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Clinical Trials on Angioedemas, Hereditary in New Zealand
Total 368 results
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AmgenCompletedBehcet SyndromeUnited States, Turkey
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Sydney Children's Hospitals NetworkJohns Hopkins University; Children's Hospital of Philadelphia; University of... and other collaboratorsUnknownCharcot-Marie-Tooth DiseaseUnited States, Australia, Italy
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New York Medical CollegeTerminatedSarcoma | Neuroblastoma | Wilms' Tumor | Refractory Solid Tumor | Recurrent Solid TumorUnited States
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Wayne State UniversityMuscular Dystrophy Association; Charcot-Marie-Tooth AssociationCompleted
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedUnilateral RetinoblastomaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedIntraocular RetinoblastomaUnited States
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Memorial Sloan Kettering Cancer CenterActive, not recruitingMesothelioma | Wilms Tumor | Pleural MesotheliomaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedKidney CancerUnited States, Canada, Puerto Rico, Australia, Netherlands, New Zealand, Switzerland
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth DiseaseUnited States
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Western Sydney Local Health DistrictRecruitingFamilial Adenomatous PolyposisAustralia
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NYU Langone HealthNovartis Pharmaceuticals; The Children's Tumor FoundationCompletedNeurofibromatosis Type IIUnited States
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The Children's Tumor FoundationRecruitingNeurofibromatosis 1 | Neurofibromatosis 2 | SchwannomatosisUnited States
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NYU Langone HealthBayer Healthcare Pharmaceuticals, Inc./Bayer Schering PharmaTerminatedneurofibromatosis1 (NF1) | Recurrent or Progressive Optic Pathway Gliomas (OPG) | Recurrent or Progressive Low-grade GliomaUnited States
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Memorial Sloan Kettering Cancer CenterCompleted
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University of IowaChildren's Hospital of Philadelphia; University College London Hospitals; National... and other collaboratorsRecruitingCharcot Marie Tooth DiseaseUnited States, United Kingdom, Australia, Italy
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Marinus PharmaceuticalsCompletedTuberous SclerosisUnited States
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National Cancer Institute (NCI)CompletedSarcoma | Lymphoma | Neuroblastoma | Wilm's TumorUnited States
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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NYU Langone HealthCompletedNeurofibromatosis Type 2 | Vestibular SchwannomasUnited States
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NYU Langone HealthCompletedNeurofibromatosis Type 2 | Meningiomas | Vestibular SchwannomasUnited States
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Memorial Sloan Kettering Cancer CenterPfizer; Dana-Farber Cancer Institute; University of Pittsburgh; University of VirginiaCompletedNeurofibromatosis | Meningioma | CNS Cancer | Hemangioblastoma | Intracranial HemangiopericytomaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingExtraocular RetinoblastomaUnited States, Canada, Australia, Brazil, Argentina, Egypt
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NYU Langone HealthGlaxoSmithKlineCompletedNeurofibromatosis 2 | Vestibular SchwannomaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedSarcoma | Lung Cancer | Brain and Central Nervous System Tumors | Neuroblastoma | Intraocular Melanoma | Melanoma (Skin) | RetinoblastomaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage III Kidney Wilms Tumor | Stage IV Kidney Wilms TumorUnited States, Canada, Australia, New Zealand, Puerto Rico, Israel, Switzerland
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Viridian Therapeutics, Inc.Recruiting
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Novartis PharmaceuticalsCompletedBreast Cancer | Advanced Solid Tumors | Cowden SyndromeNetherlands, Spain, Germany, United Kingdom, United States
