- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: exon 53 skipping
Total 883 results
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Pierre Fabre Pharma GmbHPierre Fabre Pharma Austria; Pierre Fabre Pharma AGRecruitingMelanoma Stage IV | Melanoma Stage IIIAustria, Germany, Switzerland
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InDex PharmaceuticalsCompletedUlcerative ColitisHungary, Czechia, France, Germany, Poland, Russian Federation, Serbia, Spain, Sweden, Ukraine
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UCB Biopharma S.P.R.L.ParexelCompletedAxial SpondyloarthritisBelgium, Germany, Greece, Italy, Spain, United Kingdom
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UCB PharmaCompletedRheumatoid ArthritisGermany, United States, Argentina, Australia, Austria, Belgium, Canada, Colombia, Czechia, France, Hungary, Ireland, Italy, Mexico, Monaco, Netherlands, Poland, Romania, Spain, Sweden, Switzerland, United Kingdom
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UCB Pharma SACompletedEpilepsyBelgium, Finland, France, Germany, Hungary, India, Italy, Netherlands, Poland, Spain, Switzerland, United Kingdom
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UCB BIOSCIENCES GmbHPPDCompletedCrohn DiseaseRussian Federation, Belgium, United States, Australia, Austria, Brazil, Canada, Czechia, Estonia, Germany, Hungary, Israel, Italy, Latvia, New Zealand, Poland, Romania, Ukraine
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UCB Pharma SAParexelCompletedRheumatoid ArthritisRomania, United States, Australia, Austria, Bulgaria, Canada, Czechia, France, Germany, Greece, Hungary, Ireland, Italy, Mexico, Monaco, Poland, Portugal, Spain, Switzerland, United Kingdom
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UCB BIOSCIENCES, Inc.CompletedEpilepsyAustria, United States, Australia, Canada, Denmark, France, Germany, Ireland, Italy, Poland, Puerto Rico, Spain, United Kingdom
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UCB PharmaPivotal S.L.Completed
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UCB Pharma SACompletedRheumatoid ArthritisGermany, United States, Argentina, Australia, Austria, Belgium, Canada, Colombia, Czechia, France, Hungary, Ireland, Italy, Mexico, Monaco, Netherlands, Poland, Romania, Spain, Sweden, Switzerland, United Kingdom
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UCB Biopharma S.P.R.L.PRA Health SciencesCompletedIdiopathic Parkinson's DiseaseGermany, France, Italy, Spain, United Kingdom
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UCB Pharma GmbHCompletedRheumatoid ArthritisGermany
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UCB PharmaCompletedIdiopathic Parkinson's DiseaseGermany, Austria, Belgium, Bulgaria, Czech Republic, France, Hungary, Italy, Romania, Slovakia, Spain, Switzerland
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UCB PharmaCompletedRheumatoid ArthritisPoland, Germany, Austria, France, Italy
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UCB PharmaCompletedIdiopathic Parkinson's DiseaseGermany
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Northwestern UniversityCompletedCentral Centrifugal Cicatricial Alopecia | Scarring Alopecia | Central Centrifugal Scarring AlopeciaUnited States
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Stryker OrthopaedicsCompletedArthroplasty, Replacement, HipUnited States
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Kevin FlaniganSarepta Therapeutics, Inc.Completed
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National Center of Neurology and Psychiatry, JapanNippon Shinyaku Co., Ltd.Completed
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Oslo University HospitalCompleted
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Hospital Sao DomingosCompleted
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Kahramanmaras Sutcu Imam UniversityCompleted
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GenethonInstitute of MyologyUnknownDuchenne Muscular DystrophyUnited Kingdom, France
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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SynerGene Therapeutics, Inc.Completed
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Sarepta Therapeutics, Inc.University College, London; Catholic University of the Sacred Heart; University... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited Kingdom, United States, France, Italy
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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Cancer Institute and Hospital, Chinese Academy...RecruitingEndometrial Carcinoma | Recurrent or Metastatic | TP53 MutationChina
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Alexandria UniversityRecruitingLiver Cirrhosis | Hepatocellular Carcinoma | Diagnoses DiseaseEgypt
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Cumhuriyet UniversityCompletedLung Neoplasms | Gene, p53Turkey
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Hossam Hassan Aly Hassan El SokkaryCompleted
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Karex Industries Sdn. Bhd.University of Witwatersrand, South Africa; Essential Access Health; Sigma3 Services...CompletedSexually Transmitted DiseasesUnited States, South Africa
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University Hospital, AngersNot yet recruitingCardio-Respiratory FailureFrance
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University Hospital, AngersUnknown
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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Joaquina BarandaActive, not recruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Cancer | Solid Tumor | Malignant Disease | Relapsed Hematologic MalignancyUnited States
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Sunnybrook Health Sciences CentreNovartisCompleted
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SynerGene Therapeutics, Inc.RecruitingMetastatic Pancreatic CancerUnited States
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SynerGene Therapeutics, Inc.Not yet recruiting
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SynerGene Therapeutics, Inc.TerminatedRECURRENT GLIOBLASTOMAUnited States, Taiwan
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Shenzhen SiBiono GeneTech Co.,LtdUnknownAdvanced Head and Neck CancerChina
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Sumitomo Pharma Co., Ltd.CompletedSchizophreniaChina, Japan, Korea, Republic of, Malaysia, Philippines, Russian Federation, Taiwan, Ukraine
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Wave Life Sciences Ltd.Active, not recruitingDuchenne Muscular DystrophyJordan, United Kingdom
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Medtronic - MITGCompletedColonic DiseasesSpain, France, Italy, Germany, United Kingdom
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NS Pharma, Inc.Approved for marketingMuscular Dystrophy, Duchenne | DMD
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ProTechSure Scientific, Inc.Poudre Valley Health SystemTerminated
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National Cancer Institute (NCI)Completed
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SynerGene Therapeutics, Inc.Suspended
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University of ZurichStryker European Operations BVCompletedHematoma, Subdural, Chronic | Hematoma, Subdural, Intracranial | Haematoma;Subdural;TraumaticSwitzerland