- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: sapropterin
Total 56 results
-
Sun Yat-sen UniversityInnovent Biologics (Suzhou) Co. Ltd.RecruitingPancreatic Adenocarcinoma MetastaticChina
-
D. Walter WrayUS Department of Veterans AffairsRecruitingInflammation | HFpEF - Heart Failure With Preserved Ejection FractionUnited States
-
West China HospitalNot yet recruitingHead and Neck Squamous Cell Carcinoma
-
Louis MessinaBioMarin PharmaceuticalRecruitingPeripheral Vascular Diseases | Peripheral Artery Disease | Claudication, IntermittentUnited States
-
Emory UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingRenal Insufficiency, ChronicUnited States
-
University of NebraskaWithdrawnPeripheral Arterial Disease | Peripheral Artery Disease
-
Tulane University School of MedicineBioMarin PharmaceuticalCompletedPhenylketonuria | Behavior and Behavior Mechanisms | PAH Gene ExpressionUnited States
-
University of UtahBioMarin PharmaceuticalCompletedGTP Cyclohydrolase DeficiencyUnited States
-
BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Spain, United Kingdom, Germany
-
BioMarin PharmaceuticalCompletedPhenylketonuria | HyperphenylalaninaemiaUnited States
-
Yale UniversityCompletedPost-Prandial Hyperglycemia | Post-Prandial HypoglycemiaUnited States
-
University of Massachusetts, WorcesterWithdrawnSchizophrenia | Schizo Affective DisorderUnited States
-
BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
BioMarin PharmaceuticalCompletedEndothelial DysfunctionUnited States
-
BioMarin PharmaceuticalCompletedSickle Cell DiseaseUnited States
-
Augusta UniversityCompletedChronic Obstructive Pulmonary Disease (COPD)United States
-
BioMarin PharmaceuticalCompletedIntermittent ClaudicationUnited States, Argentina
-
BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States, Canada
-
University of British ColumbiaRare Disease Foundation, Vancouver, CanadaCompleted
-
University of MiamiCompletedPhenylketonuriaUnited States
-
Stanford UniversityCompletedGastroparesisUnited States
-
Universidade do PortoBioMarin Pharmaceutical; Centro Hospitalar do PortoCompleted
-
University of California, San DiegoBioMarin PharmaceuticalWithdrawnBehavioral Manifestations of Lesch-Nyhan DiseaseUnited States
-
University of Massachusetts, WorcesterThe Glass FoundationCompleted
-
Providence VA Medical CenterBioMarin Pharmaceutical; LifespanCompletedHeart Failure | Cardiovascular DiseaseUnited States
-
Washington University School of MedicineUniversity of Missouri-Columbia; BioMarin PharmaceuticalCompleted
-
The Children's Health CouncilBioMarin PharmaceuticalCompleted
-
The Children's Health CouncilBioMarin PharmaceuticalCompleted
-
BioMarin PharmaceuticalTerminatedPhenylketonuriaItaly, Switzerland
-
Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
-
University of Missouri-ColumbiaBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
Augusta UniversityAmerican Heart AssociationCompletedPulmonary Disease, Chronic ObstructiveUnited States
-
BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Turkey, United Kingdom, Germany, Netherlands, Slovakia, Austria, Belgium, Czechia
-
New York State Psychiatric InstituteStanley Medical Research InstituteCompletedSchizophrenia | Schizoaffective DisorderUnited States
-
BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States, Canada
-
Hamilton Health Sciences CorporationChildren's Hospital of Eastern Ontario; McMaster Children's Hospital; BioMarin...CompletedPhenylketonuria | HyperphenylalaninemiaCanada
-
BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
-
The University of Texas Health Science Center,...BioMarin PharmaceuticalTerminatedPhenylketonuria | HyperphenylalaninemiaUnited States
-
Children's Hospital of PhiladelphiaCompleted
-
Emory UniversityBioMarin Pharmaceutical; Atlanta Clinical and Translational Science InstituteCompletedPhenylketonuriaUnited States
-
Children's National Research InstituteGeorgetown UniversityWithdrawn
-
Emory UniversityTerminated
-
Merck KGaA, Darmstadt, GermanyCompleted
-
BioMarin PharmaceuticalCompleted
-
Stanford UniversityBioMarin PharmaceuticalWithdrawnClassical Phenylketonuria(PKU)
-
The University of Texas Health Science Center,...BioMarin PharmaceuticalCompletedAutism Spectrum DisorderUnited States
-
Merck KGaA, Darmstadt, GermanySmerud Medical Research International AS; Merck Serono NorwayCompleted
-
Washington University School of MedicineUniversity of Missouri-Columbia; Northwestern University; Oregon Health and Science... and other collaboratorsTerminated
-
Fundacion Clinic per a la Recerca BiomédicaCompletedLiver Cirrhosis | Portal HypertensionSpain
-
Vanderbilt UniversityNational Institutes of Health (NIH); BioMarin PharmaceuticalCompleted