- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: PCT sporadic or familial
Total 205407 results
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Assistance Publique - Hôpitaux de ParisAssociation pour l'Etude des Fonctions Digestives (AEFD)UnknownPorphyria Cutanea TardaFrance
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Centre Georges Francois LeclercRecruitingCancer | Genetic PredispositionFrance
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University of Texas Southwestern Medical CenterMassachusetts General HospitalRecruitingDystonia | Dystonia; Idiopathic | Dystonia, Primary | Dystonia, Secondary | Dystonia, Familial | Dystonia Disorder | Dystonias, Sporadic | Dystonia; Orofacial | Dystonia Lenticularis | Dystonia, Paroxysmal | Dystonia 6 | Dystonia 5 | Dystonia 8 | Dystonia 9 | Dystonia 19 | Dystonia 10 | Dystonia 11 | Dystonia 20 | Dystonia 12 | Dystonia... and other conditionsUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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University of Massachusetts, WorcesterEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Frontotemporal Dementia | Miyoshi Myopathy | Amyotrophic Lateral Sclerosis, Sporadic | PLS | Lou Gehrigs Disease | Familial Disease | Amyotrophic Lateral Sclerosis With DementiaUnited States
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The Third Xiangya Hospital of Central South UniversityCompleted
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University College, LondonUnknownMitochondrial Diseases | Dystonia, Familial | Sporadic Dystonia | Parkinson Disease, Juvenile | Neurodegeneration With Brain Iron Accumulation 5
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Rigshospitalet, DenmarkUnknown
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University of North Carolina, Chapel HillNorth Carolina Translational and Clinical Sciences InstituteNot yet recruitingColorectal Cancer | Rectal Cancer | Rectal Neoplasms | Colon Cancer | Colon Adenocarcinoma | Colon Rectal Cancer | Hereditary Nonpolyposis Colon CancerUnited States
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Leiden University Medical CenterThe Dutch Brain Foundation (funding)Not yet recruitingCerebral Amyloid Angiopathy
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AstraZenecaRecruitingCarpal Tunnel Syndrome | Amyloidosis | Polyneuropathy | Hereditary Transthyretin AmyloidosisRussian Federation
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HighTide Biopharma Pty LtdShenzhen HighTide Biopharmaceutical Ltd.RecruitingT2DM (Type 2 Diabetes Mellitus)China
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M.D. Anderson Cancer CenterRUNX1 FoundationRecruitingRUNX1 Familial Platelet DisorderUnited States
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National Taiwan University HospitalRecruitingHypertension | Diabetes Mellitus | Body Weight | Preventive Medicine | Family MedicineTaiwan
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Alnylam PharmaceuticalsRecruitingCerebral Amyloid AngiopathyCanada
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Laval UniversityRecruitingFamilial Hypercholesterolemia | Cholesterol, Elevated | Nutrition, HealthyCanada
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AstraZenecaRecruiting
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Fondazione SISA (Societa Italiana per lo Studio...RecruitingFamilial Hypercholesterolemia | Genetic DisorderItaly
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Alnylam PharmaceuticalsRecruitingHereditary Amyloidosis, Transthyretin-Related | Asymptomatic Carrier StateFrance
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Chaim HuijserLevvelRecruitingObsessive-Compulsive Disorder | Anxiety Disorders and Symptoms | Obsessive-Compulsive Disorder in Children | Obsessive-Compulsive Disorder in AdolescenceNetherlands
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HighTide Biopharma Pty LtdRecruiting
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HighTide Biopharma Pty LtdRecruitingT2DM (Type 2 Diabetes Mellitus)China
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AOP Orphan Pharmaceuticals AGNot yet recruitingPulmonary Arterial HypertensionSpain, Austria, France, Hungary
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John Paul II Hospital, KrakowRecruitingTransthyretin AmyloidosisPoland
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AstraZenecaRecruitingTransthyretin Amyloidosis Cardiomyopathy, Heart Failure With Preserved Ejection FractionRussian Federation
