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Search clinical trials for: storage endotheliopathy
Total 1216 results
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Assistance Publique - Hôpitaux de ParisCystinosis Research FoundationRecruiting
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New York Stem Cell Foundation Research InstituteSilverstein FoundationRecruitingHealthy | Parkinson Disease | Gaucher Disease | GBA Gene MutationUnited States
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Assiut UniversityNot yet recruitingPlatelet Storage Pool Deficiency
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Sanguine BiosciencesDenali Therapeutics Inc.RecruitingMucopolysaccharidosis III-AUnited States
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Tongji HospitalZhongyuan Xiehe Biological Cell Storage Service (Tianjin) Co., Ltd.RecruitingChronic Kidney DiseasesChina
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Alice BertainaCalifornia Institute for Regenerative Medicine (CIRM)RecruitingCKD Stage 4 | Cystinosis | FSGS | SLE Nephritis | SIODUnited States
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Wake Forest University Health SciencesUniversity of North Carolina, Chapel Hill; University of Kentucky; East Carolina...Not yet recruiting
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain, Germany
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National Taiwan University HospitalRecruitingStroke | Magnetic Resonance Imaging | Fabry Disease | Cerebral Small Vessel Diseases | Cadasil | HTRA1-Related Autosomal Dominant Cerebral Angiopathy | COL4A1-Related Brain Small Vessel Disease With Haemorrhage | Next-generation SequencingTaiwan
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CANbridge (Suzhou) Bio-pharma Co., Ltd.RecruitingGaucher Disease, Type 1 | Gaucher Disease, Type 3China
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Centre for Analytical Biochemistry and Biomedical...University of GiessenRecruiting
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingLate-Onset Pompe Disease | Lysosomal DiseaseUnited States
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GC Biopharma CorpRecruitingMucopolysaccharidosis II | Hunter SyndromeKorea, Republic of
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University of Roma La SapienzaAlexion PharmaceuticalsRecruitingNon-Alcoholic Fatty Liver DiseaseItaly
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Academisch Medisch Centrum - Universiteit van Amsterdam...RecruitingFabry Disease | Fabry Disease, Cardiac VariantNetherlands
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Universidade do PortoHospital da Luz, Lisboa; Hospital Pedro Hispano; Centro Hospitalar de Leiria; Centro... and other collaboratorsRecruitingFabry DiseasePortugal
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Colombia, Brazil
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SanofiRecruitingAcid Sphingomyelinase Deficiency (ASMD)France
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Manchester University NHS Foundation TrustOrchard TherapeuticsRecruitingMucopolysaccharidosesUnited Kingdom
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Freeline TherapeuticsRecruitingGaucher Disease, Type 1Spain, Israel, United States, United Kingdom, Brazil, Germany, Paraguay
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States
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SanofiRecruitingFabry DiseaseItaly, United States, Austria, China, Czechia, Denmark, France, Germany, Greece, Japan, Korea, Republic of, Netherlands, Norway, Spain, Taiwan, Turkey, United Kingdom, Canada, Poland
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LMU KlinikumRecruitingPompe Disease (Late-onset) | FSHD | Spinal Muscular Atrophy Type 3 | Inclusion Body MyositisGermany
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Massachusetts Institute of TechnologyHanger Clinic: Prosthetics & OrthoticsRecruitingAmputation of Lower Limb Below KneeUnited States
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Shaare Zedek Medical CenterRecruiting
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SanofiRecruitingGaucher's Disease Type IIIUnited States, Germany, Hungary, France, China, Japan, Canada, Argentina, Italy, Turkey
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AO GENERIUMRecruitingMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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SanofiRecruitingFabry DiseaseChina, Finland, Germany, Norway, United Kingdom, United States, Denmark, Austria, Greece, Romania, Argentina, Brazil, Canada, Japan, Mexico, Poland, Italy, France, Turkey, Australia, Switzerland
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Icahn School of Medicine at Mount SinaiRecruitingHeart Failure With Reduced Ejection Fraction | CongestionUnited States
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Assiut UniversityNot yet recruitingPlatelet Storage Lesion(PSL)
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ModernaTX, Inc.RecruitingGlycogen Storage DiseaseUnited States, Canada
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University Hospital Center of MartiniqueRecruiting
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University of Erlangen-Nürnberg Medical SchoolRecruitingPompe Disease (Late-onset) | Pompe Disease | Pompe's Disease Juvenile Onset | Pompe Disease Infantile-OnsetGermany
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Children's Hospital of Orange CountyUltragenyx Pharmaceutical IncRecruitingInflammation | Mucopolysaccharidoses | Cardiac Disease | Carotid DiseaseUnited States
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TakedaRecruiting
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Chang Gung Memorial HospitalRecruitingFabry DiseaseTaiwan
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Charite University, Berlin, GermanyRecruitingKidney Failure | Kidney Transplant; Complications | Graft DysfunctionGermany
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Istanbul University - Cerrahpasa (IUC)The Scientific and Technological Research Council of TurkeyRecruitingStroke | Multiple Sclerosis | Parkinson DiseaseTurkey
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Taipei Veterans General Hospital, TaiwanNot yet recruitingGlycogen Storage Disease Type II
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Hong Kong Children's HospitalRecruitingGlycogen Storage Disease Type IBHong Kong
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National Taiwan University HospitalRecruiting
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Duke UniversityRecruiting
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Mackay Memorial HospitalSanofi Taiwan Co. LtdRecruiting
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Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
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Rigshospitalet, DenmarkDanish Research Center for Magnetic ResonanceRecruitingGlycogen Storage Disease | Pompe Disease (Late-onset) | McArdle DiseaseDenmark
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Children's Memorial Health Institute, PolandDepartment of Internal Medicine, Hypertension and Vascular Diseases, The...Not yet recruitingGlucose 6 Phosphatase DeficiencyPoland
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Assistance Publique - Hôpitaux de ParisRecruitingAdrenoleukodystrophy | Adrenomyeloneuropathy | Metachromatic Leukodystrophy | Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaFrance