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Search clinical trials for: galactosylceramide lipidosis
Total 566 results
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Rigshospitalet, DenmarkCompletedFabry DiseaseDenmark
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Genzyme, a Sanofi CompanyCompleted
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Amicus TherapeuticsCompleted
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Wolfson Medical CenterUnknownFabry Disease in the Young StrokeIsrael
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University of ZurichCompleted
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Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
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ProtalixCompleted
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Genzyme, a Sanofi CompanyWithdrawn
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ISU Abxis Co., Ltd.Completed
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, United Kingdom, Canada, Hungary, Poland, Czech Republic
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Amicus TherapeuticsCompleted
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Amicus TherapeuticsCompleted
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, France, Netherlands, Puerto Rico, United Kingdom
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University of Alabama at BirminghamCompleted
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University of Alabama at BirminghamCompletedProteinuria | Fabry DiseaseUnited States, Slovenia
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Sang Hak LeeUnknownMixed HyperlipidemiaKorea, Republic of
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University Hospital, Clermont-FerrandUnknown
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Massachusetts General HospitalAlexion PharmaceuticalsUnknownCholesterol Ester Storage Disease | Lysosomal Acid Lipase DeficiencyUnited States
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Rambam Health Care CampusUnknown
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Cedars-Sinai Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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ISU Abxis Co., Ltd.Completed
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Maastricht University Medical CenterCompletedNeutral Lipid Storage DiseaseNetherlands
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Eunice Kennedy Shriver National Institute of Child...Washington University School of Medicine; University of Oxford; National Human...CompletedNiemann-Pick Disease, Type CUnited States
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University Hospital, BordeauxCompletedPain | Fabry's DiseaseFrance
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Johannes Gutenberg University MainzUnknownMucopolysaccharidosis | Fabry DiseaseGermany
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Exsar CorporationThe Hospital for Sick Children; NYU Langone Health; University Hospitals Cleveland...WithdrawnG(M2) Ganglioside | Tay-Sachs Disease Ganglioside | Sandhoff Disease GangliosideUnited States, Canada
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Assy NimerUnknownNon-alcoholic Fatty Liver Disease | Cholesterol Ester Storage DiseaseIsrael
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Exsar CorporationSuspendedType I Gaucher DiseaseUnited States
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National Taiwan University HospitalCompleted
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Brigham and Women's HospitalGenzyme, a Sanofi CompanyUnknown
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University of RostockCompletedStroke, Acute | Cerebrovascular Accident | Cerebral StrokeGermany, Poland
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Klinikum Wels-GrieskirchenGenzyme, a Sanofi CompanyCompletedFocus of Study: Prevalence of Fabry Disease in CKD PopulationAustria
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The Hospital for Sick ChildrenCompletedGangliosidoses, GM2 | Tay-Sachs Disease | Sandhoff DiseaseCanada
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PfizerTerminatedMixed HyperlipidemiaUnited States, Canada, Czech Republic, Finland, France, Netherlands
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University Hospital, GhentCompletedBelgian Screening Project for the Detection of Anderson-Fabry Disease in Hypertrophic CardiomyopathyLeft Ventricular HypertrophyBelgium
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Nantes University HospitalCompletedPatients With Gaucher's DiseaseFrance
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Francisco Marín OrtuñoHospital General Universitario Elche; Hospital Universitario San Juan de AlicanteUnknownRight Ventricular Hypertrophy | Fabry Disease, Cardiac Variant
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National Institute of Neurological Disorders and...CompletedFabry DiseaseUnited States
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Medical University of ViennaMedical University of GrazUnknownFabry Disease | Left Ventricular HypertrophyAustria
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Centre Hospitalier Universitaire de NiceUnknown
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The Cooper Health SystemCompletedMetachromatic LeukodystrophyUnited States
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Assistance Publique - Hôpitaux de ParisShire; Zymenex A/S; European Leukodystrophy AssociationCompletedMetachromatic LeukodystrophyFrance
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Amicus TherapeuticsCompleted
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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ActelionCompleted
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Children's National Research InstituteActelionCompletedSandhoff Disease | GM2 Gangliosidoses | Tay-SachsUnited States
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National Institute of Neurological Disorders and...CompletedBrain Neoplasm | Alzheimer's Disease | Niemann Pick DiseaseUnited States
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National Institute of Neurological Disorders and...CompletedFabry DiseaseUnited States