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- US Clinical Trials Registry
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Clinical Trials on Abnormalities, Multiple
Total 33440 results
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Andrew A HerringUniversity of California, Los Angeles; Oregon Health and Science UniversityUnknown
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, Hungary, United Kingdom, Australia, Bulgaria, Poland, Turkey
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Kadmon, a Sanofi CompanyCompletedAutosomal Dominant Polycystic Kidney | ADPKDUnited States
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Atılım UniversityCompletedDown Syndrome | Gross Motor Development Delay | Congenital Heart DefectsTurkey
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Washington University School of MedicineCompleted
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Mirum Pharmaceuticals, Inc.Childhood Liver Disease Research and Education NetworkCompletedAlagille SyndromeUnited States, Canada
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Lisbet BrandiUnknownAutosomal Dominant Polycystic KidneyDenmark
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Baylor College of MedicineActive, not recruitingFocal Dermal Hypoplasia (FDH) | Goltz SyndromeUnited States
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Stealth BioTherapeutics Inc.AvailableMitochondrial Diseases | Barth Syndrome
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Edimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal Dysplasia | Hypohidrotic Ectodermal DysplasiaUnited States
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Edimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal Dysplasia | Hypohidrotic Ectodermal DysplasiaSpain
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National Cancer Institute (NCI)RecruitingNoonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello Syndrome | Capillary Arteriovenous Malformation Syndrome | RASopathyUnited States
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Foundation for Prader-Willi ResearchRTI InternationalRecruitingPrader-Willi SyndromeUnited States
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Istituto Auxologico ItalianoRecruitingPrader-Willi SyndromeItaly
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Assistance Publique - Hôpitaux de ParisRecruiting
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University of WashingtonCompletedDown Syndrome | Trisomy 21United States
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Foundation for Prader-Willi ResearchPrader-Willi Syndrome Association USA; Foundation for Prader-Willi Research... and other collaboratorsCompletedPrader-Willi SyndromeUnited States
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Riphah International UniversityCompletedVestibular System DisorderPakistan
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Radius Pharmaceuticals, Inc.TerminatedPrader-Willi SyndromeUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyeloid Proliferations Associated With Down SyndromeUnited States, Canada, Australia, Puerto Rico
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University Hospital, ToulouseCompletedPrader-Willi SyndromeFrance
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Novo Nordisk A/SCompletedObesity | Metabolism and Nutrition DisorderFrance, United States, Turkey, Italy, Australia, New Zealand, Canada, Netherlands
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University Hospital, ToulouseEpidemiological and Clinical Research Information Network; International Clinical...CompletedPrader-Willi SyndromeFrance, Belgium, Germany
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University of PennsylvaniaSequenom, Inc/Laboratory Corporation of America HoldingsCompleted
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Levo Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, Canada, Australia
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Palladio BiosciencesNo longer availablePolycystic KidneyUnited States
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Children's Mercy Hospital Kansas CityCompleted
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Garvan Institute of Medical ResearchCompletedPrader-Willi SyndromeAustralia
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University of FloridaPrader-Willi Syndrome AssociationCompleted
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GeneScience Pharmaceuticals Co., Ltd.Peking University First Hospital; Peking Union Medical College Hospital; Children... and other collaboratorsUnknown
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Essentialis, Inc.CompletedPrader-Willi SyndromeUnited States
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A. Manzoni HospitalTerminated
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University of MichiganNational Institutes of Health (NIH)Completed
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Children's Mercy Hospital Kansas CityCompletedPrader-Willi Syndrome
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Kyorin UniversityMinistry of Health, Labour and Welfare, JapanUnknown
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UCSF Benioff Children's Hospital OaklandGenentech, Inc.CompletedBasal Cell Nevus Syndrome | Gorlin's SyndromeUnited States
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University Hospital, ToulouseNot yet recruitingPrader-Willi SyndromeFrance
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Erasmus Medical CenterFoundation for Prader-Willi Research; Prader-Willi FondsNot yet recruiting
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Johns Hopkins UniversityCornelia de Lange Syndrome FoundationNot yet recruitingCornelia de Lange SyndromeUnited States
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Children's National Research InstituteRecruiting
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The Hospital for Sick ChildrenUniversity of Western Ontario, Canada; Holland Bloorview Kids Rehabilitation...Recruiting
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The Hospital for Sick ChildrenFoundation for Prader-Willi ResearchNot yet recruiting
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University of Maryland, BaltimoreNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...Recruiting
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University Hospital, ToulouseCompleted
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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Montefiore Medical CenterJazz Pharmaceuticals; Foundation for Prader-Willi ResearchActive, not recruitingPrader-Willi SyndromeUnited States
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Harmony Biosciences, LLCActive, not recruitingPrader-Willi SyndromeUnited States
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ConSynance TherapeuticsCompletedPrader-Willi SyndromeUnited States
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Radius Pharmaceuticals, Inc.TerminatedPrader-Willi SyndromeUnited States
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Rhythm Pharmaceuticals, Inc.CompletedPrader-Willi SyndromeUnited States