Search clinical trials for: Splicing-mutation-mediated Cystic Fibrosis

Total 6326 results

Hadassah Medical Organization

Completed

Efficacy and Safety Study of EGCG/Tocotrienol in 18 Patients With Splicing-mutation-mediated Cystic Fibrosis (CF)

Cystic Fibrosis

Israel
SpliSense Ltd.

Recruiting

Safety, Tolerability, Pharmacokinetics, and Preliminary Efficacy of SPL84 in Patients With Cystic Fibrosis

Cystic Fibrosis

United States
Children's Hospital Los Angeles

Not yet recruiting

Maralixibat in Patients With Cystic Fibrosis and Constipation, A Within-Subjects Pilot Study

Cystic Fibrosis | Constipation Chronic Idiopathic

United States
Ospedale San Raffaele
Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico

Recruiting

Identification of New Biological Markers for the Progression of Mycobacterium Abscessus-induced Lung Disease in Cystic Fibrosis (BioMol-MA)

Non-Tuberculous Mycobacterial Pneumonia | Cystic Fibrosis Lung

Italy
Groupe Hospitalier de la Region de Mulhouse et...

Not yet recruiting

Frequency-time Analysis of Pathological Lung Sounds: Detection and Quantification of Pathological Sounds in Patients With Cystic Fibrosis, Pulmonary Fibrosis or COPD (Chronic Obstructive Pulmonary Disease) (ATF/SPP)

Chronic Obstructive Pulmonary Disease | Pulmonary Fibrosis | Cystic Fibrosis
Hospices Civils de Lyon

Recruiting

Circadian Rhythm Disorders in Children With Cystic Fibrosis Under CFTR (Cystic Fibrosis Transmembrane Conductance Regulator) Modulators (CHRONO-MUCO)

Cystic Fibrosis

France
Centre Hospitalier Universitaire de la Réunion

Recruiting

Pathogenicity of Species of the Achromobacter Genus in Patients From Reunion Island With Cystic Fibrosis (ACHROMO-MUCO)

Cystic Fibrosis

Réunion
Centre Hospitalier Intercommunal Creteil
Assistance Publique - Hôpitaux de Paris

Not yet recruiting

Comparison of Two Antibiotic Regimens for the Treatment of Early Airways Infection With PA in Adults With Bronchiectasis (ANTEIPA)

Bronchiectasis

France
University of Kansas Medical Center

Recruiting

Targeting Inflammation With Losartan to Improve Response to Modulator Therapy in Cystic Fibrosis.

Cystic Fibrosis

United States
Assistance Publique - Hôpitaux de Paris
Vaincre la Mucoviscidose

Not yet recruiting

Oral Health Status of Cystic Fibrosis Patients. An Online Survey in Collaboration With the Vaincre la Mucoviscidose Patient Association. (E-MUCODENT)

Cystic Fibrosis

France
Assiut University

Not yet recruiting

Procalcitonin as a Marker of Severity of Non-cystic Fibrosis Bronchiectasis in Children

Non-cystic Fibrosis Bronchiectasis
Emory University
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

Recruiting

A Pilot and Feasibility Study to Evaluate High vs Low Glycemic Index Mixed Meal Tolerance Test in Adolescents and Young Adults With Cystic Fibrosis

Cystic Fibrosis

United States
Centre Hospitalier Intercommunal Creteil

Not yet recruiting

Real World Environmental Exposure Study With Healthy and Cystic Fibrosis Subjects (ExpoCF)

Environmental Exposure | Cystic Fibrosis, Pulmonary | Exhaled Breath Condansate
Children's Hospital Medical Center, Cincinnati

Recruiting

Regional Monitoring of CF Lung Disease

Cystic Fibrosis

United States
University Hospital, Strasbourg, France

Not yet recruiting

Effect of One Year Elexacaftor-tezacaftor-ivacaftor Treatment (DIATRIM)

Cystic Fibrosis
Pole Sante Grace de Dieu

Recruiting

Improving the Well-being of Caregivers of Cystic Fibrosis Patients During Physiotherapy Treatment (MucoZar)

