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Search clinical trials for: RBC transfusion dependent
Total 5326 results
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Associazione Qol-oneRecruitingMyelodysplastic Syndromes | Anemia | Transfusion-dependent Anemia | Del(5Q)Italy
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Bristol-Myers SquibbRecruitingAnemiaThailand, China, Canada, Turkey, Greece, Taiwan, Italy, Hong Kong
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Phoenicia BioScienceNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Beta Thalassemia IntermediaUnited States, Canada
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Terumo BCTbioUnited States Department of Defense; U.S. Army Medical Research and Development... and other collaboratorsTerminatedTransfusion Dependent ThalassemiaUnited States, Israel, Italy, Turkey
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CelgeneCompletedMyelodysplastic SyndromeUnited States, Australia, Canada, Czechia, France, Germany, Italy, Korea, Republic of, Mexico, Poland, Sweden, United Kingdom, Belgium, Brazil, Denmark, Finland, Greece, Israel, Netherlands, Norway, Portugal, Spain, Turkey
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University of California, San FranciscoTerminatedMyeloid Malignancy | Metabolic Disease | Bone Marrow Failure Syndrome | Transfusion-dependent Red Blood Cell (RBC) Defect | Congenital Immunodeficiency | Severe Immune DysregulationUnited States
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Weill Medical College of Cornell UniversityCelgeneTerminatedMyelodysplastic SyndromeUnited States
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Emory UniversityTerminated
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Jason Robert GotlibCelgene CorporationTerminatedLeukemia | Anemia | Myelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML)United States
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Regeneron PharmaceuticalsNot yet recruitingNon-transfusion Dependent Beta-thalassemia (NTDT)
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Ulrich Ronellenfitsch, MDGerman Federal Ministry of Education and Research; Coordinating Centre for...Not yet recruitingSurgical Blood Loss | Transfusion-dependent Anemia | Abdomen DiseaseGermany
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Editas Medicine, Inc.Not yet recruitingSickle Cell Disease | Hemoglobinopathies | Transfusion-dependent Beta-Thalassemia
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Kind Pharmaceuticals LLCNot yet recruiting
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Bangabandhu Sheikh Mujib Medical University, Dhaka...Recruiting
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Not yet recruitingTransfusion-dependent Beta-ThalassemiaChina
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Sunnybrook Health Sciences CentreNot yet recruitingMyelodysplastic Syndromes | MDSCanada
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Institute of Hematology & Blood Diseases Hospital...Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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Bristol-Myers SquibbRecruitingMyelodysplastic SyndromesSpain, United States, France, Italy, Belgium, Germany, Poland, Czechia, Puerto Rico
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Sakarya UniversityNot yet recruiting
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Institute of Hematology & Blood Diseases HospitalRecruitingGene Therapy | Transfusion-dependent Beta-ThalassemiaChina
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Shenzhen HemogenRecruiting
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Institute of Hematology & Blood Diseases HospitalR&D Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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Shenzhen HemogenRecruiting
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Shanghai BDgene Co., Ltd.Ruijin HospitalNot yet recruiting
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Shanghai BDgene Co., Ltd.Shanghai Children's Medical CenterNot yet recruiting
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RecruitingTransfusion Dependent Beta-ThalassemiaChina
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RecruitingTransfusion-dependent α-ThalassemiaChina
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Pharmacosmos A/SICON plcRecruitingBeta Thalassemia Major AnemiaDenmark
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Forma Therapeutics, Inc.RecruitingVery Low Risk, Low Risk, or Intermediate Risk MDS Per IPSS-RUnited States, France, Canada, Germany
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany, Saudi Arabia
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Sun Yat-sen UniversityRecruitingThalassemia Major | Transfusion-dependent AnemiaChina
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Editas Medicine, Inc.RecruitingHemoglobinopathies | Thalassemia Major | Thalassemia Intermedia | Transfusion Dependent Beta ThalassemiaUnited States, Canada
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Bing HanNot yet recruiting
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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Forma Therapeutics, Inc.RecruitingSickle Cell Disease | ThalassemiaUnited States, Lebanon, Canada
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McMaster UniversityCBSRecruitingMyelodysplastic SyndromeCanada
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University Hospital, Basel, SwitzerlandRecruiting
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RenJi HospitalNot yet recruitingTransfusion Related Complication
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Università degli Studi di FerraraAzienda Ospedaliero, Universitaria Pisana; Rare Partners srl Impresa Sociale; Azienda Ospedaliero, Universitaria MeyerRecruitingBeta-ThalassemiaItaly
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Children's Hospital of PhiladelphiaNational Heart, Lung, and Blood Institute (NHLBI); New York Blood CenterRecruiting
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI); Columbia UniversityRecruitingSickle Cell Disease Without CrisisUnited States
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Johann Wolfgang Goethe University HospitalWuerzburg University HospitalRecruitingAnemia | Surgery | Transfusion-dependent AnemiaGermany
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Ottawa Hospital Research InstituteCanadian Institutes of Health Research (CIHR)RecruitingSubarachnoid Hemorrhage, AneurysmalUnited States, Australia, Canada
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Daping Hospital and the Research Institute of Surgery...RecruitingAcute Respiratory Distress Syndrome (ARDS) | Red Blood Cells(RBC)China
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Cerus CorporationRecruitingAnemiaUnited States, Puerto Rico
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Emory UniversityNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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WestatEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Pediatric CancerUnited States, Brazil