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University of PalermoRecruitingFamilial Mediterranean Fever | Non-celiac Gluten SensitivityItaly
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Hospital do CoracaoUniversity of Sao Paulo; Instituto Dante Pazzanese de Cardiologia; National Institute...Not yet recruiting
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Tampere UniversityRecruitingFamily Relations | Family Dynamics | Family SupportFinland
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Vanderbilt UniversityWomen in Need (Win); The Samuels Group; New York City Center for Innovation through...RecruitingTime to Shelter Exit | Family Well-being | Child Well-beingUnited States
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AOP Orphan Pharmaceuticals AGGCP-Service International Ltd. & Co. KG; ANOVA CRO s.r.o.; PharmaLex Belgium; Aixial...RecruitingPulmonary Arterial HypertensionAustria, Spain, France, Germany, Italy, Czechia, Hungary, Poland, Portugal, Romania
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University Hospital, ToulouseNot yet recruitingFamilial Adenomatous PolyposisFrance
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Suzhou Municipal HospitalNot yet recruitingFamilial Hypercholesterolemia | Refractory Hypercholesterolemia
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Hellenic Institute for the Study of SepsisRecruitingCommunity-acquired PneumoniaGreece
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Steen Hvitfeldt PoulsenNovo Nordisk A/SRecruitingQuality of Life | Transthyretin Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Wild-Type Transthyretin-Related (ATTR)AmyloidosisDenmark
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Wayne State UniversityNational Institute on Minority Health and Health Disparities (NIMHD)Not yet recruitingType 1 Diabetes | Family RelationsUnited States
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Novartis PharmaceuticalsRecruitingHypercholesterolaemia | Familial HypercholesterolaemiaJapan
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University of OregonNational Institute on Drug Abuse (NIDA)RecruitingDepression | Stress | Anxiety | Parent-Child Relations | Parenting | Substance Use Disorders | Pediatrics | Parenting Self-efficacyUnited States
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Hospices Civils de LyonNot yet recruitingX-Linked Hypophosphatemic Rickets
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Verge GenomicsRecruitingAmyotrophic Lateral SclerosisCanada, Netherlands
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University of PennsylvaniaRecruitingLCAT DeficiencyUnited States
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Kyowa Kirin Korea Co., Ltd.RecruitingFGF23-related Hypophosphataemic Rickets and OsteomalaciaKorea, Republic of
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Cancer Institute and Hospital, Chinese Academy...RecruitingSafety Assessment of Concurrent Radiotherapy and Novel Systemic Therapy for Breast Cancer (RADIOCOM)Chemotherapeutic Toxicity | Radiotherapy; Complications | PARP Inhibitor | Immune Checkpoint Inhibitor | Trastuzumab | Breast Cancer, Familial Male | CDK4/6 Inhibitor | PertuzumabChina
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Guangdong Provincial People's HospitalRecruitingPulmonary Arterial Hypertension | Congenital Heart DiseaseChina
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Istanbul University - Cerrahpasa (IUC)Not yet recruitingPulmonary Arterial Hypertension | Heart Defects, CongenitalTurkey
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Shanxi Medical UniversityRecruitingChronic Kidney Disease | InternetChina
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Verve Therapeutics, Inc.Not yet recruitingHeterozygous Familial Hypercholesterolemia | Premature Coronary Heart Disease
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Royal Marsden NHS Foundation TrustRecruitingLynch Syndrome | Familial Adenomatous Polyposis | Hereditary Diffuse Gastric Cancer | Peutz-Jeghers Syndrome | Cowden Syndrome | Li Fraumeni Syndrome | MutYH-associated Polyposis | SMAD4 Gene MutationUnited Kingdom
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University of GdanskNational Science Centre, PolandRecruitingDiabetes | Adolescent Behavior | Family Relations | Peer Group | Adolescent Development | Disability, Developmental | Sibling Relations | Disability, Intellectual | Well-Being, Psychological | Disability PsychologicalPoland
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IRCCS San RaffaeleRecruitingGastroenteropancreatic Neuroendocrine TumorItaly