Cystic Fibrosis

France
Universidad Politecnica de Madrid
Hospital Infantil Universitario Niño Jesús, Madrid, Spain; Hospital Universitario... and other collaborators

Recruiting

Exercise in People With Cystic Fibrosis on CFTR Modulator Therapy (FIQMODE)

Cystic Fibrosis

Spain
Daniel J. Weiner

Recruiting

Intrapulmonary Percussive Ventilation for Sputum Induction in Adults With Cystic Fibrosis

Cystic Fibrosis

United States
University of Valencia
Asociación de Fibrosis Quística - Comunidad Valenciana

Not yet recruiting

e-Health Program to Prevent Exacerbations in the Cystic Fibrosis Population

Cystic Fibrosis

Spain
Halic University

Recruiting

Effect of Parental Attitude on Functional and Physical Level of Children With Cystic Fibrosis

Cystic Fibrosis | Cystic Fibrosis in Children

Turkey
Hôpital Necker-Enfants Malades

Not yet recruiting

Assessment of Patients Not Concluded After Neonatal Screening of Cystic Fibrosis.

CFTR-RD
Region Stockholm
Karolinska Institutet

Recruiting

CFTR Modulators in Pregnancy and Postpartum

Cystic Fibrosis

Sweden
University of Pittsburgh
National Heart, Lung, and Blood Institute (NHLBI); Cystic Fibrosis Foundation

Recruiting

Health Outcomes of Parents With Cystic Fibrosis-Aim 2 (HOPeCF)

Cystic Fibrosis | Parenthood Status

United States
Halic University

Recruiting

Development,Validity and Reliability of a Caregiver Version of the Breathlessness Beliefs Questionnaire

Cystic Fibrosis | Parents

Turkey
Oslo University Hospital

Recruiting

Quality of Life and Gut Health in Pediatric Patients With Cystic Fibrosis

Cystic Fibrosis in Children

Norway
Kirsehir Ahi Evran Universitesi
TC Erciyes University

Not yet recruiting

An Intervention-Based Approach to Strengthen the Psychological Health of Children With Cystic Fibrosis and Their Mothers

Children | Cystic Fibrosis | Lung Functions | Mothers | Laughter Yoga | Laughter Therapy | Resilience,Psychological | Psychological Health

Turkey
Sanofi
Regeneron Pharmaceuticals

Recruiting

A Proof-of-Concept Study to Assess the Efficacy, Safety and Tolerability of Itepekimab (Anti-IL-33 mAb) in Participants With Non-cystic Fibrosis Bronchiectasis

Bronchiectasis

United Kingdom, Japan, United States, Israel, Canada
Pilar Azevedo
Queen's University, Belfast; Medical University Innsbruck; Cystic Fibrosis Foundation and other collaborators

Recruiting

COVID-19 Antibody Responses In Cystic Fibrosis (CAR-CF)

COVID-19 | Cystic Fibrosis

Portugal
Pole Sante Grace de Dieu

Recruiting

French Validation of the AdT-Physio Scale (Trans-AdT)

Cystic Fibrosis

France
Hospices Civils de Lyon

Recruiting

Muscle Function and Physical Activity in the Modern Era of Cystic Fibrosis (MUCOMUSCLE)

Cystic Fibrosis

France
University of North Carolina, Chapel Hill
Cystic Fibrosis Foundation

Recruiting

Hypertonic Saline in NCFB

Bronchiectasis | Non-cystic Fibrosis Bronchiectasis

United States
ReCode Therapeutics

Recruiting

A Phase 1 Study Evaluating Safety and Tolerability of RCT2100 in Healthy Participants

Cystic Fibrosis

New Zealand
Physio-Assist
Medical University of Lodz; University Hospital in Krakow

