- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: RNAi therapeutic
Total 12495 results
-
Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated Amyloidosis | ATTR AmyloidosisIsrael, Italy, Netherlands, Spain, United States, France, Denmark, Germany, Portugal, Brazil, Taiwan
-
Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BBulgaria, United States, United Kingdom, Russian Federation, Switzerland
-
Alnylam PharmaceuticalsActive, not recruitingPrimary Hyperoxaluria Type 1 (PH1) | Primary HyperoxaluriaUnited States, France, United Kingdom, Israel, Germany
-
Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, Brazil, Bulgaria, France, Italy, Japan, Mexico, Netherlands, Taiwan, United Kingdom, Belgium, Czechia, Denmark, New Zealand, Sweden, Korea, Republic of, Argentina, Chile, Hong Kong, Portugal
-
Novo Nordisk A/SCompletedKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2)Poland, United States, United Kingdom, New Zealand, Australia, Canada, France, Germany, Israel, Italy, Japan, Lebanon, Netherlands, Romania, Spain
-
Alnylam PharmaceuticalsApproved for marketingAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid Polyneuropathies
-
Alnylam PharmaceuticalsTerminatedNonalcoholic Steatohepatitis | NASHUnited States, Bulgaria, United Kingdom, Belgium, Turkey
-
Alnylam PharmaceuticalsActive, not recruitingPrimary Hyperoxaluria Type 1 | Primary HyperoxaluriaUnited States, Italy, France, Lebanon, Belgium, Netherlands, Israel, United Arab Emirates, Australia, Jordan, Turkey
-
Alnylam PharmaceuticalsCompletedPrimary Hyperoxaluria | PH1 | RNAi Therapeutic | siRNA | AGTFrance, United Kingdom, Netherlands, Israel, Germany
-
Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
-
Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
-
Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisPortugal, Spain, Sweden, Brazil, United States, France, Germany
-
Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisPortugal, Sweden, Brazil, United States, France, Spain, Germany
-
Alnylam PharmaceuticalsCompletedAcute Intermittent PorphyriaUnited States, United Kingdom, Sweden
-
Alnylam PharmaceuticalsNo longer availableTransthyretin-mediated Amyloidosis With Cardiomyopathy | ATTR Amyloidosis With CardiomyopathyUnited States
-
Alnylam PharmaceuticalsCompletedPrimary Hyperoxaluria Type 1 (PH1)United States, France, United Kingdom, Switzerland, Netherlands, Israel, Germany, United Arab Emirates
-
Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
-
Baylor Research InstituteThe Methodist Hospital Research Institute; International Urogynecological AssociationCompletedOveractive Bladder | Lower Urinary Tract Symptoms | Dementia | Incontinence, UrgeUnited States
-
Alnylam PharmaceuticalsCompletedAmyloidosisUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom, Germany, France, Korea, Republic of, Brazil, Mexico, Turkey
-
Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisUnited States, United Kingdom
-
Alnylam PharmaceuticalsCompletedPolyneuropathy | Hereditary Transthyretin-mediated (ATTRv) AmyloidosisUnited States
-
Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
-
Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
-
Dicerna Pharmaceuticals, Inc.CompletedPrimary Hyperoxaluria Type 3United States, Germany, Netherlands, United Kingdom
-
Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisUnited States, Canada, United Kingdom
-
Alnylam PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Spain, United Kingdom
-
Alnylam PharmaceuticalsCompletedPrimary Hyperoxaluria Type 1 (PH1)France, United Kingdom, Netherlands, Israel, Germany
-
Alnylam PharmaceuticalsCompletedATTR Amyloidosis | Transthyretin (TTR)-Mediated Amyloidosis | Familial Amyloidotic Polyneuropathy (FAP) | Familial Amyloid NeuropathiesFrance, Germany, Portugal, United Kingdom, Sweden, Spain
-
Alnylam PharmaceuticalsCompletedPorphyria, Acute Intermittent | Acute Intermittent Porphyria (AIP) | Acute Hepatic Porphyria (AHP) | Acute PorphyriaSweden
-
Alnylam PharmaceuticalsTerminatedAntitrypsin Deficiency Liver DiseaseUnited Kingdom
-
Alnylam PharmaceuticalsWithdrawnAtypical Hemolytic Uremic SyndromeSweden, Moldova, Republic of, Latvia, Lithuania, Estonia, Bosnia and Herzegovina, Canada, Georgia, Macedonia, The Former Yugoslav Republic of, Serbia
-
Tacere Therapeutics, Inc.TerminatedHepatitis CUnited States
-
Alnylam PharmaceuticalsTerminatedHepatitis B | Chronic Hepatitis B | Hepatitis B, Chronic | HBV | Hepatitis B InfectionUnited Kingdom, New Zealand, Singapore, Korea, Republic of, Australia, Hong Kong
-
Alnylam PharmaceuticalsCompletedTransthyretin-mediated Amyloidosis (ATTR Amyloidosis)United Kingdom
-
Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | Amyloidosis, Hereditary | Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | Amyloidosis, Hereditary, Transthyretin-Related | Familial Transthyretin Cardiac AmyloidosisUnited States, France, Italy, Spain, Canada, Germany, Belgium, Sweden, United Kingdom
-
Alnylam PharmaceuticalsCompletedAcute Intermittent PorphyriaUnited States, United Kingdom, Sweden
-
Tacere Therapeutics, Inc.CompletedHepatitis CUnited States
-
Alnylam PharmaceuticalsCompleted
-
Alnylam PharmaceuticalsThe Medicines CompanyCompletedHypercholesterolemiaUnited Kingdom
-
Alnylam PharmaceuticalsCompletedA Study of the Safety, Tolerability and Pharmacokinetics of ALN-TTR02 in Japanese Healthy VolunteersTransthyretin (TTR)-Mediated AmyloidosisUnited Kingdom
-
Calando PharmaceuticalsTerminated
-
Tang-Du HospitalRecruitingSmall Cell Lung CancerChina
-
Timothy PoteruchaPfizer; American Heart Association; Eidos Therapeutics, a BridgeBio companyRecruiting
-
MSD Italia S.r.l.Not yet recruitingNSCLC | Non-small Cell Lung Cancer | NSCLC, Stage III | NSCLC, Stage I
-
Ascidian Therapeutics, IncRecruitingStargardt Disease | Stargardt Disease 1 | Juvenile Macular Degeneration | Cone Rod DystrophyUnited States
-
University of AlcalaRecruitingTo be Approved by the Ethics CommitteeSpain
-
Changhai HospitalRui TherapeuticsNot yet recruiting
-
Peter TimoneyInflammasome TherapeuticsNot yet recruiting
-
Assistance Publique - Hôpitaux de ParisNot yet recruiting
-
Milton S. Hershey Medical CenterAminex Therapeutics, Inc.Not yet recruitingEwing Sarcoma | Embryonal Tumor With Multilayered Rosettes | Osteosarcoma Recurrent | Atypical Teratoid/Rhabdoid Tumor | DIPG Brain Tumor | Neuroblastoma Recurrent