- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: SMA type II/III
Total 76891 results
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIIUnited States
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BeiGeneNot yet recruitingMetastatic Solid Tumor | Advanced Hepatocellular Carcinoma | Metastatic Hepatocellular Carcinoma | Alpha-fetoprotein (AFP)-Producing Gastric Cancer | Extragonadal Yolk Sac Tumors | Glypican-3 (GPC3)-Positive Squamous Non-small Cell Lung Cancer
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Shanghai Fudan-Zhangjiang Bio-Pharmaceutical Co...Not yet recruitingAdvanced Solid Tumor, SCLC(Small Cell Lung Cancer) or LCNEC (Large Cell Neuroendocrine Carcinoma)China
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National University Hospital, SingaporeNot yet recruitingCarcinoma, Hepatocellular | Gastric Adenocarcinoma | Non-small Cell Lung Cancer | Head and Neck Squamous Cell Carcinoma | Oesophageal Cancer | GastroEsophageal CancerSingapore
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GeneCradle IncRecruitingSpinal Muscular Atrophy Type 3China
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Daewoong Pharmaceutical Co. LTD.Not yet recruiting
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Wake Forest University Health SciencesNational Cancer Institute (NCI)Not yet recruitingMelanoma | Non-Hodgkin Lymphoma | Breast Carcinoma | Lung Non-Small Cell Carcinoma | Colorectal Carcinoma
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Fundación para la Investigación del Hospital Clínico...Not yet recruiting
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Yonsei UniversityKorea Health Industry Development InstituteRecruitingGait Disorders, NeurologicKorea, Republic of
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National Cancer Institute (NCI)Not yet recruitingCarcinoma, Neuroendocrine | Tumor, Neuroendocrine | Tumors, Neuroendocrine | Neuroendocrine; Carcinoma | Small Cell; ReceptorsUnited States
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University of North Carolina, Chapel HillAmerican Diabetes AssociationNot yet recruitingDiabetes Mellitus | Diabetes Mellitus, Type 1 | Diabetes type1 | Distress, Emotional | Diabetes, AutoimmuneUnited States
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University of North Carolina, Chapel HillAmerican Diabetes AssociationNot yet recruitingDiabetes Mellitus | Diabetes Mellitus, Type 1 | Diabetes type1 | Distress, Emotional | Diabetes, AutoimmuneUnited States
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Tisento TherapeuticsNot yet recruitingMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)United States, Australia, Italy, Germany, Canada, United Kingdom
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McGill University Health Centre/Research Institute...Not yet recruitingDiabetes Mellitus | Type 1 DiabetesCanada
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Shanghai Simnova Biotechnology Co.,Ltd.Shanghai Chest HospitalRecruitingRecurrent/Refractory Small Cell Lung Cancer Lung Large Cell Neuroendocrine CarcinomaChina
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Cancer Research UKUCB Biopharma SRLNot yet recruitingUterine Cervical Neoplasms | Carcinoma, Non-Small-Cell Lung | Colorectal Neoplasms | Pancreatic Neoplasms | Esophageal Neoplasms | Ovarian Neoplasms | Squamous Cell Carcinoma of Head and Neck | Triple Negative Breast Neoplasms | Advanced Solid Tumours | Carcinoma, Renal Cell (Clear Cell Only) | Stomach Neoplasms...United Kingdom
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Sichuan Baili Pharmaceutical Co., Ltd.Baili-Bio (Chengdu) Pharmaceutical Co., Ltd.Not yet recruiting
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Beijing InnoCare Pharma Tech Co., Ltd.Not yet recruitingHematologic MalignanciesChina
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AstraZenecaNot yet recruitingNeoplasms | Respiratory Tract Diseases | Lung Diseases | Neoplasms by Site | Carcinoma, Non-Small-Cell Lung | Lung Neoplasms | Respiratory Tract Neoplasms | Thoracic Neoplasms | Carcinoma, Bronchogenic | Bronchial NeoplasmsChina
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Francesco De CobelliA.O. Ospedale Papa Giovanni XXIII; Cardarelli Hospital; AOU Pisana, Pisa, ItalyRecruitingIntrahepatic CholangiocarcinomaItaly
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Convalife (Shanghai) Co., Ltd.Not yet recruitingHer2-positive Advanced Esophageal/Esophagogastric Junction/Gastric Adenocarcinoma With Brain Metastasis
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Fudan UniversityRecruitingNon-small Cell Lung Cancer | Neuroendocrine Carcinoma | Histology TransformationChina
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Institute of Hematology & Blood Diseases Hospital...Not yet recruitingChronic Lymphocytic Leukemia | Small Lymphocytic Lymphoma
