- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Aicardi-Goutieres Syndrome
Total 34213 results
-
Adeline Vanderver, MDEli Lilly and CompanyCompleted
-
Transposon Therapeutics, Inc.RecruitingAicardi-Goutières Syndrome (AGS)United Kingdom, France, Italy
-
Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsNot yet recruitingAicardi Goutières SyndromeUnited States
-
Assistance Publique - Hôpitaux de ParisCompleted
-
Eli Lilly and CompanyActive, not recruitingAicardi Goutieres Syndrome | Nakajo-Nishimura Syndrome | Chronic Atypical Neutrophilic Dermatosis With Lipodystrophy and Elevated Temperature Syndrome | STING-Associated Vasculopathy With Onset in InfancyJapan
-
University of EdinburghMedical Research Council; NHS LothianCompletedAicardi-Goutières SyndromeUnited Kingdom
-
Eli Lilly and CompanyNo longer availableChronic Atypical Neutrophilic Dermatosis With Lipodystrophy and Elevated Temperature (CANDLE) | Juvenile Dermatomyositis (JDM) | Stimulator of Interferon Genes (STING)-Associated Vasculopathy With Onset During Infancy (SAVI) | Aicardi-Goutières Syndrome (AGS)United States, United Kingdom
-
Baylor College of MedicineAicardi Syndrome FoundationRecruitingBrain Disorders | Aicardi SyndromeUnited States
-
University of California, San FranciscoUniversity of Washington; California Institute of TechnologyRecruiting
-
Children's Hospital of PhiladelphiaEli Lilly and Company; University of Pennsylvania; Takeda; National Institute of... and other collaboratorsRecruitingMucopolysaccharidoses | Leukoencephalopathies | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2... and other conditionsUnited States
-
Children's Hospital of PhiladelphiaIllumina, Inc.Active, not recruitingMucopolysaccharidoses | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2 Gangliosidosis | Zellweger... and other conditionsUnited States
-
Institut de Recherches Internationales ServierServier Bio-Innovation LLCNot yet recruitingMyelodysplastic Syndromes (MDS) | Hypomethylating Agent (HMA) Naive Myelodysplastic Syndromes (MDS)
-
TJ Biopharma Co., Ltd.Recruiting
-
National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI)RecruitingMyelodysplastic Syndromes (MDS)United States, Israel
-
AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndromes (MDS)United States, Australia, Canada, France, Germany, Italy, United Kingdom
-
AbbVieCelgene; Genentech, Inc.CompletedMyelodysplastic Syndromes (MDS)United States, Australia, Germany
-
The First Affiliated Hospital with Nanjing Medical...UnknownMyelodysplastic Syndromes (MDS)China
-
SCRI Development Innovations, LLCNovartis PharmaceuticalsTerminated
-
PersImmune, IncUniversity of California, San DiegoUnknown
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
-
National Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
-
Benjamin TomlinsonRecruitingMyelodysplastic Syndromes | MDS/MPN Crossover SyndromesUnited States
-
Ministry of Public Health, Democratic Republic...National Institutes of Health (NIH); Oregon Health and Science University; National... and other collaboratorsCompletedNeurotoxicity Syndrome, Cassava | Neurotoxicity Syndrome, Cyanate | Neurotoxicity Syndrome, Cyanide | Neurotoxicity Syndrome, ThiocyanateCongo, The Democratic Republic of the
-
Dana-Farber Cancer InstituteCompletedMyelodysplastic Syndromes (MDS)United States
-
Radboud University Medical CenterRecruitingMyelodysplastic Syndromes (MDS)Denmark, Switzerland, Serbia, Austria, Croatia, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Romania, Spain, Sweden, United Kingdom
-
TakedaWithdrawn
-
Prof. Janet DunnKing's College Hospital NHS Trust; University of Manchester; University of Birmingham and other collaboratorsRecruitingMyelodysplastic Syndromes (MDS)United Kingdom
-
Aston UniversityNot yet recruitingDry Eye Syndromes | Computer Vision Syndrome
-
AkesoRecruitingHigher-risk Myelodysplastic SyndromesUnited States, China
-
Nuwacell Biotechnologies Co., Ltd.The First Affiliated Hospital of University of Science and Technology of...Not yet recruitingRelapsed / Refractory Myelodysplastic Syndromes
-
Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
-
The University of QueenslandRoyal Brisbane and Women's HospitalUnknown
-
Navy General Hospital, BeijingNot yet recruitingHigher-risk Myelodysplastic SyndromesChina
-
University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
-
ALX Oncology Inc.Active, not recruitingHigher Risk Myelodysplastic SyndromesKorea, Republic of, United States, Spain
-
Rigel PharmaceuticalsRecruitingLow Risk Myelodysplastic SyndromesUnited States
-
Bristol-Myers SquibbActive, not recruitingLower-risk Myelodysplastic SyndromesJapan
-
The University of Texas Health Science Center,...RecruitingNeuropsychiatric SyndromesUnited States
-
Sumitomo Pharma America, Inc.TerminatedAnemia in Myelodysplastic SyndromesUnited States
-
Groupe Francophone des MyelodysplasiesUnknownAnemia in Myelodysplastic SyndromesFrance
-
Brian JonasNational Cancer Institute (NCI); Celgene; Pharmacyclics LLC.CompletedPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Therapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | Refractory High Risk Myelodysplastic SyndromeUnited States
-
argenxNot yet recruiting
-
argenxRecruitingCongenital Myasthenic SyndromeSpain, Italy, France, United Kingdom, United States, Canada
-
Catalyst Pharmaceuticals, Inc.CompletedMyasthenic Syndromes, CongenitalUnited States
-
The Champ FoundationChildren's Hospital of Philadelphia; The Cleveland ClinicRecruitingPearson Syndrome | Single Large Scale Mitochondrial DNA Deletion Syndromes (SLSMDS)United States
-
Peking University Third HospitalCompletedParaneoplastic Neurological SyndromeChina
-
Erasme University HospitalBrussel Medical Device Center (BMDC)RecruitingBlind Loop Syndrome Postoperative | Candy Cane SyndromeBelgium
-
Mayo ClinicCompletedCongenital Myasthenic SyndromeUnited States
-
Institut de Myologie, FranceAssistance Publique - Hôpitaux de ParisCompletedCongenital Myasthenic Syndrome
-
Rockefeller UniversityCompleted