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Clinical Trials on Anemia, Hemolytic, Congenital Nonspherocytic
Total 1754 results
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Peking Union Medical College HospitalPharmacosmos A/SRecruitingSurgery | Spinal Deformity | Adult | Perioperative AnemiaChina
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Memorial Sloan Kettering Cancer CenterBoston Children's Hospital; Fred Hutchinson Cancer Center; Children's Hospital... and other collaboratorsCompletedLeukemia | Myelodysplastic Syndrome | Aplastic AnemiaUnited States
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedLeukemia | Thrombocytopenia | Fanconi Anemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital Neutropenia | Diamond-blackfan AnemiaUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedSickle Cell Disease | Thalassemia | Cerebral Adrenoleukodystrophy | Inherited Metabolic Disorders | High Risk Hematologic DisordersUnited States
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University of VirginiaCompletedAcute Myeloid Leukemia | Myelodysplastic Syndromes | Multiple Myeloma | Hodgkin Disease | Hodgkin Lymphoma | Myelofibrosis | Acute Lymphoblastic Leukemia | Mantle Cell Lymphoma | Sickle Cell Disease | Non Hodgkin Lymphoma | Acute Lymphocytic Leukemia | Myeloproliferative NeoplasmUnited States
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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AlexionApproved for marketingHemoglobinuria, ParoxysmalUnited States
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Alexion PharmaceuticalsCompletedHemoglobinuria, ParoxysmalUnited States, United Kingdom, Australia, Belgium, Canada, France, Germany, Ireland, Italy, Netherlands, Spain, Sweden, Switzerland
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Children's Hospital of PhiladelphiaRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)CompletedPancytopenia | Fanconi's AnemiaUnited States
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University of MinnesotaUnknown
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University of ZurichETH ZurichRecruiting
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of...TerminatedFANCONI ANEMIAUnited States
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University of MinnesotaCompleted
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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AlexionCompletedParoxysmal Nocturnal HemoglobinuriaFrance, United Kingdom, Norway, Russian Federation, Netherlands, United States
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AlexionAchillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal HemoglobinuriaNew Zealand, Korea, Republic of, Italy
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Kira Pharmacenticals (US), LLC.CompletedParoxysmal Nocturnal HemoglobinuriaAustralia
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaHong Kong, Thailand, Malaysia, Singapore, Serbia, Peru, Philippines, Colombia, Mexico, Poland
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AKARI TherapeuticsTerminatedParoxysmal Nocturnal HemoglobinuriaPoland
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria
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Samsung Medical CenterUnknownHemoglobinuria, ParoxysmalKorea, Republic of
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Alexion PharmaceuticalsCompletedHemoglobinuria, ParoxysmalUnited States, Australia, Belgium, Canada, Germany, Italy, United Kingdom, France, Ireland, Netherlands, Sweden, Switzerland
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain
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Jason Robert GotlibCelgene CorporationTerminatedLeukemia | Anemia | Myelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML)United States
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Aplastic Anemia and MDS International FoundationNational Organization for Rare DisordersRecruiting
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Kira Pharmacenticals (US), LLC.Not yet recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Wuhan Createrna Science and Technology Co., LtdCompletedParoxysmal Nocturnal HemoglobinuriaChina
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BioCryst PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Austria, South Africa
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Alexion PharmaceuticalsCMIC Co, Ltd. JapanCompletedParoxysmal Nocturnal Hemoglobinuria
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Peking Union Medical College HospitalUnknownParoxysmal Nocturnal HemoglobinuriaChina
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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XperiomeThe Touro College and University SystemWithdrawnHemophilia A | Hemophilia B | Idiopathic Pulmonary Fibrosis | Myasthenia Gravis | Cystic Fibrosis | Sickle Cell Disease
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Rocket Pharmaceuticals Inc.UnknownFanconi Anemia Complementation Group AUnited States
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Rocket Pharmaceuticals Inc.Enrolling by invitationFanconi Anemia | Fanconi Anemia Complementation Group ASpain
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Assistance Publique - Hôpitaux de ParisCompleted
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Alexion PharmaceuticalsCompletedPNHKorea, Republic of, Australia
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParoxysmal HemoglobinuriaUnited States
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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Assistance Publique - Hôpitaux de ParisLeeds Cancer Centre at St. James's University HospitalCompleted
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaUnited States, France, Russian Federation, Korea, Republic of, Canada, Germany, Australia, Japan, Spain, Belgium, United Kingdom
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BiocadCompletedParoxysmal Nocturnal HemoglobinuriaRussian Federation
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaHong Kong, Thailand, New Zealand, Malaysia
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AO GENERIUMCompletedParoxysmal Nocturnal HemoglobinuriaRussian Federation
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Alexion PharmaceuticalsCompletedHemoglobinuria, ParoxysmalUnited States
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University of UtahNational Institutes of Health (NIH)CompletedHemoglobinuria, ParoxysmalUnited States