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Gruppo Italiano Malattie EMatologiche dell'AdultoNot yet recruitingChronic Lymphocytic Leukemia | Small Lymphocytic Lymphoma | CLL-like MBL | Varicella-zoster Virus ReactivationItaly
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National Cancer Institute (NCI)Not yet recruitingLeukemia, Lymphocytic, Chronic, B-Cell | B-Cell Chronic Lymphocytic Leukemia | B-Lymphocytic Leukemia, ChronicUnited States
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7 Hills Pharma, LLCNot yet recruitingMelanoma | Kidney Cancer | Renal Cell Carcinoma | Hepatocellular Carcinoma | Colorectal Cancer | NSCLC | Non Small Cell Lung Cancer | Skin Cancer | Metastasis | Advanced Solid Tumor | Advanced Cancer | Renal Cell Cancer | Hepatocellular Cancer | Mismatch Repair Deficiency | Pleural Mesothelioma | MSI-High | Anaplastic Lymphoma... and other conditionsUnited States
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Jiangsu Healthy Life Innovation Medical Technology...Not yet recruiting
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Zhejiang Cancer HospitalRecruitingExtensive Stage Lung Small Cell CancerChina
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Mayo ClinicRecruitingMetastatic Lung Non-Small Cell Carcinoma | Metastatic Clear Cell Renal Cell Carcinoma | Resectable Lung Non-Small Cell Carcinoma | Metastatic Malignant Solid Neoplasm | Metastatic Bladder Urothelial Carcinoma | Metastatic Colorectal Carcinoma | Metastatic Triple-Negative Breast Carcinoma | Locally... and other conditionsUnited States
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National Cancer Institute, NaplesRecruiting
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Cairo UniversityNot yet recruitingMolar Incisor Hypomineralization
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University of KentuckyNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Department...RecruitingDiabetes Mellitus, Type 2United States
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Azienda Ospedaliero Universitaria Maggiore della...Università degli Studi del Piemonte Orientale "Amedeo Avogadro"RecruitingRenal Cell CarcinomaItaly
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IRCCS SYNLAB SDNFondazione Santobono PausiliponRecruitingAcute Lymphoblastic Leukemia, PediatricItaly
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UNICANCERGlaxoSmithKline; National Cancer Institute, FranceNot yet recruitingSoft Tissue Sarcoma | Pancreatic Adenocarcinoma | Gastric Adenocarcinoma | Neuroendocrine Carcinoma | Adrenocortical Carcinoma | Small Bowel Adenocarcinoma | Ampulla of Vater Carcinoma | Duodenum AdenocarcinomaFrance
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LG ChemNot yet recruitingUrothelial Carcinoma | Malignant Melanoma | Non-small Cell Lung Cancer(NSCLC) | Head and Neck Squamous Cell Carcinoma(HNSCC) | Renal Cell Carcinoma(RCC)
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Inhye AhnLoxo Oncology, Inc.RecruitingChronic Lymphocytic Leukemia | Small Lymphocytic LymphomaUnited States
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Al-Azhar UniversityRecruitingRenal Tumor | Renal Malignant TumorEgypt
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Mount Sinai Hospital, CanadaMitacsRecruitingGestational Diabetes | Small for Gestational Age at Delivery | type1diabetes | Type2diabetesCanada
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McGill University Health Centre/Research Institute...Not yet recruitingHealthy Subjects | Type 1 Diabetes (T1D)
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Giulio FrontinoNot yet recruitingDiabetes Mellitus, Type 1
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Sun Yat-sen UniversityFifth Affiliated Hospital, Sun Yat-Sen University; Ningbo Medical Center Lihuili...Not yet recruitingHepatocellular CarcinomaChina
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Tubulis GmbHNot yet recruitingOvarian Cancer | Non-small Cell Lung CancerUnited States
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Sun Yat-sen UniversityNot yet recruitingCervical Cancer | Breast Cancer | Non-Small Cell Lung Cancer | Endometrial Cancer | Head And Neck Squamous Cell CarcinomasChina
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Guangzhou Medical UniversityNot yet recruiting
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AbbVieNot yet recruitingChronic Lymphocytic Leukemia | Small Lymphocytic Lymphoma
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National Cancer Institute (NCI)Not yet recruitingStage IV Lung Cancer AJCC v8 | Extensive Stage Lung Small Cell Carcinoma
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PfizerRecruitingMelanoma | Neoplasms | Renal Cell Carcinoma | Non-small-cell Lung Cancer | Squamous Cell Carcinoma of the Head and Neck | Urothelial Carcinoma | Colorectal Carcinoma | Ovarian CarcinomaPuerto Rico, Japan, United States
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Suzhou Zelgen Biopharmaceuticals Co.,LtdNot yet recruitingSmall Cell Lung Cancer | Neuroendocrine CancerChina