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Search clinical trials for: Sanfilippo syndrome Type A
Total 497239 results
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis Type IIIAUnited States
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudNot yet recruitingSanfilippo Syndrome Type CUnited States, France
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Sanguine BiosciencesDenali Therapeutics Inc.RecruitingMucopolysaccharidosis III-AUnited States
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationSanfilippo Syndrome Type DUnited States
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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Allievex CorporationActive, not recruitingMucopolysaccharidosis Type IIIB | MPS III BGermany, United States, Turkey, United Kingdom, Colombia, Spain, Taiwan
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Allievex CorporationActive, not recruitingMucopolysaccharidosis Type IIIBUnited States, Germany, Spain, Argentina, Australia, Brazil, Colombia, Taiwan, Turkey
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Abeona Therapeutics, IncTerminatedMucopolysaccharidosis Type 3 BUnited States, Germany, France, Spain
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Turkey
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Germany, Turkey
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LYSOGENEActive, not recruitingMucopolysaccharidosis Type IIIAGermany, United States, United Kingdom, France, Netherlands
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ShireTerminatedSanfilippo SyndromeNetherlands, United Kingdom
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ShireCompletedMucopolysaccharidosis (MPS)United Kingdom, Netherlands
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ShireCompletedSanfilippo Syndrome Type AUnited States
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ShireTerminatedSanfilippo Syndrome | Mucopolysaccharidosis (MPS)United States, United Kingdom, Spain, Germany, France, Italy, Netherlands
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ShireCompletedSanfilippo SyndromeUnited States, Spain, United Kingdom, Argentina, France, Germany, Italy, Netherlands
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ShireCompletedSanfilippo Syndrome Type BUnited States, United Kingdom, Germany
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Allievex CorporationCompletedMucopolysaccharidosis Type IIIB | MPS III BUnited States, Taiwan, Spain, Colombia, Germany, United Kingdom, Turkey
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Allievex CorporationCompletedMucopolysaccharidosis Type IIIB | Mucopolysaccharidosis Type 3 B | MPS III B | MPS 3 BUnited States, Spain, Turkey, Taiwan, Australia, Colombia, Germany, United Kingdom
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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Alexion PharmaceuticalsTerminatedMPS IIIB (Sanfilippo B Syndrome)Spain, United States, Brazil, United Kingdom, Portugal, Italy
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Alexion PharmaceuticalsCompletedMucopolysaccharidosis IIIBUnited States, United Kingdom, Spain
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo Syndrome)Spain, Netherlands, United Kingdom, United States, Brazil
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo B Syndrome)United Kingdom
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LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance
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Amanda ShallcrossAmerican Heart AssociationNot yet recruitingHypertension | Obesity | Metabolic Syndrome | Type2diabetes
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Rutgers, The State University of New JerseyEthos Farm to HealthNot yet recruitingCardiovascular Diseases | Obesity | Diabetes Mellitus | Metabolic Syndrome | Hyperlipidemias | Kidney Disease, Chronic | Hypertension,Essential
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Helse Møre og Romsdal HFNot yet recruitingCarpal Tunnel Syndrome | Cardiac Amyloidosis | ATTR Amyloidosis Wild Type | ATTR Gene Mutation
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City of Hope Medical CenterNational Cancer Institute (NCI)Not yet recruitingRecurrent Acute Myeloid Leukemia | Recurrent Myelodysplastic Syndrome | Refractory Acute Myeloid Leukemia | Refractory Myelodysplastic Syndrome | Myelodysplastic Syndrome/Acute Myeloid LeukemiaUnited States
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University Hospital, Basel, SwitzerlandNot yet recruitingNeuroendocrine TumorsSwitzerland
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Khondrion BVNot yet recruitingMitochondrial Diseases | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Maternally Inherited Diabetes and Deafness (MIDD) | Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke-like Episodes (MELAS)
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City of Hope Medical CenterNational Cancer Institute (NCI)Not yet recruitingRecurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3a Follicular Lymphoma | Refractory Grade 1 Follicular Lymphoma | Refractory Grade 2 Follicular Lymphoma | Refractory Grade 3a Follicular LymphomaUnited States
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Hong Kong Baptist UniversityNot yet recruitingType 2 Diabetes Mellitus With Metabolic Syndrome
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Nantes University HospitalInstitut National de la Santé Et de la Recherche Médicale, FranceNot yet recruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic LeukemiaFrance
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Peking University First HospitalPeking University Third Hospital; Peking University Cancer Hospital & InstituteRecruitingCutaneous T Cell Lymphoma | Cutaneous T-Cell Lymphoma/Mycosis FungoidesChina
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Universitätsklinikum Hamburg-EppendorfRecruitingFamilial Adenomatous Polyposis | Adenomatous Polyposis Coli | Duodenal AdenomaGermany
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Second Affiliated Hospital, School of Medicine,...Not yet recruiting
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The Second Hospital of Nanjing Medical UniversityRecruitingType A Aortic DissectionChina
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Fundació EurecatUniversity Rovira i VirgiliNot yet recruitingCardiovascular Diseases | Cholesterol Level, High | Circadian Rhythm Sleep Disorder, Shift Work TypeSpain
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Ontario Clinical Oncology Group (OCOG)PfizerNot yet recruitingRefractory Multiple MyelomaCanada
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Fujian Medical University Union HospitalRecruitingType B Aortic Dissection | Return to WorkChina
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Bristol-Myers SquibbNot yet recruitingAcute Myeloid Leukemia | Myelodysplastic SyndromeUnited States, Canada
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Brooklyn Clinical ResearchRecruitingCardiovascular Diseases | Obesity | Metabolic Syndrome | PreDiabetes | Diabetes Type 2United States
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University Medical Center, KazakhstanNazarbayev University; Astana Medical University; Ministry of Science and Higher... and other collaboratorsRecruitingMetabolic SyndromeKazakhstan
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Assistance Publique - Hôpitaux de ParisCentre Leon Berard; Institut National de la Santé Et de la Recherche Médicale... and other collaboratorsNot yet recruitingEnvironmental Exposure | SDH Gene Mutation | SDH-Related Familial Paraganglioma | SDHx-Related SyndromesFrance
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Tisento TherapeuticsNot yet recruitingMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)United States, Australia, Italy, Germany, Canada, United Kingdom