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Testicular Germ Cell Tumor | Ovarian Cancer | Brain and Central Nervous System Tumors | Unspecified Adult Solid Tumor, Protocol Specific | Retinoblastoma | Extragonadal Germ Cell Tumor | Childhood Germ Cell TumorUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage I Kidney Wilms Tumor | Stage II Kidney Wilms Tumor | Stage III Kidney Wilms TumorUnited States, Canada, Australia, New Zealand, Puerto Rico, Israel, Switzerland
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Memorial Sloan Kettering Cancer CenterRecruitingBRCA1 Mutation | BRCA2 Mutation | APC Gene Mutation | MLH1 Gene Mutation | RAD51C Gene Mutation | RAD51D Gene Mutation | BRIP1 Gene Mutation | PALB2 Gene Mutation | PTEN Gene Mutation | ATM Gene Mutation | CHEK2 Gene Mutation | BARD1 Gene Mutation | MSH2 Gene Mutation | MSH6 Gene Mutation | PMS2 Gene Mutation | POLD1 Gene... and other conditionsUnited States
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Recurrent Childhood Pilocytic Astrocytoma | Recurrent Childhood Visual Pathway GliomaUnited States, Canada, Australia, New Zealand
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Immunovant Sciences GmbHTerminatedGraves' Ophthalmopathy (GO)United States, Germany, Spain, Canada, Italy
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Roswell Park Cancer InstituteCompletedLymphoma | Brain and Central Nervous System Tumors | Neuroblastoma | RetinoblastomaUnited States
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Alnylam PharmaceuticalsCompletedAcute Hepatic PorphyriaUnited States, Belgium, Bulgaria, France, Italy, Mexico, Spain, Taiwan, United Kingdom, Netherlands, Korea, Republic of, Switzerland, Czechia, Poland, Finland, Australia, Germany, Israel, Norway, South Africa
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Dana-Farber Cancer InstituteCompletedSarcoma | Neuroblastoma | Wilms Tumor | Pediatric Solid TumorUnited States
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NYU Langone HealthWithdrawnSarcoma | Brain and Central Nervous System Tumors | Neuroblastoma | RetinoblastomaUnited States, Canada, Argentina
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedSarcoma | Kidney Cancer | Ovarian Cancer | Brain and Central Nervous System Tumors | Neuroblastoma | Retinoblastoma | Liver Cancer | Extragonadal Germ Cell Tumor | Childhood Germ Cell TumorUnited States
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New York Medical CollegeRecruitingEwing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Germ Cell TumorUnited States
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Michael ShyJohns Hopkins University; University of Colorado, Denver; King's College Hospital... and other collaboratorsRecruitingCharcot Marie Tooth DiseaseUnited States, Australia, Italy, United Kingdom, Canada
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingHereditary Breast and Ovarian Cancer Syndrome | Premenopausal | Deleterious BARD1 Gene Mutation | Deleterious BRCA1 Gene Mutation | Deleterious BRCA2 Gene Mutation | Deleterious BRIP1 Gene Mutation | Deleterious EPCAM Gene Mutation | Deleterious MLH1 Gene Mutation | Deleterious MSH2 Gene Mutation | Deleterious... and other conditionsUnited States
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Alnylam PharmaceuticalsRecruitingAcute Hepatic PorphyriaBelgium, France, Germany, United Kingdom, United States, Italy, Switzerland, Sweden
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Flex Pharma, Inc.TerminatedCharcot-Marie-Tooth DiseaseUnited States
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Pharnext S.C.A.Worldwide Clinical TrialsActive, not recruitingCharcot-Marie-Tooth DiseaseUnited States, Spain, Belgium, Italy, Israel, Canada, Denmark, France, Germany
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Manhattan Eye, Ear & Throat HospitalGenentech, Inc.CompletedPolypoidal Choroidal Vasculopathy | Pseudoxanthoma Elasticum | Pathological Myopia | Retinal Angiomatous Proliferation | Coats' Disease | Idiopathic Retinal Telangiectasia | Multi-focal Choroiditis | Rubeosis Iridis | Von Hippel Lindau Disease | BEST VITELLIFORM MACULAR DYSTROPHY, MULTIFOCAL (Disorder)United States
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AstraZenecaRecruitingAdv Solid Malig - H&N SCC, ATM Pro / Def NSCLC, Gastric, Breast and Ovarian CancerSpain, United States, Belgium, United Kingdom, France, Hungary, Canada, Korea, Republic of, Australia
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Memorial Sloan Kettering Cancer CenterCompletedSarcoma | Lymphoma | Kidney Cancer | Testicular Germ Cell Tumor | Head and Neck Cancer | Ovarian Cancer | Neuroblastoma | Retinoblastoma | Liver Cancer | Extragonadal Germ Cell Tumor | Childhood Germ Cell TumorUnited States