Recruiting

Simeox Therapy at Home Versus Standard of Care in NCFB Patients With CMH

Non-cystic Fibrosis Bronchiectasis | Chronic Mucus Hypersecretion

Poland
Papworth Hospital NHS Foundation Trust
Innovate UK; Cystic Fibrosis Trust; US Cystic Fibrosis Foundation

Recruiting

Analysis of Remote Monitoring/Virtual Clinic Data in Adult Patients With Cystic Fibrosis (Project Breathe)

Cystic Fibrosis

United Kingdom
Boston Children's Hospital
Cystic Fibrosis Foundation

Recruiting

Skeletal Health and Bone Marrow Composition in Adolescents With Cystic Fibrosis

Cystic Fibrosis

United States
Hospices Civils de Lyon

Recruiting

Renal Impact of KAFTRIO in Mucoviscidose Population (IRT-MUCO)

Cystic Fibrosis

France
University of California, Los Angeles
University of Iowa; Children's Hospital Colorado; University of Kansas Medical... and other collaborators

Recruiting

Sinus Disease in Young Children With Cystic Fibrosis

Chronic Rhinosinusitis (Diagnosis) | Cystic Fibrosis | Olfactory Disorder | Cystic Fibrosis in Children | Olfactory Impairment

United States
Hacettepe University

Recruiting

Assessment of Cognitive Function and Exercise Capacity in Cystic Fibrosis

Cystic Fibrosis

Turkey
National Cancer Institute (NCI)

Recruiting

Dinutuximab With Chemotherapy, Surgery and Stem Cell Transplantation for the Treatment of Children With Newly Diagnosed High Risk Neuroblastoma

Neuroblastoma | Ganglioneuroblastoma

United States
University of California, San Francisco

Recruiting

Impact of Support Groups for Patients With Non-Cystic Fibrosis Bronchiectasis (BronchConnect)

Non-cystic Fibrosis Bronchiectasis

United States
University of Cincinnati

Recruiting

Hormonal Responses to a Mixed Meal in People With Cystic Fibrosis

Cystic Fibrosis

United States
Clarametyx Biosciences, Inc.

Recruiting

A Study To Evaluate The Safety Of CMTX-101 In People With Cystic Fibrosis

Cystic Fibrosis | Persistent Infection

United States
Postgraduate Institute of Medical Education and...

Recruiting

Compare Oral Itraconazole and Standard Care Versus Standard Care Alone in Patients With Non-cystic Fibrosis Related Bronchiectasis With Chronic Aspergillus Infection in Reducing Bronchiectasis Exacerbations (BAIT)

Bronchiectasis | Bronchiectasis Adult

India
Vertex Pharmaceuticals Incorporated

Recruiting

A Phase 1, First-in-human Study of VX-828

Cystic Fibrosis

United States
Papworth Hospital NHS Foundation Trust
LifeArc

Not yet recruiting

Early Detection of Pulmonary Exacerbations in Non-cystic Fibrosis Bronchiectasis (Bronch-EX)

Non-cystic Fibrosis Bronchiectasis

United Kingdom
Amir Moheet

Recruiting

SGLT2 Inhibitor Therapy in Cystic Fibrosis-related Diabetes

Cystic Fibrosis | Cystic Fibrosis-related Diabetes

United States
Ad scientiam
Vertex Pharmaceuticals Incorporated

Not yet recruiting

Performances and Safety of MuCopilot, a Digital Tool for the Unsupervised Objective Assessment of Cystic Fibrosis (MuControl)

Cystic Fibrosis

France
Assistance Publique - Hôpitaux de Paris

Not yet recruiting

Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders (DANNIgene)

Hemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditions

France
CHU de Reims

Recruiting

Cystic Fibrosis and Periodontal Diseases (MucoParo)

Periodontitis | Gingivitis | Cystic Fibrosis

France
Ad scientiam

Not yet recruiting

A Usability Validation of the MuCopilot Mobile Application, a Digital Tool for the Unsupervised Objective Assessment of Cystic Fibrosis (MuControl-Sum)

Cystic Fibrosis

France

Search clinical trials for: Splicing-mutation-mediated Cystic Fibrosis

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