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Clinical Trials on Alpha-Mannosidase B Deficiency
Total 364 results
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Skane University HospitalIndiana Hemophilia &Thrombosis Center, Inc.; Bioverativ Therapeutics Inc.; Swedish...Active, not recruitingFactor IX DeficiencyUnited States
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Hospital Universitario Dr. Jose E. GonzalezLaboratorios Valdecasas S.A.CompletedDiabetic Nephropathies | HyperhomocysteinemiaMexico
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Central Hospital, Nancy, FranceNot yet recruitingAlzheimer Disease | Homocystinemia
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Universidade Estadual de LondrinaCompletedCardiovascular Disease | Hemodialysis | Chronic Renal Failure | Uremia | HyperhomocysteinemiaBrazil
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedFatigue | Thrombocytopenia | Fever | Chronic Lymphocytic Leukemia | Lymphadenopathy | Small Lymphocytic Lymphoma | Hypogammaglobulinemia | Lymphocytosis | Night Sweats | ParaproteinemiaUnited States
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National Center for Research Resources (NCRR)University of North CarolinaCompletedHemophilia B | Factor IX Deficiency
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Georgetown UniversityCompletedEnd Stage Renal Disease | HyperhomocysteinemiaUnited States
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Clionsky Neuro Systems Inc.CompletedBrain Injuries | Hypoxia | Parkinson's Disease | Anemia | TDP-43 Proteinopathies | Dementia | Tauopathies | Mild Cognitive Impairment | Iron Deficiency | Vitamin B 12 Deficiency | Frontotemporal Dementia | Vascular Dementia | Alzheimer's Disease | Neurodegenerative Disorders | TBI | Lewy Body Dementia | Hyperhomocysteinemia
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Istanbul Medeniyet UniversityCompletedEpilepsy | Ischemic Stroke | Hyperhomocysteinemia, Thrombotic, Cbs-RelatedTurkey
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Shenzhen Ausa Pharmed Co.,LtdNanfang Hospital of Southern Medical UniversityWithdrawn
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National Taiwan University HospitalTaipei Veterans General Hospital, TaiwanRecruitingHIV Infections | Immunization; Infection | Viral Hepatitis BTaiwan
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Acquired Bleeding Disorder | Acquired Haemophilia | Congenital FVII Deficiency | Glanzmann's DiseaseFrance
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Washington University School of MedicineCompletedLung Diseases | Lung Diseases, Interstitial | Respiratory Distress Syndrome, Newborn | Pulmonary SurfactantUnited States
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ANRS, Emerging Infectious DiseasesMCM Vaccines B.V.Completed
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI)CompletedMyocardial Infarction | Heart Diseases | Cardiovascular Diseases | Coronary Disease | Cerebrovascular Accident | Hyperhomocysteinemia
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Valme University HospitalHospital Universitario Virgen Macarena; Hospital Universitario Reina Sofia... and other collaboratorsCompletedHepatitis C, Chronic | Hepatitis B, Chronic | Human Immunodeficiency VirusSpain
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMyocardial Infarction | Heart Diseases | Cardiovascular Diseases | Cerebrovascular Disorders | Peripheral Vascular Diseases | Atherosclerosis | Hyperhomocysteinemia
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Chiang Mai UniversityUnknown
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Institut de Recherche pour le DeveloppementExpertise France-L'Initiative; French National Research Institute for Sustainable...RecruitingHIV Infections | Hepatitis C | Hepatitis B, Chronic | Sexually Transmitted InfectionThailand
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Masonic Cancer Center, University of MinnesotaRecruitingMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Severe Aplastic Anemia | Bone Marrow Failure | T Cell Receptor Alpha/Beta Depletion | Telomere Biology DisorderUnited States
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National Institute of Allergy and Infectious Diseases...WithdrawnHIV Infections | Hepatitis B
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Tel-Aviv Sourasky Medical CenterSciGen, IsraelUnknown
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Shattuck Labs, Inc.CompletedMelanoma | Renal Cell Carcinoma | Hodgkin Lymphoma | Gastric Adenocarcinoma | Non Small Cell Lung Cancer | Squamous Cell Carcinoma of the Head and Neck | Diffuse Large B Cell Lymphoma | Urothelial Carcinoma | Gastroesophageal Junction Adenocarcinoma | Squamous Cell Carcinoma of the Skin | Squamous Cell Carcinoma... and other conditionsUnited States, Canada, Belgium, Spain
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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Virginia Commonwealth UniversityCompletedHepatitis B | Human Immunodeficiency VirusUnited States, Canada
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ANRS, Emerging Infectious DiseasesMCM Vaccines B.V.Completed
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National Institute of Allergy and Infectious Diseases...WithdrawnHIV Infections | Hepatitis B | Hepatitis C
