Research Council of Turkey

Not yet recruiting

Evaluating the Efficacy of a Mobile Epilepsy Education Application

Epilepsy | Anxiety | Knowledge, Attitudes, Practice | Epilepsy in Children

Canada
University of Florida
EDAP-TMS Focal One

Not yet recruiting

High Intensity Focused Ultrasound in Prostate Cancer

Prostate Cancer

United States
Bayer

Not yet recruiting

A Study to Learn About How BAY 3283142 Moves Into, Through, and Out of the Body After a Single Dose in Participants With Reduced Liver Function Compared to Participants With Normal Liver Function

Chronic Kidney Disease | Hepatic Impairment
Seoul National University Hospital

Recruiting

Transversalis Fascia Plane Block for Iliac Bone Graft in Children

Postoperative Pain, Acute

Korea, Republic of
Istanbul Demiroglu Bilim University

Not yet recruiting

Delirium Prevention Guideline for Intensive Care Patients

Delirium | Nurse's Role

Turkey
Swiss Group for Clinical Cancer Research

Not yet recruiting

Darolutamide in Metastatic Castration-Resistant Prostate Cancer (mCRPC)

Metastatic Castration-resistant Prostate Cancer

Switzerland
Qatar University
Hamad Medical Corporation

Not yet recruiting

A Pragmatic Randomized Trial of GDM Diagnosis (UPDATE-GDM)

Pregnancy | Gestational Diabetes | Diagnosis
Tisento Therapeutics

Not yet recruiting

A Phase 2b Study of Zagociguat in Patients With MELAS (PRIZM)

Mitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)

United States, Australia, Italy, Germany, Canada, United Kingdom
Assiut University

Not yet recruiting

Characteristics and Outcomes of Patients With Hematological Malignancies

Haematologic Neoplasm
China Medical University Hospital
National Science and Technology Council

Recruiting

Acupressure Therapy on Post-stroke Fatigue, Depression, and Sleep Disturbances in Ischemic Stroke Patients

Ischemic Stroke | Sleep | Circadian Rhythm | Post-stroke Fatigue | Acupressure | Inflammatory Cytokine

Taiwan
University of Auckland, New Zealand
Health Research Council, New Zealand; Auckland City Hospital; Kitea Health Ltd

Not yet recruiting

First-in-human Trial of Home Brain Pressure Measured Using Kitea ICP Sensor, Placed During Hydrocephalus Shunt Surgery. (HomeICP)

Hydrocephalus

New Zealand
HoHo Biotech
Tri-Service General Hospital; Taoyuan Armed Forces General Hospital

Recruiting

To Evaluate the Efficacy of Oral Molecular Hydrogen Supplement in Patients With Chronic Diseases

Chronic Disease | Chronic Inflammation

Taiwan
Queen Margaret University

Not yet recruiting

A 12-week Digital Physical Activity Programme, With or Without Physical Education Support for Type 2 Diabetes Patients.

Diabetes Mellitus, Type 2

United Kingdom
University of Copenhagen

Recruiting

Home-based E-biking Intervention Among Adolescents With Cerebral Palsy

Cerebral Palsy

Denmark
Kahramanmaras Sutcu Imam University

Not yet recruiting

Reliability, Validity, and Responsiveness of the Turkish Version of Eating Assessment Tool-10 for Patients With Primer Sjögren's Syndrome

Sjogren's Syndrome
Ain Shams University

Not yet recruiting

A Comparative Study Between Ultrasound Guided Erector Spinae Plane Block and Combined Ultrasound Guided Pericapsular Nerve Group and Lateral Femoral Nerve Block Following Total Hip Arthroplasty

Post Operative Pain
Seoul National University Bundang Hospital
Samjin Pharmaceutical Co., Ltd.

