- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: bi-allelic glucocerebrosidase-1
Total 46669 results
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National Center for Research Resources (NCRR)University of PittsburghUnknownGaucher's DiseaseUnited States
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ProtalixCompleted
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National Institute of Neurological Disorders and...CompletedGaucher's DiseaseUnited States
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Assistance Publique - Hôpitaux de ParisRecruitingDementia With Lewy BodiesFrance
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PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, Israel, Mexico, Russian Federation, Argentina, Italy
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain
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ShireCompleted
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ProtalixCompleted
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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PfizerCompletedGaucher DiseaseIsrael, Paraguay, South Africa
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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ProtalixCompleted
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National Center for Research Resources (NCRR)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...Completed
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ShireApproved for marketingGaucher Disease, Type 1United States
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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PfizerNo longer availableGaucher DiseaseUnited States, Israel
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ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
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ShireCompletedGaucher Disease, Type 3Egypt, India, Tunisia
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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National Institute of Mental Health (NIMH)Completed
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ShireCompletedGaucher DiseaseUnited States, Israel, United Kingdom, Poland, Spain
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Northwell HealthMichael J. Fox Foundation for Parkinson's Research; The Silverstein Foundation...RecruitingParkinson's DiseaseUnited States
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ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
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Ankara Yildirim Beyazıt UniversityRecruitingStroke | Exoskeleton Device | LocomotionTurkey
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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National Institute of Neurological Disorders and...CompletedType 2 Gaucher DiseaseUnited States
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Agyany Pharma LTDRecruiting
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Tianjin Medical University Cancer Institute and...Recruiting
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University of LiegeUnknown
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Hasan Kalyoncu UniversityRecruiting
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Suleyman Demirel UniversityRecruitingShoulder Injuries | Shoulder Pain | Shoulder LesionsTurkey
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National Human Genome Research Institute (NHGRI)Enrolling by invitationParkinson Disease | Gaucher Disease | Lysosomal Storage DisordersUnited States
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EZUS-LYON 1Active, not recruiting
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EZUS-LYON 1Active, not recruitingElderly | Gait | Balance, PosturalFrance
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Eastern Mediterranean UniversityNot yet recruitingQuality of Life | Health Education | Yoga | Menopause SymptomsCyprus
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Eastern Mediterranean UniversityNot yet recruitingPain | Anxiety | Coronary Angiography | Vital SignsCyprus
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Uro-1 MedicalRecruiting
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Uro-1 MedicalRecruiting
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Alpha-1 FoundationRecruiting
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Genzyme, a Sanofi CompanyCompletedCerebroside Lipidosis Syndrome | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease Type I | Clucocerebrosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States
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Cukurova UniversityNot yet recruitingPatient Acceptance of Health Care | Drug Compliance
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Taiho Pharmaceutical Co., Ltd.Completed
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Kitasato UniversityYokohama City University Medical Center; St. Marianna University School of... and other collaboratorsUnknownHypertension | Type 2 Diabetes MellitusJapan
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Uro-1 MedicalNot yet recruiting
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Children's Hospital 1RecruitingTotal Anomalous Pulmonary Venous Connection | Pulmonary Venous Stenosis | Sutureless ClosureVietnam