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Search clinical trials for: Paroxysmal Nocturnal hemoglobinuria
Total 1090 results
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Alexion Pharmaceuticals, Inc.Not yet recruitingParoxysmal Nocturnal Hemoglobinuria | PNH | Extravascular Hemolysis
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Masonic Cancer Center, University of MinnesotaRecruitingAcquired Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Acquired Amegakaryocytic ThrombocytopeniaUnited States
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Novartis PharmaceuticalsNot yet recruitingParoxysmal Nocturnal Hemoglobinuria
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Alexion Pharmaceuticals, Inc.Not yet recruitingPregnancy | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Atypical Hemolytic Uremic Syndrome (aHUS) | Ultomiris-exposed Pregnant/ Postpartum | Generalized Myasthenia Gravis (gMG) | Neuromyelitis Optica Spectrum Disorder (NMOSD)
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaSwitzerland, Germany, Ukraine, United Kingdom
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Longbio PharmaRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)China
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Chengdu Suncadia Medicine Co., Ltd.RecruitingParoxysmal Nocturnal HemoglobinuriaChina
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AstraZenecaRecruitingParoxysmal Nocturnal HemoglobinuriaChina
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Wuhan Createrna Science and Technology Co., LtdNot yet recruitingParoxysmal Nocturnal Hemoglobinuria (PNH)
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BioCryst PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaSouth Africa, Malaysia
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Wuhan Createrna Science and Technology Co., LtdRecruitingParoxysmal Nocturnal HemoglobinuriaChina
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaGermany, Greece, Switzerland, United Kingdom
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaUkraine
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ADARx Pharmaceuticals, Inc.ADARx Australia Pty LtdRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)Australia
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Swedish Orphan BiovitrumRecruitingParoxysmal Nocturnal HemoglobinuriaSpain
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Aplastic Anemia and MDS International FoundationNational Organization for Rare DisordersRecruiting
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Regeneron PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaTaiwan, Korea, Republic of, Turkey, Spain, Thailand, Singapore, Japan, Canada, Malaysia, Poland, Italy, Romania
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NovelMed TherapeuticsNot yet recruitingPNH - Paroxysmal Nocturnal Hemoglobinuria
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NovelMed TherapeuticsNot yet recruitingParoxysmal Nocturnal Hemoglobinuria
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NovelMed TherapeuticsNot yet recruitingParoxysmal Nocturnal Hemoglobinuria
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Kira Pharmacenticals (US), LLC.Not yet recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Alexion Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal HemoglobinuriaItaly
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Regeneron PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaMexico, Korea, Republic of, Turkey, Italy, United Kingdom, Thailand, Poland, Singapore, Spain, Taiwan, Canada, Japan, United States, Malaysia, Greece, Romania, Hungary
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Amegakaryocytic Thrombocytopenia | Paroxysmal Nocturnal Hemoglobinuria | Diamond-Blackfan Anemia | Shwachman-Diamond Syndrome | Bone Marrow Failure Syndrome | Hereditary Sideroblastic Anemia | Hematologic Neoplasm With Germline GATA2 Mutation | Hematologic Neoplasm With Germline SAMD9... and other conditionsUnited States
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Apellis Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Paroxysmal HemoglobinuriaMalaysia, United States, Czechia, France, Netherlands, Serbia, Spain, Thailand, United Kingdom
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Novartis PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaUnited States, Korea, Republic of, Singapore, Taiwan, Italy, Turkey, France, Germany, Malaysia, Lithuania, Netherlands, United Kingdom, Japan, Czechia, Spain, China, Brazil
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Hoffmann-La RocheChugai PharmaceuticalRecruitingParoxysmal Nocturnal HemoglobinuriaKorea, Republic of, Spain, United States, Germany, Estonia, Japan, Colombia, Turkey, Brazil, France, Greece, Poland, Taiwan, Netherlands, Saudi Arabia, Italy, Australia, Sweden, Singapore, Portugal, Hungary, Belgium, Canada, Czechia, Hong... and more
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic Anemia (SAA) | Hypo-Plastic Myelodysplastic Syndrome (MDS)United States
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
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Alexion Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal HemoglobinuriaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingMDS (Myelodysplastic Syndrome) | Severe Aplastic AnemiaUnited States
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Alexion Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaItaly, Spain, Belgium, France, Turkey, Austria, Brazil, Netherlands, Australia, Finland, Russian Federation, Sweden, Canada, United States
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Alexion Pharmaceuticals, Inc.Active, not recruitingParoxysmal Nocturnal HemoglobinuriaFrance, Italy, Spain, United States, Thailand, Korea, Republic of, United Kingdom, Israel, Czechia, Greece, Poland, Brazil, Japan, Canada, Malaysia
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaTaiwan, Singapore, Korea, Republic of, Malaysia
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH) With Signs of Active HemolysisItaly, Germany, France
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Novartis PharmaceuticalsActive, not recruitingParoxysmal Nocturnal HemoglobinuriaUnited States, Germany, France, United Kingdom, Spain, Korea, Republic of, Turkey, Italy
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Alexion Pharmaceuticals, Inc.TerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)Italy, Turkey, United Kingdom, New Zealand, Korea, Republic of, Canada, Spain
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Hoffmann-La RocheActive, not recruiting
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Hoffmann-La RocheChugai PharmaceuticalActive, not recruitingParoxysmal Hemoglobinuria, NocturnalFrance, Korea, Republic of, Italy, Japan, Germany, Hungary, Netherlands
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Hoffmann-La RocheChugai PharmaceuticalActive, not recruitingParoxysmal Nocturnal HemoglobinuriaSpain, Korea, Republic of, France, Sweden, Thailand, Malaysia, China, Turkey, Netherlands, Japan, Australia, United Kingdom, Germany, South Africa, Brazil, Romania, Argentina, Poland, Greece, Hong Kong, Lithuania, Mexico, Philippines, Portuga... and more
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Alexion Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Italy, United States, Taiwan, Thailand, Brazil, Russian Federation, United Kingdom, Belgium, Canada, Korea, Republic of, Poland, Malaysia, Japan, Czechia, Spain, Germany, Austria, France, Serbia, Mexico, Sweden, Estonia, Singapore, Ar... and more
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Alexion Pharmaceuticals, Inc.AstraZenecaActive, not recruitingParoxysmal Nocturnal HemoglobinuriaChina
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BioCryst PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria | PNHUnited Kingdom, Austria, South Africa
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)China, Germany, Singapore, Korea, Republic of, Italy, United Kingdom, Malaysia, France
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Graft Versus Host Disease | Precancerous/Nonmalignant Condition
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Italy, Japan, Taiwan, Germany, France, United Kingdom, Spain, Korea, Republic of, Czechia, Brazil, Netherlands, United States
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Roswell Park Cancer InstituteActive, not recruitingAcute Myeloid Leukemia | Polycythemia Vera | Myelofibrosis | Chronic Myelomonocytic Leukemia | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Secondary Acute Myeloid Leukemia | Sickle Cell Disease | Myelodysplastic Syndrome | Plasma Cell Myeloma | Chronic Granulomatous... and other conditionsUnited States
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Samsung Bioepis Co., Ltd.CompletedParoxysmal Nocturnal HemoglobinuriaKorea, Republic of, Taiwan, Malaysia, Thailand, Romania, India, Mexico, Ukraine
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SanofiCompletedParoxysmal Nocturnal HemoglobinuriaUnited States