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Search clinical trials for: mps symptoms
Total 243534 results
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Frank VandenabeeleJessa HospitalRecruiting
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CanSino Biologics Inc.Not yet recruiting
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis Type IIIAUnited States
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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Institut National de la Santé Et de la Recherche...RecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multiple Sulfatase Deficiency Disease | Mucopolysaccharidosis IXFrance
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University of Milano BicoccaRecruiting
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Uskudar State HospitalBasaksehir Cam & Sakura Şehir HospitalNot yet recruitingMyofascial Pain Syndrome
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Kailea ManningEdward Via Virginia College of Osteopathic MedicineNot yet recruitingMyofascial Pain SyndromeUnited States
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Uskudar State HospitalNot yet recruiting
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudNot yet recruitingSanfilippo Syndrome Type CUnited States, France
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRecruitingSanfilippo Syndrome | MPS3United States
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Cairo UniversityNot yet recruitingMyofascial Pain Syndrome | Trigger Point Pain, Myofascial
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National University of SingaporeRecruitingMajor Depressive DisorderSingapore
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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Sanguine BiosciencesDenali Therapeutics Inc.RecruitingMucopolysaccharidosis III-AUnited States
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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GC Biopharma CorpRecruitingMucopolysaccharidosis II | Hunter SyndromeKorea, Republic of
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Colombia, Brazil
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States
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University of BolognaRecruitingJuxtarenal Aortic Aneurysm | Aortic Aneurysm, Thoracoabdominal | Thoracoabdominal Aortic Aneurysm | Penetrating Aortic Ulcer | Endoleak | Pararenal Aortic Aneurysm | Pseudoaneurysm | Dissection Aortic AneurysmItaly
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AO GENERIUMRecruitingMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Duke UniversityRecruiting
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Dana-Farber Cancer InstituteCharles H. Hood FoundationRecruitingMyelodysplastic Syndromes | Leukemia | Myeloproliferative SyndromeUnited States
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Mustafa Kemal UniversityRecruitingEfficacy of Dextrose Prolotherapy in Myofascial Pain SyndromeTurkey
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Samsung Medical CenterNot yet recruitingSanfilippo Syndrome A
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University of OxfordUniversity of Rochester; University of Turin, Italy; University of Texas at AustinRecruitingHemianopsia | Hemianopia | Quadrantanopia | Stroke Induced Vision LossUnited Kingdom
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Universidad del DesarrolloInstituto Milenio para Investigación en Depresión y Personalidad; Peñalolén...RecruitingDepression, Postpartum | Anxiety Disorders and Symptoms | Maternal BehaviorChile
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Ultragenyx Pharmaceutical IncPRA Health SciencesRecruitingSly Syndrome | Mucopolysaccharidosis VII | MPS VII | MPS 7United States, Germany, Brazil, Argentina, France, Netherlands, Portugal, Spain, Turkey
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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Genzyme, a Sanofi CompanyRecruitingMucopolysaccharidosis I (MPS I)Croatia, United States, Argentina, Australia, Belgium, Brazil, Canada, Denmark, France, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Lebanon, Malaysia, Netherlands, Pakistan, Philippines, Poland, Saudi Arabia, Singapore, Slovaki... and more
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Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
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Novartis PharmaceuticalsActive, not recruitingRelapsing Multiple SclerosisUnited States, Puerto Rico
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Istituto Ortopedico RizzoliActive, not recruitingOsteogenesis Imperfecta | Multiple Osteochondroma | Ollier DiseaseItaly
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncActive, not recruitingMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Australia, Spain
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ShireCompletedHunter SyndromeUnited States, United Kingdom, Canada
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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Denali Therapeutics Inc.CompletedMucopolysaccharidosis IIUnited Kingdom, United States, Italy, Netherlands
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Green Cross CorporationCompleted
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Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationSanfilippo Syndrome Type DUnited States
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University of Maryland, BaltimoreActive, not recruitingPain, Postoperative | Opioid UseUnited States
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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Ultragenyx Pharmaceutical IncAvailableSly Syndrome | Mucopolysaccharidosis VII | MPS VII
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Aalto UniversityTurku University Hospital; Helsinki University Central Hospital; Business FinlandActive, not recruitingMajor Depressive DisorderFinland
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCTerminatedMucopolysaccharidosis I | Hurler's Syndrome | Hurler-Scheie Syndrome | ScheieItaly
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InDex PharmaceuticalsTerminatedUlcerative ColitisKorea, Republic of, United Kingdom, United States, Mexico, Belgium, Netherlands, Denmark, Poland, Israel, Germany, France, Australia, Austria, Canada, Lithuania, Croatia, Italy, Romania, Turkey, Portugal, Slovakia, Hungary, Norway, Bosnia... and more
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REGENXBIO Inc.Active, not recruitingHurler Syndrome | Hurler-Scheie Syndrome | Mucopolysaccharidosis Type I (MPS I)United States, Brazil, Israel