- ICH GCP
- US Clinical Trials Registry
- Researchers
- Canada
- Pseudoneonatal Adrenoleukodystrophy
Medical specialists from Canada tagged as investigators in clinical trials studying Pseudoneonatal Adrenoleukodystrophy
Total 1 results
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Nancy E Braverman, MD, MSSeen in:
- Quebec, Montreal, Frederique Arnaud
- Quebec, Montreal, Research Institute of the McGill University Health Center
Trials:- NCT01668186 (Principal Investigator)
- NCT06190626 (Principal Investigator)
Conditions:- Peroxisome Biogenesis Disorder;
- Zellweger Spectrum Disorder;
- RCDP - Rhizomelic Chondrodysplasia Punctata;
- D-Bifunctional Protein Deficiency;
- Alpha-Methylacyl-CoA Racemase Deficiency;
- Peroxisomal Acyl-CoA Oxidase Deficiency;
- Peroxisomal Acyl-CoA Oxidase 2 Deficiency;
- ATP Binding Cassette Subfamily D Member 3 Gene Mutation;
- ACBD5 (AcylCoA Binding Domain 5) Deficiency;
- Adult Refsum Disease;
- Sterol Carrier Protein 2 Deficiency
Clinical Trials on Pseudoneonatal Adrenoleukodystrophy
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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Masonic Cancer Center, University of MinnesotaRecruitingCerebral Adrenoleukodystrophy | Adrenoleukodystrophy | ALD (Adrenoleukodystrophy)United States
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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Thomas S. ScanlanWithdrawnAdrenomyeloneuropathy | X-Linked AdrenoleukodystrophyUnited States
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NeuroVia, Inc.UnknownX-Linked AdrenoleukodystrophyUnited States
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Beijing Tiantan HospitalRecruiting
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University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States