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- US Clinical Trials Registry
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Search clinical trials for: Spinal Muscular Atrophy
Total 22877 results
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); St. Jude Children... and other collaboratorsEnrolling by invitationAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia | Multisystem ProteinopathyUnited States, South Africa, Germany
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...Active, not recruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | ALS-Frontotemporal DementiaUnited States
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Hoffmann-La RocheActive, not recruitingSpinal Muscular AtrophyBelgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
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Hoffmann-La RocheActive, not recruitingMuscular Atrophy, SpinalUnited States, Belgium, Brazil, Russian Federation, Australia, Taiwan, Poland
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BiogenEnrolling by invitationMuscular Atrophy, SpinalUnited States, Spain, Taiwan, Chile, Saudi Arabia, Brazil, Russian Federation, Mexico, Germany, Estonia, Japan, Canada, Colombia, Lebanon, Poland, Italy, China
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Hospital Israelita Albert EinsteinBiogenActive, not recruitingSpinal Muscular AtrophyBrazil, Argentina, Chile, Colombia, Mexico, Uruguay
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Hadassah Medical OrganizationActive, not recruitingNeurodegenerative DisordersIsrael
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Grand Valley State UniversityActive, not recruitingCerebral Palsy | Spinal Cord Injuries | Spinal Muscular Atrophy | Genetic Disease | Spina Bifida | Development DelayUnited States
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Novartis PharmaceuticalsActive, not recruitingType 2 Spinal Muscular AtrophyUnited States, China, Saudi Arabia, Thailand, Singapore, Brazil, Malaysia, Taiwan, Colombia, Mexico, Denmark, Egypt, India, South Africa, Vietnam
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedMuscular Atrophy, Spinal | UltrasoundItaly
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Charite University, Berlin, GermanyMax Planck Institute for Infection BiologyCompletedAmyotrophic Lateral Sclerosis (ALS)Germany
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Centre Hospitalier Universitaire de NiceActive, not recruitingSpinal Muscular AtrophyFrance
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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University of AlbertaWithdrawnHealthy | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Muscular Atrophy, ProgressiveCanada
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Clinic for Special ChildrenGenentech, Inc.Active, not recruitingSpinal Muscular AtrophyUnited States
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BiogenCompletedSpinal Muscular AtrophyGermany
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BiogenCompletedSpinal Muscular AtrophyUnited States, Spain, Germany, United Kingdom, Australia, Japan, Canada, Belgium, France, Hong Kong, Italy, Korea, Republic of, Sweden, Turkey
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Nemours Children's ClinicCompletedMuscular Dystrophy | Spinal Muscular Atrophy | Arthrogryposis
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Novartis PharmaceuticalsActive, not recruitingSpinal Muscular AtrophyJapan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands
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Duke UniversityCReATe Consortium (funded by NIH/NCATS/NINDS)CompletedAmyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, France, Brazil, Croatia, Italy, Russian Federation, Saudi Arabia, Serbia, Switzerland, Turkey, Ukraine, Poland
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AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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Hospices Civils de LyonCompletedSpinal Muscular AtrophyFrance
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Istanbul Medipol University HospitalActive, not recruitingMuscular Atrophy, SpinalTurkey
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Novartis PharmaceuticalsCompleted
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BiogenActive, not recruitingMuscular Atrophy, SpinalUnited States, Spain, Germany, Italy, Israel
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BiogenCompletedMuscular Atrophy, SpinalChina
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Catalyst Pharmaceuticals, Inc.TerminatedSpinal Muscular Atrophy Type 3Italy
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University College London HospitalsCompletedDistal Hereditary Motor Neuropathy, Type II | Distal Hereditary Motor Neuropathy, Type V | Distal Hereditary Motor Neuronopathy Type I | Distal Hereditary Motor Neuronopathy Type VIUnited Kingdom
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University Hospital, Basel, SwitzerlandEnrolling by invitationSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIISwitzerland
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Novartis PharmaceuticalsCompletedMuscular Atrophy, SpinalBrazil, Argentina
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Biohaven Pharmaceuticals, Inc.Active, not recruitingNeuromuscular Diseases | Spinal Muscular Atrophy | SMAUnited States, Netherlands, United Kingdom, Spain, Czechia, Belgium, Germany, Italy, Poland
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2 | Anti-myostatinUnited States, Germany, Belgium, Spain, United Kingdom, Netherlands, France, Italy, Poland
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Centre Hospitalier Régional de la CitadelleCompletedSafety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 (EMOTAS)Spinal Muscular Atrophy Type 3Belgium
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Dr. Stéphanie DelstancheQueen Fabiola Children's University Hospital; Erasme University Hospital; SYSNAV and other collaboratorsActive, not recruiting
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Cystinose StiftungLabor Becker & Kollegen, Munich, Germany; Screening Labor Hannover; Genetikum... and other collaboratorsCompletedSpinal Muscular Atrophy | Cystinosis | Cystinosis, NephropathicGermany
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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Eisai Co., Ltd.CompletedAmyotrophic Lateral Sclerosis (ALS)Japan
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Eisai Co., Ltd.CompletedAmyotrophic Lateral Sclerosis (ALS)Japan
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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BiogenActive, not recruitingSpinal Muscular AtrophyUnited States, Taiwan, Israel, Australia, Qatar, United Kingdom, Turkey, Italy, Germany, Argentina, Canada
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyBelgium, Germany, Italy, Russian Federation, Poland, Bulgaria, Denmark
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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Ohio State UniversityCompletedSpinal Cord Injuries | Metabolic Disease | Skeletal Muscle AtrophyUnited States
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Columbia UniversityThe Spinal Muscular Atrophy FoundationCompleted
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Synchron Medical, Inc.WithdrawnParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Neurologic Disorder | Spinal Muscular Atrophy | Spinal Cord Injury | Stroke, Lacunar | Upper Limb Injury | Paralysis; Stroke | Stroke, BrainstemAustralia
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Northwell HealthCompletedAdult Spinal Muscular AtrophyUnited States