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Search clinical trials for: chromosome
Total 2688 results
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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SpinogenixAvance Clinical Pty Ltd.Not yet recruiting
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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Riphah International UniversityNot yet recruiting
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Başak Çağla ArslanHacettepe UniversityRecruitingDuchenne Muscular Dystrophy | Occupational Therapy | GamificationTurkey
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M.D. Anderson Cancer CenterAscentage Pharma Group Inc.Not yet recruitingAdvanced Chronic Myeloid Leukemia | Philadelphia Chromosome-Positive Acute Myeloid LeukemiaUnited States
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CSL BehringNot yet recruiting
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Peking Union Medical College HospitalNot yet recruitingDuchenne Muscular Dystrophy (DMD)
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Institute of Hematology & Blood Diseases Hospital...Not yet recruitingPrecursor Cell Lymphoblastic Leukemia-Lymphoma
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Regeneron PharmaceuticalsIntellia TherapeuticsNot yet recruiting
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IRCCS Eugenio MedeaRecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Limb Girdle Muscular Dystrophy | Facio-Scapulo-Humeral DystrophyItaly
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University of Colorado, DenverChildren's Hospital ColoradoRecruitingSex Chromosome AneuploidyUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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Harmony Biosciences, LLCRecruiting
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University of MalagaNot yet recruitingMuscular Dystrophy | Duchenne Muscular Dystrophy | Becker Muscular DystrophySpain
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Seoul National University HospitalNot yet recruitingMuscular Dystrophy, Duchenne | Upper Extremity | Orthotic DevicesKorea, Republic of
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Rigshospitalet, DenmarkNot yet recruitingInfertilityDenmark
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IRCCS Eugenio MedeaRecruitingEpilepsy | Angelman Syndrome | Dup15q SyndromeItaly
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Hasan Kalyoncu UniversityRecruitingDown SyndromeTurkey
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Equilibra Bioscience LLCRecruitingHemophilia A | Hemophilia B | Healthy ParticipantsUnited States
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Federico II University; Istituto Auxologico Italiano; Università degli Studi...RecruitingBeckwith-Wiedemann SyndromeItaly
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Recruiting
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West China HospitalRecruiting
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama... and other collaboratorsRecruiting
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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IRCCS Eugenio MedeaRecruiting
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IRCCS San RaffaeleRecruiting
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Centre Hospitalier Sud FrancilienNot yet recruiting
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Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States
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Chiesi Farmaceutici S.p.A.ICON plcNot yet recruiting
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ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
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Meyer Children's Hospital IRCCSRecruiting
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Caroline Michaela KistorpSanofiNot yet recruitingChronic Kidney Diseases | Fabry DiseaseDenmark
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
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University of AarhusAarhus University HospitalRecruitingCardiovascular Diseases | Inflammation | Lymphedema | Turner SyndromeDenmark
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Qilu Hospital of Shandong UniversityRecruitingChild | Williams Syndrome | Neurodevelopmental DelayChina
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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Erasmus Medical CenterNot yet recruiting
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M.D. Anderson Cancer CenterNovartis PharmaceuticalsNot yet recruitingAcute Lymphoblastic Leukemia | Philadelphia Chromosome-PositiveUnited States
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Institute of Hematology & Blood Diseases Hospital...Recruiting
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PfizerNot yet recruitingChronic Leukemia Myelogenous
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Lise AksglædeNot yet recruitingKlinefelter Syndrome
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Istituto Auxologico ItalianoRecruitingPrader-Willi SyndromeItaly
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IRCCS Fondazione Stella MarisRecruitingFragile X SyndromeItaly
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IRCCS Fondazione Stella MarisRecruitingCreatine Deficiency, X-linked | Creatine Deficiency Syndrome Due to Gamt DeficiencyItaly
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Not yet recruitingMuscular Dystrophy | Exercise | Duchenne Muscular Dystrophy | Vasodilation | DMD | Muscular Dystrophy in Children | Duchenne Disease
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Memorial Sloan Kettering Cancer CenterRecruitingRefractory Acute Lymphoblastic Leukemia | Philadelphia-Negative ALL | Philadelphia-Positive ALL | Refractory Acute Lymphoblastic Leukemia (ALL) | Relapsed ALL, Adult | Refractory Acute Lymphoid Leukemia in RelapseUnited States
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InnoVec Biotherapeutics Inc.Peking Union Medical College HospitalRecruitingEye Diseases | Retinal Degeneration | Retinal Disease | RetinoschisisChina
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRecruitingFragile X SyndromeSerbia