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Search clinical trials for: SMA, SMN1, Kugelberg-Welander
Total 12 results
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Centre Hospitalier Régional de la CitadelleRoche Pharma AG; Biogen; AveXis, Inc.; Association Belge contre les Maladies neuro...CompletedSpinal Muscular AtrophyBelgium
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UMC UtrechtCompletedSpinal Muscular Atrophy | SMA | Kugelberg-Welander DiseaseNetherlands
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Rigshospitalet, DenmarkDana-Farber Cancer Institute; St. Jude Children's Research Hospital; European... and other collaboratorsCompletedAcute Lymphoblastic LeukemiaDenmark
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National Taiwan University HospitalUnknown
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University Hospital, RouenSociety GENOMIC VISIONTerminatedSpinal Muscular AtrophyFrance
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Hospital Israelita Albert EinsteinMinistry of Health, BrazilCompletedSpinal Muscular AtrophyBrazil
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Hospital Israelita Albert EinsteinBiogenActive, not recruitingSpinal Muscular AtrophyBrazil, Argentina, Chile, Colombia, Mexico, Uruguay
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Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
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National Institute of Neurological Disorders and...Completed
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National Taiwan University HospitalUnknownColon Cancer | Spinal Muscular Atrophy | Neonatal HyperbilirubinemiaTaiwan
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Malaysia, China, Japan, Italy, Singapore, United Kingdom, France, Australia, Thailand, Denmark, United States
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Massachusetts General HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownSpinal Muscular AtrophyUnited States