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Search clinical trials for: Other human genetics and inherited disorders
Total 473217 results
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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Yale UniversityNational Institute on Drug Abuse (NIDA)Not yet recruitingSchizophrenia | Cannabis Use DisorderUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingAutism Spectrum Disorder | Fragile X Syndrome | Developmental Delay | Genetic Disorder | Asperger DisorderUnited States
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Daniel BenjaminEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHeart Failure | Epilepsy | Pain | Pneumonia | Sepsis | Inflammation | Hypertension | Chronic Kidney Diseases | Hemophilia | Schizophrenia | Central Nervous System Infections | Nosocomial Pneumonia | Insomnia | Anxiety | Bipolar Disorder | Neutropenia | Staphylococcal Infections | Bradycardia | Seizures | Urinary Tract Infections | Pulmonary... and other conditionsUnited States, Canada, United Kingdom, Israel, Singapore
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Epirium Bio Inc.CompletedBecker Muscular DystrophyUnited States
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedMetabolic Disease | Genetic DisorderUnited States
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University of California, San DiegoNational Institute of Mental Health (NIMH)CompletedSchizophreniaUnited States
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rEVO BiologicsCompletedAntithrombin Deficiency, CongenitalFrance, United Kingdom, Germany, United States, Sweden, Italy
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CSL BehringCompletedFactor XIII DeficiencyUnited States
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rEVO BiologicsCompletedAntithrombin III DeficiencyUnited States, France, United Kingdom, Germany, Canada, Austria, Australia, Italy
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CSL BehringCompletedFactor XIII DeficiencyUnited States, Spain
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Masonic Cancer Center, University of MinnesotaNot yet recruitingAcquired Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Acquired Amegakaryocytic Thrombocytopenia
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Washington University School of MedicineNational Cancer Institute (NCI); The Foundation for Barnes-Jewish HospitalRecruitingMultiple Myeloma | Rectal Cancer | Cholangiocarcinoma | Colon CancerUnited States
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Sinocelltech Ltd.Not yet recruitingNon-Hodgkin Lymphoma, B-cellChina
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Chia Tai Tianqing Pharmaceutical Group Nanjing...Not yet recruiting
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Duke UniversityNational Human Genome Research Institute (NHGRI)Not yet recruitingLiver Diseases | Cardiovascular Diseases | Cancer | HyperthermiaUnited States
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Radboud University Medical CenterEnzyre B.V.Recruiting
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University of CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruiting
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University Hospital, BordeauxNot yet recruitingInfluenza | Acute Respiratory Distress SyndromeFrance
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NeuroBo Pharmaceuticals Inc.Recruiting
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Unity Health TorontoNot yet recruiting
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Tim McClintockNational Institute on Deafness and Other Communication Disorders (NIDCD)Recruiting
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University of Beira InteriorResearch Center in Sports Sciences, Health Sciences and Human Development...RecruitingMild Cognitive Impairment | Mild DementiaPortugal
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University of NicosiaCyprus Institute of Neurology and GeneticsRecruitingNeurodegenerative Diseases | Cognition Disorders in Old AgeCyprus
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Jiangsu Gensciences lnc.RecruitingSevere Hemophilia AChina
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Jiangsu Gensciences lnc.Not yet recruitingSevere Hemophilia AChina
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Columbia UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Albert...Not yet recruitingInsulin Resistance | Prediabetic State | Overweight and Obesity | Non-Alcoholic Fatty Liver DiseaseUnited States
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OctapharmaNot yet recruiting
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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The Affiliated Hospital of Qingdao UniversityRecruitingSchizophrenia | BioequivalenceChina
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Beijing Children's HospitalOffice for Rare Conditions Registries, University of GlasgowRecruitingGrowth Disorders | Growth Hormone TreatmentChina
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London School of Hygiene and Tropical MedicineUniversity of Ibadan; University of Zimbabwe; University of Malawi; University... and other collaboratorsRecruitingSchizophrenia | Schizoaffective Disorder | Delusional Disorder | Schizotypal Disorder | Acute and Transient Psychotic Disorder | Other Specified or Unspecified Primary Psychotic Disorder | Bipolar Type I Disorder With Psychotic Symptoms | Bipolar Type II Disorder With Psychotic Symptoms | Single Episode... and other conditionsMalawi, Nigeria, Sierra Leone, Zimbabwe
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University of North Carolina, Chapel HillNorth Carolina Department of Health and Human ServicesRecruitingSchizophrenia | Schizoaffective Disorder | Schizophreniform Disorders | Unspecified or Other Psychotic DisordersUnited States
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Hoffmann-La RocheRecruitingHemophilia ASpain, Canada, United States, New Zealand, Italy, Poland
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MED-LIFE DISCOVERIES LPBioPharma Services, IncRecruitingRhizomelic Chondrodysplasia PunctataCanada
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OctapharmaNot yet recruitingHemophilia ASpain, France, Finland, Germany, Italy, Serbia
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OctapharmaRecruitingSevere Hemophilia ASpain, Croatia, Italy, North Macedonia, Serbia
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University of Social Sciences and Humanities, WarsawRecruitingPsychotic Disorders | Affective DisorderPoland
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David Bond, MDRecruitingRecurrent Primary Mediastinal (Thymic) Large B-Cell Lymphoma | Refractory Primary Mediastinal (Thymic) Large B-Cell Lymphoma | Recurrent High Grade B-Cell Lymphoma With MYC, BCL2, and BCL6 Rearrangements | Refractory High Grade B-Cell Lymphoma With MYC, BCL2, and BCL6 Rearrangements | Recurrent... and other conditionsUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingFollicular Lymphoma | Myelodysplastic Syndromes | Leukemia, Myeloid | Myelofibrosis | Burkitt Lymphoma | Marginal Zone Lymphoma | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Prolymphocytic Leukemia | Plasma Cell Leukemia | Myeloproliferative Neoplasm | Small Lymphocytic... and other conditionsUnited States
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Maastricht University Medical CenterNot yet recruitingHyperinsulinism | Insulin Sensitivity | Glucose Metabolism Disorders (Including Diabetes Mellitus)Netherlands
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Zhiming JiangRecruitingRespiratory Distress SyndromeChina
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Columbia UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Albert...RecruitingObesity | Insulin Resistance | Prediabetic State | Hyperinsulinemia | Non-Alcoholic Fatty Liver DiseaseUnited States
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingObesity | Insufficient SleepUnited States
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Hoffmann-La RocheRecruitingHuntington DiseaseUnited States, Australia, Argentina, Canada, Germany, Italy, Spain, France, United Kingdom, Portugal, New Zealand, Austria, Poland, Switzerland, Denmark
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Novo Nordisk A/SRecruitingHaemophilia A With Inhibitors | Haemophilia ATaiwan, Canada, Spain, Netherlands, Korea, Republic of, India, United States, United Kingdom, China, Portugal, Lithuania, Turkey, South Africa, Ireland, Italy, France, Japan, Belgium, Germany, Malaysia, Poland, Austria, Bulgaria, Denmark and more
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National Institute of Allergy and Infectious Diseases...RecruitingObstructive Sleep Apnea | Sleep Disordered Breathing | Tonsillitis | Periodic Fever, Aphthous Stomatitis, Pharyngitis, And Cervical Adenitis (Pfapa) | Tonsil DisorderUnited States
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Peking University People's HospitalNot yet recruitingPregnancy Related | Immune Thrombocytopenia