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Search clinical trials for: vacuoles
Total 14 results
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NYU Langone HealthRecruitingAutoimmune Disease | Autoinflammatory Disease | Rheumatic Disease | VEXAS SyndomeUnited States
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National Cancer Institute (NCI)RecruitingHematopoietic Stem Cell Transplantation | ImmunodeficiencyUnited States
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CHU de Quebec-Universite LavalCanadian Institutes of Health Research (CIHR); BiovaloremRecruitingPancreatic Cancer | Metastatic Cancer | Pancreatic Ductal Adenocarcinoma | Pancreas CancerCanada
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Leadiant Biosciences, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsActive, not recruiting
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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NobelpharmaCompletedGNE Myopathy | Nonaka Disease | Distal Myopathy With Rimmed Vacuoles (DMRV) | Hereditary Inclusion Body Myopathy (hIBM)Japan
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Hoffmann-La RocheNo longer availableCancers With RET AlterationsUnited States
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
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Ultragenyx Pharmaceutical IncNewcastle UniversityCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Nonaka Disease | Quadriceps Sparing Myopathy (QSM) | Distal Myopathy With Rimmed Vacuoles (DMRV)United States, Bulgaria, Canada, France, United Kingdom
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University Hospital, RouenCompletedMale InfertilityFrance
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE MyopathyUnited States, Israel
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University Hospital, ToulouseCompleted
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University Hospital, ToulouseCompleted