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Clinical Trials on AMC-Arthrogryposis Multiplex Congenita in China
Total 40 results
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Shanghai Changzheng HospitalUnknownAutosomal Dominant Polycystic Kidney Disease (ADPKD)China
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Children's Hospital of Fudan UniversitySecond Affiliated Hospital of Wenzhou Medical University; Guangzhou Women and... and other collaboratorsRecruitingGenetic Disease | Congenital Malformation | Multiple MalformationChina
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Mei changlinUnknownHypertension | Autosomal Dominant Polycystic Kidney DiseaseChina
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Children's Hospital of Chongqing Medical UniversityThe First Hospital of Jilin University; Xuzhou Maternity and Child Health Care... and other collaboratorsCompletedGenetic Diseases | Birth Defect | Congenital Malformation | Multiple Malformation | Newborn; FitChina
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Xiaofan ZhuAvailableFanconi Anemia | Autosomal or Sex Linked Recessive Genetic Disease | Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases. | Hematopoiesis Maintainance.China
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Changlin MeiThe First Affiliated Hospital with Nanjing Medical University; The First Affiliated... and other collaboratorsCompletedPolycystic Kidney, Type 1 Autosomal Dominant DiseaseChina
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Xinhua Hospital, Shanghai Jiao Tong University...UnknownIntellectual Disability | Rare Diseases | Multiple Congenital AnomalyChina
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Ministry of Health, Labour and Welfare, JapanUnknownKidney, Polycystic, Autosomal DominantJapan
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney Disease, Autosomal DominantUnited States, Belgium, United Kingdom, Russian Federation, France, Australia, Netherlands, Italy, Japan, Denmark, Romania, Poland, Canada, Argentina, Germany
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Argentina, Australia, Belgium, Brazil, Canada, Czech Republic, France, Germany, Italy, Japan, Netherlands, Norway, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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Second Affiliated Hospital, School of Medicine,...Active, not recruitingMarfan Syndrome | Lens Subluxation or DislocationChina
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Children's Hospital of Fudan UniversityRecruitingAlagille Syndrome | Atorvastatin | XanthomaChina
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Peking Union Medical College HospitalRecruiting
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Peking Union Medical College HospitalCelgene CorporationCompleted
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Peking Union Medical College HospitalUnknown
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Xiangya Hospital of Central South UniversityUnknownWaardenburg Syndrome | Large Vestibular Aqueduct SyndromeChina
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Zhi-Hong Liu, M.D.Terminated
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Shanghai Pudong HospitalUTC Therapeutics Inc.WithdrawnAcute Myeloid Leukemia (AML) | Multiple Myeloma (MM) | B-cell Non-Hodgkin's Lymphoma (B-NHL) | T-Cell Leukemia/Lymphoma, Adult | B-cell Acute Lymphoblastic Leukemia (B-ALL)China
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Children's Hospital of Fudan UniversityRecruitingPrader-Willi SyndromeChina
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Austria, Netherlands, Portugal
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Kyorin UniversityMinistry of Health, Labour and Welfare, JapanUnknown
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Chiba UniversityCompleted
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GeneScience Pharmaceuticals Co., Ltd.Peking University First Hospital; Peking Union Medical College Hospital; Children... and other collaboratorsUnknown
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Beijing Children's HospitalPeking University First Hospital; Xijing Hospital; Xiangya Hospital of Central... and other collaboratorsRecruitingEpilepsy | Tuberous Sclerosis ComplexChina
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Beijing Children's HospitalXiangya Hospital of Central South University; Peking University People's Hospital and other collaboratorsCompletedEpilepsy | Tuberous Sclerosis ComplexChina
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Peking University First HospitalRecruitingMultiple Myeloma | Amyloidosis | Smoldering Multiple Myeloma | Plasma Cell Leukemia | Cryoglobulinemia | Light Chain Deposition Disease | Castleman's Disease | Heavy Chain Deposition Disease | Polyneuropathy Organomegaly Endocrinopathy Monoclonal Gammopathy and Skin Changes | Monoclonal Gammopathy of Undetermined... and other conditionsChina
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Zhejiang UniversityYake Biotechnology Ltd.RecruitingVasculitis | Amyloidosis | Autoimmune Hemolytic Anemia | POEMS SyndromeChina
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Peking Union Medical College HospitalShijiazhuang Yiling Pharmaceutical Co. LtdUnknownEpilepsy | Tuberous Sclerosis Complex | Aspirin | Cognitive Decline | Skin LesionsChina
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The University of Hong KongCompletedEpilepsy | Cerebral Palsy | Intellectual Disability | Down Syndrome | Developmental Disability | Developmental Delay | Learning Disorders | Autistic Spectrum Disorders | Developmental DisordersChina
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Peking University First HospitalRecruitingRenal Cell Carcinoma | VHL SyndromeChina
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Tongji HospitalNanjing IASO Biotechnology Co., Ltd.RecruitingMultiple Sclerosis | Autoimmune Diseases of the Nervous System | Autoimmune Diseases | Myasthenia Gravis | Neuromyelitis Optica Spectrum Disorder | Autoimmune Encephalitis | Idiopathic Inflammatory Myopathies | Chronic Inflammatory Demyelinating Polyradiculoneuropathy | Myelin Oligodendrocyte Glycoprotein... and other conditionsChina
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Betta Pharmaceuticals Co., Ltd.Not yet recruitingRenal Cell Carcinoma | Solid Tumor | Von Hippel-Lindau DiseaseChina
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Novartis PharmaceuticalsCompleted
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Aucta Pharmaceuticals, IncTerminatedTuberous Sclerosis | Angiofibroma of FaceUnited States, China
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RenJi HospitalPeking University First Hospital; Shanghai Zhongshan Hospital; First Affiliated... and other collaboratorsRecruitingKidney Cancer | Renal Cell Carcinoma | ALK Gene Mutation | MET Gene Mutation | HLRCC | Renal Tumor Histology | Cutaneous Leiomyoma | BAP1 Tumor Predisposition Syndrome | VHL Syndrome | Birt-Hogg-Dube Syndrome | Familial Renal Cancer | FLCN Gene Mutation | FH Gene Mutation | Cutaneous Leiomyomata With Uterine LeiomyomataChina
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Genzyme, a Sanofi CompanyTerminatedPolycystic Kidney, Autosomal DominantBelgium, Germany, Czechia, United States, Italy, Poland, Argentina, Australia, Austria, Canada, China, Denmark, France, Israel, Japan, Korea, Republic of, Netherlands, Portugal, Romania, Spain, Taiwan, Turkey, United Kingdom
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Marinus PharmaceuticalsEnrolling by invitationTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, China, Italy, France, Israel, Germany, Canada, Australia
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Karyopharm Therapeutics IncActive, not recruitingAcute Myeloid Leukemia (AML) | Metastatic Colorectal Cancer (mCRC) | Metastatic Castration-Resistant Prostate Cancer (mCRPC) | Relapsed/Refractory Multiple Myeloma (RRMM) | Higher-Risk Myelodysplastic Syndrome (HR-MDS) | Newly Diagnosed Intermediate/High-Risk MDSUnited States, France, Canada, Spain, China
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Merck Sharp & Dohme LLCRecruitingVon Hippel-Lindau Disease | Pancreatic Neuroendocrine Tumor | Pheochromocytoma/Paraganglioma | Advanced Gastrointestinal Stromal Tumor | HIF-2α Mutated CancersCanada, United States, Denmark, France, Germany, Hungary, Italy, Russian Federation, Spain, Sweden, Turkey, Israel, United Kingdom, Netherlands, Australia, China, Singapore, Japan