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Search clinical trials for: Wolman syndrome
Total 37275 results
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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Alexion PharmaceuticalsTerminatedLysosomal Acid Lipase DeficiencyUnited Kingdom, Finland, United States, Italy
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Masonic Cancer Center, University of MinnesotaCompletedWolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Sanfilippo Syndrome | GM1 Gangliosidosis | Globoid Cell Leukodystrophy | Tay Sachs Disease | Sandhoffs Disease | I-Cell DiseaseUnited States
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Alexion PharmaceuticalsCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited Kingdom, France, United States, Egypt, Ireland
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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Masonic Cancer Center, University of MinnesotaCompletedLysosomal Storage Disease | Peroxisomal DisorderUnited States
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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SpinogenixAvance Clinical Pty Ltd.Not yet recruiting
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Brooklyn Clinical ResearchNot yet recruitingCardiovascular Diseases | Obesity | Metabolic Syndrome | PreDiabetes | Diabetes Type 2United States
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IRCCS Ospedale San RaffaeleNot yet recruitingRare Diseases | Corneal Neovascularization | Limbal Stem Cell Deficiency | Aniridia | Neurotrophic Keratopathy | Ocular Cicatricial Pemphigoid | Ocular Graft-versus-host Disease | EEC Syndrome
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Charles Darwin UniversityThe Affiliated Hospital Of Southwest Medical University; Zunyi Medical College and other collaboratorsNot yet recruitingBreast Neoplasm Female | Symptom Cluster
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United States Naval Medical Center, San DiegoMinneapolis Veterans Affairs Medical Center; United States Department of Defense and other collaboratorsNot yet recruitingBrain Injuries | Brain Injuries, Traumatic | Brain Concussion | Mild Cognitive Impairment | Memory Impairment | Mild Traumatic Brain Injury | Attention Impaired | Neurocognitive Dysfunction | Brain Trauma | Attention Concentration Difficulty | Post Concussive SymptomsUnited States
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Magnus SimrénRecruitingIrritable Bowel Syndrome | Food SensitivitySweden
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SleepRes Inc.Not yet recruiting
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Axsome Therapeutics, Inc.RecruitingObstructive Sleep Apnea | Narcolepsy | Pregnant Women and Their OffspringUnited States
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Ainsworth Institute of Pain ManagementSaluda Medical Pty LtdRecruitingPudendal Neuralgia | Chronic Pelvic PainUnited States
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Masonic Cancer Center, University of MinnesotaNot yet recruitingAcquired Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Acquired Amegakaryocytic Thrombocytopenia
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Jordan Collaborating Cardiology GroupCardiovascular Academy; The Association of Jordanian Medical Laboratory Specialists...Not yet recruitingCardiovascular-renal-metabolic SyndromeJordan
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China National Center for Cardiovascular DiseasesNot yet recruitingAerobic Exercise | M-health | OSAHS | Oropharyngeal Muscle Training | Comprehensive Physical Therapy
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Charite University, Berlin, GermanyAlmond Board of CaliforniaNot yet recruiting
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Peking Union Medical College HospitalShengjing Hospital; The Affiliated Hospital of Qingdao University; Children's... and other collaboratorsRecruitingPediatric ALL | Sjogren's SyndromeChina
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Radboud University Medical CenterCanisius-Wilhelmina Hospital; Donders Centre for Cognitive NeuroimagingNot yet recruitingDystonia | Tremor | Dystonic Tremor Syndrome
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Novartis PharmaceuticalsNot yet recruitingParoxysmal Nocturnal Hemoglobinuria
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Novartis PharmaceuticalsNot yet recruitingSystemic Lupus Erythematosus | Sjogren Disease
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Cairo UniversityNot yet recruiting
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Guang'anmen Hospital of China Academy of Chinese...Recruiting
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Kahramanmaras Sutcu Imam UniversityNot yet recruiting
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University Medical Center, KazakhstanNazarbayev University; Astana Medical University; Ministry of Science and Higher... and other collaboratorsRecruitingMetabolic SyndromeKazakhstan
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Dompé Farmaceutici S.p.ARecruitingDry Eye | Sjögren SyndromeUnited States
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St George's, University of LondonMU-JHU CARE; Biomedical Research and Training Institute, ZimbabweRecruitingNeonatal SepsisUganda, United Kingdom
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Konstantinos ToutouzasUniversité Catholique de Louvain; University of Patras; Centre Hospitalier Universitaire... and other collaboratorsNot yet recruitingCoronary Artery Disease | Acute Coronary SyndromeBelgium, Greece
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Dokuz Eylul UniversityNot yet recruitingSubacromial Pain Syndrome
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Education University of Hong KongThe Hong Kong Polytechnic UniversityNot yet recruitingCaregiver Stress Syndrome
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Assistance Publique - Hôpitaux de ParisCentre Leon Berard; Institut National de la Santé Et de la Recherche Médicale... and other collaboratorsNot yet recruitingEnvironmental Exposure | SDH Gene Mutation | SDH-Related Familial Paraganglioma | SDHx-Related SyndromesFrance
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Johns Hopkins UniversityNational Center for Complementary and Integrative Health (NCCIH); Bowdoin CollegeRecruitingTourette Syndrome | Tic Disorders | Tourette's Disorder | Persistent Tic Disorder | Chronic Motor Tic Disorder | Chronic Vocal Tic Disorder | Persistent Motor Tic Disorder | Persistent Vocal Tic DisorderUnited States
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NovavaxNot yet recruitingSevere Acute Respiratory Syndrome Coronavirus 2 Infection
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Sohag UniversityRecruitingAcute Coronary Syndrome | Subclinical hypothyroïdismEgypt
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The First Affiliated Hospital of Soochow UniversitySoochow UniversityRecruitingIrritable Bowel Syndrome | Functional Magnetic Resonance Imaging | Repetitive Transcranial Magnetic Stimulation | Chronic Visceral PainChina
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Rigshospitalet, DenmarkNot yet recruitingBronchiectasis | Bronchopulmonary Dysplasia (BPD) | Tracheomalacia | Cystic Lung Disease | Vascular Ring | Chronic Atelectasis
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Riphah International UniversityNot yet recruiting
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Chang Gung Memorial HospitalRecruitingDry Eye Syndromes | Sjogren's SyndromeTaiwan
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Riphah International UniversityNot yet recruitingQuadratus Lumborum SyndromePakistan
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SleepRes Inc.Not yet recruiting
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Riphah International UniversityRecruitingUpper Crossed SyndromePakistan
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Hanoi Medical UniversityRecruitingTooth Abnormalities | Tooth Injuries | Teeth, Endodontically-Treated | Tooth Fracture | Tooth Crowding | Dislocation, Tooth | Cracked Tooth SyndromeVietnam
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Riphah International UniversityRecruitingPronation Deformity of the FootPakistan
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University Hospital of CreteRecruitingDietary Habits | Cholelithiases | Postcholecystectomy Syndrome | Gallstone Disease | Gallstone; Colic | Gallstone; Cholecystitis, AcuteGreece