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National Institutes of Health Clinical Center (CC)CompletedHIV Infections | Lymphoma, AIDS-RelatedUnited States
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ViiV HealthcarePfizerCompletedHIV CoinfectionUnited States, Germany, Poland, Spain, Czechia, United Kingdom, Hungary, Puerto Rico, France
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Aalborg University HospitalUnknownHIV Infections | Hepatitis B | Hepatitis ADenmark
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GlaxoSmithKlineTerminatedLiver Diseases | HIV Infection | Thrombocytopenia | Hepatitis C Virus | HBV | NASH - Nonalcoholic Steatohepatitis | Human Immunodeficiency Virus | Chronic Liver Disease | HCV | Non-alcoholic Steatohepatitis | Hepatitis B VirusUnited States, Spain, Taiwan, Italy, Belgium, France, Korea, Republic of, Canada, Russian Federation, Pakistan, Poland, India, Argentina
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American Thrombosis and Hemostasis NetworkNovo Nordisk A/S; Sanofi; Pfizer; Genentech, Inc.; CSL Behring; Hemophilia of Georgia... and other collaboratorsRecruitingHemophilia | Thrombosis | Thrombophilia | Sickle Cell Disease | Thalassemia | Bleeding Disorder | Von Willebrand Diseases | Factor IX Deficiency | Connective Tissue Disorder | Factor VIII Deficiency | Hematologic Disorder | Rare Bleeding Disorder | Platelet DisorderUnited States
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National Cancer Institute (NCI)TerminatedHIV Infection | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma | Recurrent Adult Lymphoblastic Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular... and other conditionsUnited States
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National Institute of Allergy and Infectious Diseases...Completed
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Fundacion para la Investigacion Biomedica del Hospital...Fundación Mutua MadrileñaCompletedHepatocellular Carcinoma | Acquired Immunodeficiency Syndrome Virus | Hepatitis, Viral, Non-A, Non-B, Parenterally-TransmittedSpain
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Stanford UniversityNot yet recruitingLiver Failure | Liver Cirrhosis | Hemophilia A | Hemophilia B | Hemophilia | Liver Transplant Disorder | Coagulation Factor DeficiencyUnited States
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Centre Hospitalier de CayenneFoundation for Scientific Research Suriname (SWOS) Paramaribo, SurinameCompletedHIV Infections | Hepatitis B | Hepatitis C | Hepatitis D | Prevalence | EpidemiologyFrench Guiana, Suriname
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Hasselt UniversityZiekenhuis Oost-LimburgCompletedHepatitis B | Human Immunodeficiency Virus | Hepatitis cBelgium
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Wake Forest University Health SciencesRecruitingMyelodysplastic Syndromes | Multiple Myeloma | Non-Hodgkin's Lymphoma | Chronic Lymphocytic Leukemia | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Hodgkin's Disease | Germ Cell Neoplasms | Immunodeficiency DiseasesUnited States
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ViiV HealthcarePfizerWithdrawnHepatitis B | Hepatitis C, Chronic | Human Immunodeficiency VirusUnited States, Canada, Poland
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National Institute of Allergy and Infectious Diseases...National Cancer Institute (NCI)CompletedHIV Infections | Lymphoma, Non-Hodgkin | Lymphoma, AIDS-Related | Sarcoma, KaposiUnited States
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National Institutes of Health Clinical Center (CC)Washington D.C. Veterans Affairs Medical CenterCompletedHepatitis B | Hepatitis C | HIV-HCV Co-InfectionUnited States
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Andres J. M. FerreriCompletedHIV | Burkitt's LymphomaItaly
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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Faculty Hospital Kralovske VinohradyCompletedInfections | Multiple Sclerosis | Autoimmune Diseases | Diabetes Mellitus, Type 1 | Rheumatoid Arthritis | Vaccine Reaction | Inflammatory Bowel Diseases | Psoriasis | Crohn Disease | Ulcerative Colitis | Down Syndrome | Atopic Dermatitis | Vitiligo | Alopecia Areata | COVID-19 Pandemic | Ankylosing Spondylitis | Lupus Erythematosus and other conditionsCzechia
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Eline C. B. EskesRecruitingAsmd, Visceral TypeNetherlands
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHIV Infections | Acquired Immunodeficiency Syndrome | Retroviridae Infections | Hepatitis B | Hepatitis, Viral, Human | Blood Transfusion | HIV-1 | Blood Donors | Hepacivirus | HIV-2 | HTLV-I | HTLV-II | West Nile Virus
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingFatigue | Overweight | Lynch Syndrome | Chronic Lymphocytic Leukemia | BRCA1 Gene Mutation | BRCA2 Gene Mutation | Breast Carcinoma | Cancer Survivor | Ovarian Carcinoma | Health Status Unknown | Body Mass Index 25 or GreaterUnited States
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SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)RecruitingGangliosidoses | Galactosialidosis | Sialidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Morquio B Disease | Gm2-Gangliosidosis, Variant B1 | GM2 Activator DeficiencyGermany