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Clinical Trials on Acid Maltase Deficiency Disease in Australia
Total 312 results
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Medical University of GrazCompletedHealthy | Oxidative Stress | Vitamin B 12 Deficiency | Polyphenols | Thiamine and Niacin Deficiency States | Pyridoxine Deficiency | Folic Acid Deficiency Anemia, Dietary | Peroxidase; Defect | Homocystine; Metabolic DisorderAustria
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Medical University of ViennaCompletedHeart Failure | Acidosis, Lactic | Thiamine DeficiencyAustria
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Medical University of ViennaCompletedObesity, Morbid | Bariatric Surgery Candidate | Vitamin B 12 Deficiency | Folate Deficiency | Homocystine; Metabolic DisorderAustria
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease (Late-Onset) | Glycogenesis Type II | Acid Maltase Deficiency (AMD)United States, France, Canada, Netherlands, Australia
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Medical University of ViennaCompletedHyperemesis Gravidarum | Nausea Gravidarum | Vitamin C DeficiencyAustria
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CSL LimitedCompletedPrimary Immune Deficiency (PID)Australia
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St Vincent's Hospital MelbourneCompletedDiabetes Mellitus | KetoacidosisAustralia
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Australian and New Zealand Intensive Care Research...RecruitingShock | Metabolic AcidosisAustralia
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Nemysis LtdRDC Clinical Pty LtdRecruitingIron-deficiencyAustralia
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The Queen Elizabeth HospitalCompletedArrhythmias, Cardiac | HypokalemiaAustralia
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Keros Therapeutics, Inc.RecruitingIron Deficiency AnemiaAustralia, Israel, Romania
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CSL BehringRecruiting
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RDC Clinical Pty LtdNot yet recruiting
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NestléCompletedPhenylketonuriaAustralia, Germany
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Green BeatMedical University of GrazCompletedInflammation | Oxidative Stress | AcidosisAustria
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CSL LimitedCompletedPrimary Immune DeficiencyAustralia, New Zealand
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University Children's Hospital, ZurichActive, not recruitingVitamin B 12 DeficiencyAustria, Germany
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Australia, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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Medical University of ViennaCompletedMetabolic Acidosis | Hyperkalaemia Requiring Postoperative DialysisAustria
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South Australian Health and Medical Research InstituteFlinders UniversityCompletedIron-deficiency | Anemia | Microbial ColonizationAustralia
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States, Australia
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Kirby InstituteBristol-Myers Squibb; GlaxoSmithKline; Merck Sharp & Dohme LLC; Roche Pharma AG; Boehringer... and other collaboratorsCompleted
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Aeglea BiotherapeuticsTerminatedHomocystinuria Due to Cystathionine Beta-Synthase DeficiencyUnited States, United Kingdom, Australia
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Orphatech Pharmaceuticals, GmbHWithdrawnMolybdenum Cofactor Deficiency Type AAustralia
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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The George InstituteNot yet recruitingDiabetic KetoacidosisAustralia
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CSL LimitedCompleted
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ADARx Pharmaceuticals, Inc.RecruitingHereditary AngioedemaAustralia
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Menzies Institute for Medical ResearchRoyal Hobart Hospital Research Foundation (funding source)CompletedVitamin D Deficiency | Respiratory Tract InfectionAustralia
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Reneo Pharma LtdCompletedFatty Acid Oxidation DisorderUnited States, Spain, France, Austria, Poland, Belgium, Czechia, Denmark, Hungary, Italy, United Kingdom
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Medical University of GrazEuropean UnionCompletedVitamin D DeficiencyAustria
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Vifor PharmaParexel; ClinStar, LLCCompletedAnemia | Crohn's Disease | Ulcerative Colitis | Iron Deficiency | Inflammatory Bowel Disease | Iron-Deficiency AnemiaAustria
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
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Medical University of GrazJohannes Kepler University of Linz; Fresenius Kabi Austria GmbH, GrazCompleted
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Lumos PharmaEnrolling by invitationGrowth Hormone DeficiencyUnited States, Australia
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Merck KGaA, Darmstadt, GermanyCompletedAdult Growth Hormone DeficiencyUnited Kingdom, Germany, Australia, Sweden
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Bayside HealthNational Health and Medical Research Council, Australia; Monash University; Cystic...UnknownCystic FibrosisAustralia
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ModernaTX, Inc.RecruitingMethylmalonic AcidemiaUnited States, Spain, Canada, Netherlands, France, Australia, United Kingdom
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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Harald Dobnig, MDCompletedCritical Illness | Vitamin D DeficiencyAustria
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Menzies School of Health ResearchCompleted
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Vifor PharmaICON Clinical Research; American Regent, Inc.CompletedChronic Kidney Disease | Iron Deficiency AnaemiaUnited Kingdom, United States, Australia, Austria, Belgium, Czech Republic, Denmark, France, Germany, Greece, Italy, Netherlands, Norway, Poland, Portugal, Romania, Spain, Sweden, Turkey
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MedicureRecruitingPyridox(am)Ine 5'-Phosphate Oxidase DeficiencyUnited States, Australia
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
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HemoShear TherapeuticsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Saudi Arabia, Australia
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Medical University of GrazCompletedHeart Failure | Vitamin D DeficiencyAustria
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Kepler University HospitalTerminated