- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: bi-allelic glucocerebrosidase-1
Total 46837 results
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National Center for Research Resources (NCRR)University of PittsburghUnknownGaucher's DiseaseUnited States
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ProtalixCompleted
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National Institute of Neurological Disorders and...CompletedGaucher's DiseaseUnited States
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Assistance Publique - Hôpitaux de ParisRecruitingDementia With Lewy BodiesFrance
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PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, Israel, Mexico, Russian Federation, Argentina, Italy
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain, Germany
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ShireCompleted
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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ProtalixCompleted
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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PfizerCompletedGaucher DiseaseIsrael, Paraguay, South Africa
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ProtalixCompleted
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ShireApproved for marketingGaucher Disease, Type 1United States
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National Center for Research Resources (NCRR)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...Completed
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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PfizerNo longer availableGaucher DiseaseUnited States, Israel
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ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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ShireCompletedGaucher Disease, Type 3Egypt, India, Tunisia
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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National Institute of Mental Health (NIMH)Completed
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ShireCompletedGaucher DiseaseUnited States, Israel, United Kingdom, Poland, Spain
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Northwell HealthMichael J. Fox Foundation for Parkinson's Research; The Silverstein Foundation...RecruitingParkinson's DiseaseUnited States
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ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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Ankara Yildirim Beyazıt UniversityRecruitingStroke | Exoskeleton Device | LocomotionTurkey
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National Institute of Neurological Disorders and...CompletedType 2 Gaucher DiseaseUnited States
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Tianjin Medical University Cancer Institute and...Recruiting
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Agyany Pharma LTDRecruiting
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University of LiegeUnknown
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Hasan Kalyoncu UniversityRecruiting
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National Human Genome Research Institute (NHGRI)Enrolling by invitationParkinson Disease | Gaucher Disease | Lysosomal Storage DisordersUnited States
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Suleyman Demirel UniversityRecruitingShoulder Injuries | Shoulder Pain | Shoulder LesionsTurkey
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EZUS-LYON 1Active, not recruiting
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EZUS-LYON 1Active, not recruitingElderly | Gait | Balance, PosturalFrance
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Uro-1 MedicalRecruiting
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Uro-1 MedicalRecruiting
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Alpha-1 FoundationRecruiting
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Genzyme, a Sanofi CompanyCompletedCerebroside Lipidosis Syndrome | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease Type I | Clucocerebrosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States
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Eastern Mediterranean UniversityNot yet recruitingQuality of Life | Health Education | Yoga | Menopause SymptomsCyprus
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Eastern Mediterranean UniversityNot yet recruitingPain | Anxiety | Coronary Angiography | Vital SignsCyprus
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Taiho Pharmaceutical Co., Ltd.Completed
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OSCAR StudyJapan Heart FoundationCompletedCardiovascular Diseases | HypertensionJapan
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Uro-1 MedicalNot yet recruiting
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Children's Hospital 1RecruitingTotal Anomalous Pulmonary Venous Connection | Pulmonary Venous Stenosis | Sutureless ClosureVietnam
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Alpha-1 FoundationCompletedChronic Obstructive Pulmonary Disease | Alpha-1 Antitrypsin DeficiencyUnited States, Puerto Rico