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Search clinical trials for: Sickle Cell Disease & Thalassemia
Total 386429 results
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Novo Nordisk A/SNot yet recruitingHealthy Volunteers Sickle Cell Disease, ThalassemiaUnited States
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Editas Medicine, Inc.Not yet recruitingSickle Cell Disease | Hemoglobinopathies | Transfusion-dependent Beta-Thalassemia
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National Heart, Lung, and Blood Institute (NHLBI)Children's National Research InstituteRecruitingSickle Cell Disease | Thalassemia | HemoglobinopathyUnited States
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Hospital Universitari Vall d'Hebron Research InstituteERN-EuroBloodNet (European Reference Network on Rare Hematological DiseasesRecruitingLeukemia | Anemia | Iron Metabolism Disorders | Anemia, Sickle Cell | Thalassemia | Bleeding Disorder | Myeloma | Lymphoid Neoplasm | Blood Cancer | Bone Marrow Failure | Red Cell Membrane and Enzyme Abnormalities | Myeloma, MalignantSpain
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Markus MaparaITB-Med LLCRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingSickle Cell Disease | Sickle Cell Disorders | Hb-SS Disease | Hemoglobin S | Disease Sickle Cell Anemia | Hemoglobin Beta Thalassemia DiseaseUnited States
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Assiut UniversityNot yet recruitingSickle Cell Disease, Beta Thalassemia Intermedia
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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Memorial Sloan Kettering Cancer CenterRecruitingSickle Cell Disease | Thalassemia | Thalassemia, BetaUnited States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Sanguine BiosciencesRecruitingHeart Diseases | Stroke | Lymphoma | Multiple Sclerosis | Kidney Diseases | Diabetes | Leukemia | Age-Related Macular Degeneration | Cancer | Arthritis | Schizophrenia | Thyroid Diseases | Parkinson Disease | Hepatitis | Vasculitis | Psoriasis | Asthma | Amyloidosis | Fibromyalgia | Graves Disease | Alzheimer Disease | Celiac Disease | Cirr... and other conditionsUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany, Saudi Arabia
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Universitair Ziekenhuis BrusselRecruitingHematologic Diseases | Cancer | Sickle Cell ThalassemiaBelgium
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Novo Nordisk A/SRecruitingSickle Cell DiseaseSpain, United States, United Kingdom, Canada, Italy, India, Turkey, Greece, South Africa, France, Lebanon, Oman
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Anemia | Beta ThalassemiaUnited States
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Novo Nordisk A/SRecruitingHaemophilia A and B With and Without InhibitorsUnited States, Spain, Italy, Estonia, Thailand, Canada, India, Malaysia, United Kingdom, Turkey, South Africa, Lebanon, Bosnia and Herzegovina, Bulgaria, France, Greece, Japan, Lithuania, Norway, Poland, Romania, Russian Federation, Swede... and more
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Forma Therapeutics, Inc.RecruitingSickle Cell Disease | ThalassemiaUnited States, Lebanon, Canada
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Assistance Publique - Hôpitaux de ParisRecruiting
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Phoenicia BioScienceNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Beta Thalassemia IntermediaUnited States, Canada
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American Thrombosis and Hemostasis NetworkSanofi; Pfizer; Genentech, Inc.; CSL Behring; Hemophilia of Georgia, Inc.; Hemab TherapeuticsRecruitingHemophilia | Thrombosis | Thrombophilia | Sickle Cell Disease | Thalassemia | Bleeding Disorder | Von Willebrand Diseases | Factor IX Deficiency | Connective Tissue Disorder | Factor VIII Deficiency | Hematologic Disorder | Rare Bleeding Disorder | Platelet DisorderUnited States
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Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingMalaria | Sickle Cell Disease | Alpha and Beta Thalassemia | Human PhysiologyUnited States
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Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
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Vanderbilt University Medical CenterWashington University School of Medicine; University of Alabama at BirminghamRecruitingStroke | Sickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Thalassemia | Sickle Cell-Beta0-ThalassemiaUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health Clinical Center (CC); National Cancer Institute...RecruitingStem Cell Transplantation | Sickle Cell Disease | Thalassemia | Graft vs Host DiseaseUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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Massachusetts General HospitalRecruitingBone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders (BMT)Autoimmune Diseases | Multiple Myeloma | Hodgkin Disease | AL Amyloidosis | Myelofibrosis | Chronic Kidney Disease | Sickle Cell Anemia | Thalassemia | Aplastic Anemia | Chronic Lymphocytic Leukemia (CLL) | Acute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Non-Hodgkin... and other conditionsUnited States
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Abdullah KutlarSecura Bio, Inc.RecruitingSickle Cell DiseaseUnited States
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Sangamo TherapeuticsEnrolling by invitationBlood and Lymphatic DiseasesUnited States
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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Diane GeorgeActive, not recruitingAcute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Chronic Myeloid Leukemia (CML) | Juvenile Myelomonocytic Leukemia (JMML) | Lymphoma (Hodgkin's and Non-Hodgkin's)United States
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University of British ColumbiaCompletedSickle Cell Disease | Beta-Thalassemia | Sickle Cell Trait | Sickle Cell-Beta Thalassemia | Sickle Cell-SS DiseaseCanada, Nepal
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LGDProRelix Services LLPActive, not recruiting
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WestatEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Pediatric CancerUnited States, Brazil
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National Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationSickle Cell Anemia | Sickle Beta Thalassemia | Sickle Cell Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Pain | Hbss | Hbsc | Sickle Cell Syndrome VariantUnited States
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Klein Buendel, Inc.National Institute on Minority Health and Health Disparities (NIMHD); Hilton...CompletedSickle Cell Disease | Sickle Cell Anemia in Children | Sickle Cell Thalassemia | Sickle Cell SC DiseaseUnited States
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Timothy OlsonActive, not recruitingSickle Cell Disease | Thalassemia MajorUnited States
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Emory UniversityBristol-Myers Squibb; Thrasher Research Fund; Sickle Cell Transplant Advocacy... and other collaboratorsActive, not recruitingGraft Versus Host DiseaseUnited States
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Sanguine BiosciencesCompletedDepression | Melanoma | Epilepsy | Lymphoma | Multiple Sclerosis | Kidney Cancer | Cervical Cancer | Diabetes Mellitus | Leukemia | Breast Cancer | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Parkinson's Disease | Systemic Lupus Erythematosus | Multiple Myeloma | Hepatitis B | Insomnia | Colorectal Cancer | HIV/AID... and other conditionsUnited States
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PfizerActive, not recruitingSickle Cell DiseaseUnited States, Oman, United Kingdom, France, Egypt, Ghana, Italy, Kenya, Nigeria, Saudi Arabia
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Roswell Park Cancer InstituteActive, not recruitingAcute Myeloid Leukemia | Polycythemia Vera | Myelofibrosis | Chronic Myelomonocytic Leukemia | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Secondary Acute Myeloid Leukemia | Sickle Cell Disease | Myelodysplastic Syndrome | Plasma Cell Myeloma | Chronic Granulomatous... and other conditionsUnited States
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PfizerActive, not recruitingSickle Cell DiseaseUnited States, Lebanon, United Kingdom, Oman, Turkey, Canada, Egypt, Kenya, France, Italy, Netherlands
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
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City of Hope Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Active, not recruitingSickle Cell Disease | Anemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Sickle Cell DisorderUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany