Search clinical trials for: SMN2

Total 7 results

Novartis Gene Therapies
PRA Health Sciences

Completed

Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies

Spinal Muscular Atrophy Type I

Korea, Republic of, Taiwan, Japan
National Taiwan University Hospital

Unknown

Quantitative Analysis of SMN1 and SMN2 Gene Based on DHPLC System

Spinal Muscular Atrophy

Taiwan
Hugh McMillan
Families of Spinal Muscular Atrophy; Gwendolyn Strong Foundation

Terminated

Effect of Low-Dose Celecoxib on SMN2 in Patients With Spinal Muscular Atrophy (SMA)

Spinal Muscular Atrophy (SMA)

Canada
Novartis Gene Therapies
PRA Health Sciences

Completed

Pre-Symptomatic Study of Intravenous Onasemnogene Abeparvovec-xioi in Spinal Muscular Atrophy (SMA) for Patients With Multiple Copies of SMN2 (SPR1NT)

Spinal Muscular Atrophy

United States, United Kingdom, Australia, Belgium, Canada, Japan
National Institute of Neurological Disorders and...

Completed

SMN Copy Number Distribution in Mali, West Africa

Spinal Muscular Atrophy

Mali
National Taiwan University Hospital

Unknown

Establishing Novel Detection Techniques for Various Genetic-Related Diseases by Applying DHPLC Platform.

Colon Cancer | Spinal Muscular Atrophy | Neonatal Hyperbilirubinemia

Taiwan
Novartis Pharmaceuticals

Recruiting

Long-term Follow-up of Patients With Spinal Muscular Atrophy Treated With OAV101 in Clinical Trials (SPECTRUM)

Spinal Muscular Atrophy (SMA)

Spain, Canada, Taiwan, Belgium, Malaysia, China, Japan, Italy, Singapore, United Kingdom, France, Australia, Thailand, Denmark, United States

Search clinical trials for: SMN2

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