Recruiting

Clopidogrel Versus Cilostazol on Vessels

Atherosclerosis | Type 2 Diabetes

Korea, Republic of
Huashan Hospital

Not yet recruiting

The Effectiveness and Safety of Body Posture in Preventing Postoperative Recurrence for Chronic Subdural Hematoma

Recurrence | Chronic Subdural Hematoma

China
Medical University of Graz

Not yet recruiting

The Effect of Alcohol on Common Tremor Syndromes

Parkinson Disease | Dystonia | Essential Tremor

Austria
Maastricht University Medical Center
Gilead Sciences

Not yet recruiting

Sacituzumab Govitecan and Bevacizumab for NSCLC Brain Metastases

NSCLC Stage IV | Brain Metastases, Adult

Netherlands
Hubei Cancer Hospital

Not yet recruiting

SBRT, Chemotherapy, and AK112 Neoadjuvant Therapy for Luminal-type Breast Cancer

Breast Cancer
Hadeer Gomaa Ebraheem Aly

Recruiting

Prevalence of Muscle and Nerve and Joint Pain

Joint Pain | Muscle Pain | Nerve Pain

Egypt
University of Western Sydney
University of Auckland, New Zealand

Recruiting

Body Surface Gastric Mapping in Patients on Semaglutide

Gastroparesis | Semaglutide-Induced Gastric Motility

Australia
Hoffmann-La Roche

Recruiting

A Study to Evaluate the Safety and Biomarker Effects of RO7269162 in Participants at Risk for or at the Prodromal Stage of Alzheimer's Disease (AD)

Alzheimer's Disease

Korea, Republic of, France
Instituto de Oftalmología Fundación Conde de Valenciana

Recruiting

Comparison of Recurrence Between Mini-SLET and Limbal-Conjunctival Autograft Techniques in Primary Pterygium

Pterygium | Pterygium of Both Eyes | Pterygium of Right Eye | Pterygium of Left Eye

Mexico
Fondazione Policlinico Universitario Agostino Gemelli...

Recruiting

Observational Study on GEP-and Pulm-NET Treated at FPG (ETNA-FPG)

Neuroendocrine Tumors | Pulmonary Neuroendocrine Neoplasm | Gep Net

Italy
Zeenat Qureshi Stroke Institute

Not yet recruiting

Clevidipine for the Antihypertensive Treatment of Acute Intracerebral Hemorrhage (CLUTCH)

Stroke | Hypertension | Intracerebral Hemorrhage
University of California, San Francisco

Not yet recruiting

PeRampanel fOr Status ePilEpticus pRophylaxis Post-cardiac Arrest (PROSPER)

Heart Arrest, Seizure, Status Epilepticus

United States
Erasme University Hospital

Recruiting

Transfusion Surveillance in Anaesthesia (STAR)

Blood Loss | Anesthesia | Transfusion Reaction | Blood Coagulation Disorder | Transfusion Related Complication | Side Effect | Anesthesia; Shock | Fresh Blood Stool

Belgium
York University
University of Alberta; Australian Catholic University; Social Sciences and Humanities...

Not yet recruiting

Tackling Two of the Most Important Unresolved Tasks in Reading Intervention

Dyslexia, Developmental
The Third Affiliated hospital of Zhejiang Chinese...

Recruiting

Peripheral-central Correlation Study on the Treatment of Chronic Tinnitus With "Dao qi Tong Luo" Based on the Theory of "Connecting the Two Ears to the Brain"

Tinnitus

China
University Hospital, Ghent

Recruiting

Amyloid PET in Patients With Mild Cognitive Impairment and Early Dementia

MCI

Belgium
NoNO Inc.

Not yet recruiting

NoNO-42 Trial in Acute Ischemic Stroke Patients Selected for Thrombolysis With or Without Endovascular Thrombectomy

Acute Ischemic Stroke
Yale University
American Heart Association

Not yet recruiting

Impact of a Community Health Worker Strategy on Produce Prescription Program Uptake Among People With Diabetes

Diabetes Type 2

United States
Fudan University

Recruiting

Postoperative Adjuvant Chemotherapy for Thymic Cancer (FUSCC-Thymic 3)

Thymic Carcinoma

China
Federal University of São Paulo

Not yet recruiting

Surgical Treatment of Osteoarticular Infections Using Bioactive Bone Substitute

Infections | Osteomyelitis | Fracture | Antibiotics

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