- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: long term follow up of children
Total 446786 results
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Bioray LaboratoriesXiangya Hospital of Central South University; Sun Yat-Sen Memorial Hospital... and other collaboratorsNot yet recruiting
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Novartis PharmaceuticalsRecruitingSickle Cell DiseaseUnited States
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St. Jude Children's Research HospitalRecruitingRefractory Hematologic Malignancy | Relapsed Hematologic MalignancyUnited States
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National Cancer Institute (NCI)RecruitingLugano Classification Limited Stage Hodgkin Lymphoma AJCC v8United States, Puerto Rico, Canada
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Semmelweis UniversityRecruiting
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Genentech, Inc.RecruitingSpinal Muscular AtrophyUnited States, Puerto Rico
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University Hospital, ToulouseRecruiting
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Centre Leon BerardUniversity of Paris 5 - Rene Descartes; Institut d'Hématologie et d'Oncologie...Recruiting
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Chinese University of Hong KongRecruiting
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Novartis PharmaceuticalsRecruitingGlioblastoma | Astrocytoma | Anaplastic Astrocytoma | Neurofibromatosis Type 1 | Anaplastic Ganglioglioma | Anaplastic Pleomorphic Xanthoastrocytoma | Ganglioglioma | Pleomorphic Xanthoastrocytoma | Diffuse Astrocytoma | Anaplastic Oligodendroglioma | Pilocytic Astrocytoma | Gangliocytoma | Central Neurocytoma | Oligodendroglioma... and other conditionsUnited States, Belgium, Spain, Denmark, Germany, Czechia, Italy, Australia, Russian Federation, France, Brazil, Netherlands, Japan, Canada, Finland, Sweden, United Kingdom, Argentina, Israel
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Children's Hospital Los AngelesRecruitingQuality of Life | Respiration Disorders | Ventilator-Induced Lung Injury | Respiratory Distress Syndrome, Adult | Neurocognitive DysfunctionUnited States
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CelgeneRecruitingNeoplasmsUnited States, Belgium, Spain, Switzerland, Canada, France, Germany, Japan, Finland, United Kingdom, Austria, Italy, Netherlands, Norway, Sweden
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Novartis PharmaceuticalsUniversity of PennsylvaniaRecruitingLong Term Safety of Patients Receiving CAR-T in an Eligible Clinical Trial or Managed Access ProgramUnited States, Japan, Australia, Germany, Spain, Belgium, Taiwan, Italy, Canada, Israel, Singapore, United Kingdom, Denmark, Finland, Norway, Austria, Netherlands, France
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingLeukemia | Solid Tumor | Hematopoietic Cell Transplantation RecipientUnited States, Puerto Rico
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St. Jude Children's Research HospitalRecruitingMucopolysaccharidosis I | Severe Combined Immunodeficiency | Neuroblastoma | Neoplasm | Malignancy, HematologicUnited States
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University Hospital, GasthuisbergCharles University, Czech Republic; Erasmus Medical Center; Fondazione IRCCS... and other collaboratorsRecruitingCancer | PregnancyUnited States, Argentina, Austria, Belgium, Czechia, Denmark, France, Germany, Greece, Italy, Mexico, Netherlands, Norway, Poland, Portugal, Russian Federation, Sweden, Tunisia, Turkey, Ukraine
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Sangamo TherapeuticsEnrolling by invitationBlood and Lymphatic DiseasesUnited States
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CSL BehringEnrolling by invitation
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitationDuchenne Muscular DystrophyUnited States
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncEnrolling by invitationMucopolysaccharidosis III-AUnited States, Australia, Spain
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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Ultragenyx Pharmaceutical IncActive, not recruitingOrnithine Transcarbamylase (OTC) DeficiencyCanada, United States, France, Spain, United Kingdom
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BioMarin PharmaceuticalEnrolling by invitationHemophilia AUnited Kingdom, United States
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Sangamo TherapeuticsEnrolling by invitationFabry Disease | Fabry Disease, Cardiac VariantUnited States, Australia, United Kingdom
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St. Jude Children's Research HospitalActive, not recruitingHematopoietic Stem Cell TransplantationUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Novartis PharmaceuticalsCompletedGrowth and DevelopmentBelgium, United States, Russian Federation
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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OPKO Health, Inc.CompletedGrowth Hormone Deficiency (GHD)United States, Belarus, Greece, Hungary, Russian Federation, Ukraine
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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bluebird bioEnrolling by invitationSickle Cell DiseaseUnited States, France
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Sarah KeimEunice Kennedy Shriver National Institute of Child Health and Human Development...Enrolling by invitation
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REGENXBIO Inc.Enrolling by invitation
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Institut de Recherches Internationales ServierADIR, a Servier Group companyActive, not recruitingAdvanced Lymphoid LeukemiaUnited States, United Kingdom, Japan, France, Spain
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Wugen, Inc.Enrolling by invitationT-cell Acute Lymphoblastic Leukemia | T-cell Lymphoblastic LymphomaUnited States, Australia
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Institut Cancerologie de l'OuestCompleted
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Mental Health Services in the Capital Region, DenmarkFrederiksberg University Hospital; The Danish Mental Health Foundation; Defactum...CompletedDepressive Symptoms | Mental Health Disorder | Emotional Problem | Anxiety Disorder of Childhood | Behavior Problem of Childhood and AdolescenceDenmark
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The Children's Hospital of Zhejiang University...Withdrawn
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Autolus LimitedEnrolling by invitationMultiple Myeloma | DLBCL | T Cell Lymphoma | Patients Followed for up to 15 Years Following Their First Dose of AUTO CAR T Cell Therapy | ALL, Adult and PediatricUnited Kingdom
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Amicus TherapeuticsActive, not recruitingBatten Disease | CLN6United States
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DBV TechnologiesEnrolling by invitationPeanut AllergyUnited States
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Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
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Swedish Orphan BiovitrumSeventh Framework ProgrammeCompletedHemophagocytic LymphohistiocytosisUnited States, France, Italy, Spain, United Kingdom
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Abeona Therapeutics, IncTerminatedMucopolysaccharidosis III-BUnited States, Germany, France
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University of AarhusRanders Municipality, Denmark; Aarhus KommuneCompleted
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University of CalgaryCanadian Institutes of Health Research (CIHR); University of AlbertaTerminatedInfant, Premature, Diseases | Asthma | Asthma in Children | Infant | Infant, Extremely Premature | AllergiesCanada
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REGENXBIO Inc.Enrolling by invitation
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ByHeartPaidion Research, Inc.CompletedHealthy | Term InfantsUnited States
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Janssen Research & Development, LLCCompleted