- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on ART in Australia
Total 1236 results
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GRIN Therapeutics, Inc.RecruitingTuberous Sclerosis Complex | Focal Cortical DysplasiaSpain, United Kingdom, Australia, Belgium, Canada, Italy, Poland
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ModernaTX, Inc.RecruitingMethylmalonic AcidemiaUnited States, Spain, Canada, Netherlands, France, Australia, United Kingdom
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Hoffmann-La RocheRecruitingThyroid Eye Disease | TEDJapan, Australia, Singapore, United States, Argentina, Germany, Italy, Hong Kong
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Gilead SciencesCompletedCystic FibrosisUnited States, Canada, Australia, New Zealand
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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IntraBio IncActive, not recruitingNiemann-Pick Disease, Type CUnited States, Australia, United Kingdom, Germany, Slovakia, Netherlands, Czechia, Switzerland
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AlbireoEnrolling by invitationBiliary AtresiaSpain, United States, Netherlands, Malaysia, Canada, Germany, Turkey, Italy, France, Australia, Poland, New Zealand
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University of IowaChildren's Hospital of Philadelphia; University College London Hospitals; National... and other collaboratorsRecruitingCharcot Marie Tooth DiseaseUnited States, United Kingdom, Australia, Italy
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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Belite Bio, IncActive, not recruitingStargardt Disease 1United States, Australia, Belgium, China, France, Germany, Hong Kong, Netherlands, Switzerland, Taiwan, United Kingdom
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Heinrich-Heine University, DuesseldorfMedtronic; The George Institute; KKS Netzwerk; CHDI Foundation, Inc.; Egyptian Society...CompletedHuntington DiseaseAustria, Germany, France, Switzerland
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HemoShear TherapeuticsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Saudi Arabia, Australia
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Ionis Pharmaceuticals, Inc.RecruitingAlexander DiseaseUnited States, United Kingdom, Australia, Canada, Israel, Italy, Japan, Netherlands
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked Hypophosphatemia (XLH)Sweden, Spain, United Kingdom, Italy, Austria, France
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Gilead SciencesCompletedCystic FibrosisUnited States, Canada, Australia, New Zealand
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Bioverativ Therapeutics Inc.CompletedSevere Hemophilia BUnited States, Italy, Belgium, Australia, Brazil, Hong Kong, India, Ireland, Japan, South Africa, United Kingdom, Netherlands, Sweden, Canada, Poland, China, France, Germany
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Dr. Rebecca SchuleGerman Federal Ministry of Education and Research; German Center for Neurodegenerative...RecruitingHereditary Spastic ParaplegiaAustria, Germany, Italy
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Philip MoonsCompletedHeart Defects, CongenitalNorway, Taiwan, Belgium, Netherlands, United States, Sweden, Switzerland, Canada, Argentina, Australia, France, India, Italy, Japan, Malta
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Prof. Dr. Marcus J. SchultzEuropean Society of AnaesthesiologyCompletedMechanical VentilationGermany, Netherlands, Chile, Brazil, Italy, Belgium, Spain, France, Austria
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University Hospital PadovaCompletedHyperaldosteronismUnited States, Taiwan, Canada, Germany, Australia, Czech Republic, France, Italy, Japan, Netherlands
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Novartis PharmaceuticalsCompletedChronic Iron OverloadAustria, Italy, Greece
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Merck Sharp & Dohme LLCActive, not recruitingPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)United States, Australia, Brazil, Italy, United Kingdom
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Gilead SciencesCompletedCystic Fibrosis | Pseudomonas Aeruginosa | Lung InfectionUnited States, Australia, Canada
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada, France, Spain, Israel, Australia, Austria
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, United Kingdom, Belgium, France, Germany
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Novartis PharmaceuticalsActive, not recruitingSpinal Muscular AtrophyJapan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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University College, LondonUniversity of LiverpoolTerminatedCortical DysplasiaUnited Kingdom, France, Austria, United States, Czechia, Germany, Italy, Switzerland
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Novo Nordisk A/STerminatedHaemophilia AAustria, Serbia, Bulgaria, United Kingdom, Germany, France, Turkey
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Amryt Research LimitedCompletedEpidermolysis BullosaUnited States, Spain, Israel, Australia, France, Denmark, Switzerland, Italy, Hong Kong, Argentina, Austria, Brazil, Chile, Colombia, Czechia, Georgia, Germany, Greece, Hungary, Ireland, Romania, Russian Federation, Serbia, Singapore, U... and more
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of RochesterRecruitingFriedreich Ataxia | Neuro-Degenerative DiseaseUnited States, Canada, New Zealand, Australia, India
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Novartis PharmaceuticalsCompletedTumors Characterized by Genetic Abnormalities of ALKAustralia, Belgium, Germany, Netherlands, Spain, Italy, Singapore, Korea, Republic of, United Kingdom, United States, Canada
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Janssen Research & Development, LLCActive, not recruitingHemolytic Disease of the Fetus and NewbornUnited States, Canada, Netherlands, Belgium, Germany, Spain, Sweden, United Kingdom, Australia
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Sergiusz JozwiakMedical University of Vienna; Charite University, Berlin, Germany; Institut National... and other collaboratorsUnknownEpilepsy | Tuberous Sclerosis Complex | TSCPoland, Austria, Belgium, Czech Republic, France, Germany, Italy, Netherlands
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AlexionTerminatedWilson DiseaseUnited States, France, Germany, Spain, Canada, Singapore, Poland, Denmark, Hungary, Australia, Austria, Czechia, Hong Kong, Israel, Japan, Korea, Republic of, New Zealand, Russian Federation, Serbia, Taiwan, Turkey, United Kingdom
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Idorsia Pharmaceuticals Ltd.Active, not recruitingFabry DiseaseUnited States, United Kingdom, Norway, Germany, Australia, Canada, Spain, Switzerland, Austria, Belgium, France, Netherlands, Poland
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Population Health Research InstituteThe Hospital for Sick ChildrenCompletedTetralogy of Fallot | Congenital Heart Disease | Congenital Heart DefectCanada, United States, Korea, Republic of, Australia, China, Japan, India, Indonesia, Nepal, Russian Federation, Saudi Arabia, Ukraine
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CSL BehringCompletedHereditary AngioedemaCanada, Australia, Germany, United States, Israel
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PfizerCompletedHemophilia BGermany, Austria
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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ErydelRecruitingAtaxia TelangiectasiaUnited States, Australia, Belgium, Germany, India, Italy, Poland, Spain, Tunisia
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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AmgenCompletedOsteogenesis ImperfectaUnited States, Italy, United Kingdom, Belgium, Czechia, Australia, Canada, France, Bulgaria, Poland, Spain, Hungary, Germany
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Laurent Pharmaceuticals Inc.Cystic Fibrosis FoundationCompletedCystic FibrosisUnited States, Australia, Canada
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The Radiosurgery SocietyVisionTreeRecruitingNeoplasms | Trigeminal Neuralgia | Arteriovenous Malformation of Central Nervous SystemUnited States, Australia
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)Denmark, Germany, Japan, Australia, France, Brazil, Czechia