- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Wolman Disease (early onset LAL Deficiency)
Total 381653 results
-
National Heart and Lung InstituteWexham Park Hospital; 4th Military HospitalUnknownHeart Diseases | Anemia, Iron-Deficiency | Chronic Heart FailurePoland, United Kingdom
-
Assistance Publique - Hôpitaux de ParisCompletedUrinary Incontinence by Intrinsic Sphincter DeficiencyFrance
-
Continuity Research NetworkCompletedHealth Knowledge, Attitudes, PracticeUnited States
-
University of PittsburghHorizon Pharma Ireland, Ltd., Dublin IrelandCompletedMedium-chain Acyl-CoA Dehydrogenase (MCAD) DeficiencyUnited States
-
Hospices Civils de LyonUnknownLiver Post-transplant PatientsFrance
-
Mahidol UniversityUnknownDiabetes Mellitus | Metabolic SyndromeThailand
-
University of California, DavisUniversidad Peruana Cayetano Heredia; Asociacion Civil Selva AmazonicaCompletedIron-deficiency | Anemia | Iron Deficiency Anemia
-
Ludwig-Maximilians - University of MunichCompletedChild | Iron Deficiency | Iron-deficiency AnemiaGermany
-
Avera McKennan Hospital & University Health CenterCompletedEvaluate the Change in Iron, Vitamin D, and C-Reactive Protein Level (CRP) in a 12 to 24 Week PeriodAnemia | Vitamin D DeficiencyUnited States
-
Pharmacosmos A/SMax Neeman InternationalCompletedInflammatory Bowel DiseaseUnited Kingdom, Denmark, India
-
RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
-
Merz North America, Inc.CompletedFemale Stress Urinary Incontinence Due to Intrinsic Sphincter DeficiencyUnited States
-
Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
-
Shield TherapeuticsRecruitingIron-deficiency | AnemiaUnited States, United Kingdom, Puerto Rico
-
Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingSuccinic Semialdehyde Dehydrogenase DeficiencyUnited States, United Kingdom, Germany, Spain
-
Texas Tech University Health Sciences Center, El...CompletedIron-deficiency | Iron Deficiency Anemia | Iron Deficiency Anemia Treatment | Iron Deficiency Anemia Due to Blood LossUnited States
-
BioMarin PharmaceuticalActive, not recruiting
-
Baxalta now part of ShireCompletedHemophilia AUnited States, Canada, Puerto Rico
-
GWT-TUD GmbHVifor PharmaCompletedType 2 Diabetes Mellitus | Iron DeficiencyGermany
-
Eunice Kennedy Shriver National Institute of Child...University of IowaCompleted
-
Ajou University School of MedicineUnknown
-
Children's Hospital of PhiladelphiaCompleted
-
LG Life SciencesBioPartners GmbHCompletedAdult Growth Hormone Deficiency | Pituitary Disorders
-
Ultragenyx Pharmaceutical IncTerminatedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States
-
Trent StellingwerffUniversity of British Columbia; MitacsRecruitingNutrition Disorders | Health, Subjective | Cardiovascular Abnormalities | Bone Loss | Athletic Injuries | Mental Health Wellness 1 | Eating Disorders | Hormone Disturbance | Sleep Hygiene | Weight Change, Body | Bone Fracture | Exercise-related AmenorrheaCanada
-
Rare Thyroid Therapeutics International ABErasmus Medical CenterActive, not recruitingAllan-Herndon-Dudley SyndromeUnited States, Netherlands, Czechia, Germany
-
Rocket Pharmaceuticals Inc.Active, not recruiting
-
TESS Research FoundationStanford UniversityEnrolling by invitationEpilepsy | Movement Disorders | Rare Diseases | Genetic Disorder | Citrate Transporter Deficiency | SLC13A5 Deficiency | EIEE25 | Kohlschutter-Tonz Syndrome (Non-ROGDI) | 17p13.1 Deletions Confined to SLC13A5 Gene | Citrate Transporter DisorderUnited States
-
Roy E. Weiss, M.D.AvailableMct8 (Slc16A2)-Specific Thyroid Hormone Cell Transporter DeficiencyUnited States
-
Shiraz University of Medical SciencesCompleted
-
Taipei Veterans General Hospital, TaiwanBioMarin PharmaceuticalUnknownPAH Deficiency | Pku Phenylketonuria
-
Iuliu Hatieganu University of Medicine and PharmacyUnknownAnemia, Iron Deficiency | Anemia of Chronic DiseaseRomania
-
University of MinnesotaUniversity of HawaiiCompletedIron-deficiency | Iron Deficiency Anemia | Iron Deficiency (Without Anemia)United States
-
Beijing University of Chinese MedicineUnknownGastric Cancer | Gastritis, Atrophic
-
Klinikum der Universitaet Muenchen, GrosshadernCompleted
-
Creighton UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Completed
-
National Institute of Diabetes and Digestive and...Genentech, Inc.Completed
-
Texas A&M UniversityUnknownCognitive Change | Nutritional Anemia | Diet, Healthy | Nutrient Deficiency | Diet; Deficiency | Visual Spatial Processing | Dietary Deficiency | Dietary B12 Deficiency | Dietary Zinc Deficiency | Dietary Vitamin B12 Deficiency Anemia | Dietary Deficiency of Selenium and Vitamin EUnited States
-
Vanderbilt University Medical CenterCompleted
-
Bio Products LaboratoryTerminatedFactor X DeficiencyUnited Kingdom, United States, Spain, Turkey
-
Instituto Nacional de Salud Publica, MexicoCompletedAnemia | Iron Deficiency | StuntingMexico
-
SourseCitruslabsActive, not recruitingMood | Energy Supply; Deficiency | B12 Deficiency VitaminUnited States
-
Vinmec Research Institute of Stem Cell and Gene...Not yet recruitingSexual Dysfunction FemaleVietnam
-
Rhythm Pharmaceuticals, Inc.CompletedPOMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityTurkey
-
University of California, DavisUniversity of California, San Francisco; University of Rhode Island; Ethiopian... and other collaboratorsEnrolling by invitationVitamin B 12 Deficiency | Folate Deficiency | Iodine Deficiency | Anemia Deficiency | Salt Intake | Anemia MacrocyticEthiopia
-
Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
-
Assiut UniversityNot yet recruitingHeavy Menstrual Bleeding
-
Walid Ahmed Ragab AbdelhamidCompleted
-
London School of Hygiene and Tropical MedicineUniversity of OxfordUnknown
-
University of Colorado, DenverEunice Kennedy Shriver National Institute of Child Health and Human Development...Completed